- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Alpha-Mannosidosis in United States
Total 134 results
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David MossRecruitingAnxiety | Heart Rate Variability | Cognitive Behavioral Therapy | Alpha Stim | Cranial Electrotherapy StimulationUnited States
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Adverum Biotechnologies, Inc.Completed
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Active, not recruitingPortal Hypertension | Cholestasis | Liver Fibrosis | Biliary Atresia | Alagille Syndrome | Alpha1 Anti-Trypsin DeficiencyUnited States, Canada
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Kamada, Ltd.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Adverum Biotechnologies, Inc.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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University of FloridaCompletedAlpha-1 Antitrypsin Deficiency | Liver Fibrosis | AATD | AAT DeficiencyUnited States
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St. Louis UniversityBoston University; University College, London; University of Massachusetts, Worcester and other collaboratorsActive, not recruiting
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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CSL BehringCompletedCystic FibrosisBulgaria, Hungary, Poland, United Kingdom
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyUnited States, United Kingdom
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Medical University of South CarolinaNational Center for Research Resources (NCRR); Alpha-1 FoundationCompletedAlpha-1 Antitrypsin DeficiencyUnited States
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Vertex Pharmaceuticals IncorporatedCompleted
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Vertex Pharmaceuticals IncorporatedCompleted
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Medical University of South CarolinaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedChronic PancreatitisUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedLung Diseases, Obstructive | Emphysema | Alpha 1-Antitrypsin DeficiencyUnited States
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University of Michigan Rogel Cancer CenterCSL Behring; The Leukemia and Lymphoma SocietyCompletedGraft vs Host DiseaseUnited States
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CSL BehringCompletedEmphysema | Alpha1-proteinase Inhibitor DeficiencyAustralia, Russian Federation, United States, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden, Canada, Czech Republic
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Medical University of South CarolinaCSL BehringCompletedSmoking | Emphysema | Alpha-1 Antitrypsin Deficiency | COPDUnited States
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University of FloridaTerminatedChronic Obstructive Pulmonary Disease | Alpha-1 Antitrypsin DeficiencyUnited States
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University of FloridaRecruitingAlpha-1 Antitrypsin Deficiency | Cystic Fibrosis (CF) | AATD | AAT DeficiencyUnited States
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Talaris Therapeutics Inc.Duke UniversityWithdrawnAnemia, Sickle Cell | Thalassemia | Beta-Thalassemia | Bone Marrow Failure Syndromes | Diamond-Blackfan Anemia | Alpha-Thalassemia | Complex and Transfusion-dependent HemoglobinopathiesUnited States
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Inhibrx, Inc.CompletedAlpha-1 Antitrypsin Deficiency | AATDUnited States, New Zealand, United Kingdom
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Virginia Commonwealth UniversityCompletedAcute Myocardial InfarctionUnited States
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Grifols Therapeutics LLCEnrolling by invitationPulmonary Emphysema in Alpha-1 Antitrypsin DeficiencyUnited States, New Zealand, Denmark, Australia, Finland, Estonia, Canada, Poland, Russian Federation, Sweden, France
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Vertex Pharmaceuticals IncorporatedActive, not recruitingAlpha-1 Antitrypsin DeficiencyUnited States, United Kingdom, Germany, Ireland
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University of California, San FranciscoEnrolling by invitationStroke | Vasculitis | Aneurysm | Tumor Necrosis Factor-alphaUnited States
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Columbia UniversityAlpha-1 FoundationRecruitingChronic Obstructive Pulmonary Disease | Acute Exacerbation Copd | Alpha-1 Anti-trypsin DeficiencyUnited States
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Columbia UniversityAlpha-1 Foundation; Stony Wold-Herbert Fund, Inc.CompletedChronic Obstructive Pulmonary Disease | Emphysema | Alpha-1 Antitrypsin DeficiencyUnited States
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Wave Life Sciences Ltd.RecruitingAlpha-1 Antitrypsin DeficiencyUnited Kingdom
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Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, United States, Ireland, Belgium, New Zealand, Spain, Netherlands, Portugal, Canada, Australia, France, Austria, Germany, Sweden
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Grifols Therapeutics LLCActive, not recruitingPulmonary Emphysema in Alpha-1 PI DeficiencyUnited States, Australia, Denmark, New Zealand, Estonia, Poland, Russian Federation, Sweden, Brazil, Canada, France, Finland
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Grifols Therapeutics LLCTerminatedCOVID-19United States, Brazil, Chile, Colombia, Mexico
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Mereo BioPharmaSyneos HealthCompletedEmphysema | Alpha 1-Antitrypsin Deficiency | COPDUnited Kingdom, Belgium, United States, Denmark, Canada, Sweden, Poland, Spain
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Gerard TurinoCompletedEmphysema | Alpha 1-Antitrypsin DeficiencyUnited States, Canada
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Columbia UniversityNational Heart, Lung, and Blood Institute (NHLBI); Alpha-1 FoundationActive, not recruitingAlpha 1-Antitrypsin Deficiency | Genetic DiseaseUnited States
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Arrowhead PharmaceuticalsTerminatedAlpha-1 Antitrypsin DeficiencyAustralia, Netherlands, Germany, United Kingdom
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Kamada, Ltd.Syneos HealthRecruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, Sweden, Ireland, Netherlands, Belgium, Finland
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University of Alabama at BirminghamNational Institutes of Health (NIH); Mereo BioPharmaCompletedEmphysema or COPD | Alpha-1 Antitrypsin Deficiency (AATD) | Pi*ZZ, Pi*SZ, Pi*Null, Another Rare Phenotype/Genotype Known to be Associated With Either Low or Functionally Impaired AAT Including F or I MutationsUnited States
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John LevineNational Cancer Institute (NCI)CompletedGVHD | Graft-versus-host-diseaseUnited States
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Arrowhead PharmaceuticalsCompletedAlpha 1-Antitrypsin DeficiencyUnited States, Spain, Netherlands, Germany, Italy, Portugal
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Arrowhead PharmaceuticalsActive, not recruitingAlpha 1-Antitrypsin DeficiencyAustria, Germany, United Kingdom
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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Alnylam PharmaceuticalsTerminatedAntitrypsin Deficiency Liver DiseaseUnited Kingdom
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Vertex Pharmaceuticals IncorporatedTerminatedAlpha 1-Antitrypsin DeficiencyUnited States, Germany, Canada, Ireland
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University of Colorado, DenverOmni Bio Pharmaceutical, Inc.CompletedDiabetes | Type 1 DiabetesUnited States
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Stanford UniversityWithdrawnNeuromyelitis OpticaUnited States
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University of NottinghamNottingham University Hospitals NHS TrustRecruitingChronic Obstructive Pulmonary Disease | Alpha 1-Antitrypsin DeficiencyUnited Kingdom