- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Amino Acid Transport Disorders, Inborn
Total 7628 results
-
Emory UniversityAtlanta Clinical and Translational Science InstituteCompleted
-
The University of Texas Health Science Center,...BioMarin PharmaceuticalTerminatedPhenylketonuria | HyperphenylalaninemiaUnited States
-
Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
-
The University of Texas Health Science Center,...BioMarin PharmaceuticalCompleted
-
Emory UniversityTerminated
-
Merck KGaA, Darmstadt, GermanyCompleted
-
BioMarin PharmaceuticalCompleted
-
Shoji YanoBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
-
BioMarin PharmaceuticalApproved for marketing
-
BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
-
University of Texas Southwestern Medical CenterRecruitingGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1 | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport DefectUnited States
-
Children's Hospital Medical Center, CincinnatiCompletedBile Acid Synthesis Defect | Inborn Error of Bile Acid Metabolism | Inborn Error of Bile Acid ConjugationUnited States
-
Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Australia, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
-
University College, LondonRecruitingOrnithine Transcarbamylase DeficiencyUnited Kingdom
-
Arcturus Therapeutics, Inc.Active, not recruitingOrnithine Transcarbamylase DeficiencyUnited States
-
Aeglea BiotherapeuticsTerminatedArginase I Deficiency | HyperargininemiaCanada
-
Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
-
Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedBrain Diseases, Metabolic, Inborn | Ornithine Transcarbamylase Deficiency | Urea Cycle DisorderUnited States
-
PTC TherapeuticsNot yet recruitingPhenylketonuriaUnited States
-
First Affiliated Hospital Bengbu Medical CollegeRecruiting
-
Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustRecruiting
-
Jnana TherapeuticsRecruitingPhenylketonuriaUnited States, Australia
-
University Medical Centre LjubljanaNot yet recruitingPhenylketonurias | Nutritional and Metabolic Diseases
-
SynlogicTerminatedPhenylketonuriaUnited States, Canada, Georgia, Turkey
-
University of Southern CaliforniaNational PKU AllianceActive, not recruitingPhenylketonuriasUnited States
-
Boston Children's HospitalBioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
-
University of NebraskaCompleted
-
Homology Medicines, IncTerminated
-
University of Missouri-ColumbiaBioMarin PharmaceuticalEnrolling by invitationPhenylketonuriasUnited States
-
APR Applied Pharma Research s.a.Terminated
-
University Hospital Inselspital, BerneUniversity of ZurichCompleted
-
University Hospitals Cleveland Medical CenterBioMarin PharmaceuticalCompleted
-
The University of Texas Medical Branch, GalvestonTerminated
-
Boston Children's HospitalBioMarin PharmaceuticalCompleted
-
NestléWithdrawn
-
Universidade do PortoBioMarin Pharmaceutical; Centro Hospitalar do PortoCompleted
-
University of British ColumbiaVitaflo International, LtdUnknown
-
BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
Nutricia UK LtdWithdrawn
-
BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
University of Wisconsin, MadisonBoston Children's HospitalCompletedPhenylketonuriaUnited States
-
BioMarin PharmaceuticalTerminatedPhenylketonuriaItaly, Switzerland
-
Emory UniversityBioMarin Pharmaceutical; Atlanta Clinical and Translational Science InstituteCompletedPhenylketonuriaUnited States
-
Children's National Research InstituteGeorgetown UniversityWithdrawn
-
Oregon Health and Science UniversityTerminated
-
Merck KGaA, Darmstadt, GermanySmerud Medical Research International AS; Merck Serono NorwayCompleted