- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Amino Acid Transport Disorder in Germany
Total 60 results
-
University of BonnGerman Federal Ministry of Education and Research; University of Bonn, Department...Active, not recruitingPlasma Amino Acid Appearance and Disappearance | Postprandial Metabolic EventsGermany
-
Cytonet GmbH & Co. KGCompletedUrea Cycle DisordersGermany
-
Recordati Rare DiseasesRecruitingPropionic Acidemia | Methylmalonic AcidemiaFrance, Spain, Italy, United Kingdom, Norway, Germany, Sweden
-
PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedAmino Acid Metabolism, Inborn ErrorsFrance, United Kingdom, Italy, Belgium, Germany, Switzerland
-
Ludwig-Maximilians - University of MunichCompletedPhenylketonuria | Nutritional DeficienciesGermany
-
Klaus ParhoferTerminated
-
Merck KGaA, Darmstadt, GermanyCompleted
-
Kyberg Vital GmbHCompletedto Improve the Effectiveness of a Amino Acid Dietary Supplement in Chronic Pharyngeal Infections vs PlaceboGermany
-
Vitaflo International, LtdJohannes Gutenberg University Mainz; Kreiskliniken ReutlingenCompleted
-
Nutricia ResearchCompletedPhenylketonuriasGermany, Netherlands
-
NestléCompletedPhenylketonuriaAustralia, Germany
-
Cytonet GmbH & Co. KGCRS Clinical Research Services Mannheim GmbHCompleted
-
CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India
-
Dr. Loges & Co. GmbHBioTeSys GmbHCompletedEndothelial Dysfunction | Hyperhomocysteinemia | Hypertension Grade I, Subgroup "Borderline" (WHO)Germany
-
Ludwig-Maximilians - University of MunichEuropean UnionCompletedPhenylketonuriaGermany, Italy, Spain, United Kingdom
-
Swedish Orphan BiovitrumCompletedEfficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 (HT-1)Hereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Sweden
-
Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IGermany, United Kingdom, France
-
BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Spain, United Kingdom, Germany
-
Cytonet GmbH & Co. KGCompletedOrnithine Transcarbamylase Deficiency | Urea Cycle Disorders | Citrullinemia | Carbamoylphosphate Synthetase I DeficiencyGermany
-
Kaleido BiosciencesTerminatedUrea Cycle DisorderBelgium, United States, Spain, United Kingdom, Germany, Switzerland, Turkey
-
Andrea GropmanEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingBrain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Urea Cycle DisordersUnited States, Canada, Germany, Switzerland
-
Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
-
BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Turkey, United Kingdom, Germany, Netherlands, Slovakia, Austria, Belgium, Czechia
-
BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
-
BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
-
BioMarin PharmaceuticalSyneos HealthRecruitingPhenylketonuria, MaternalGermany, United States, Italy
-
BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States, Turkey, Canada, France, Germany, Italy, United Kingdom
-
Ultragenyx Pharmaceutical IncRecruitingLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)Turkey, United Kingdom, Spain, Saudi Arabia, Poland, Czechia, Germany
-
BioMarin PharmaceuticalCompletedTetrahydrobiopterin Deficiencies | Hyperphenylalaninemia, Non-PhenylketonuricGermany, United States
-
Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
-
Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
-
PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
-
PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
-
CENTOGENE GmbH RostockWithdrawnCholesterol Ester Storage Disease | Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Wolman TypeGermany, India, Sri Lanka
-
Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Austria, Czechia, Finland, Hungary, Ireland, Italy, Netherlands, Norway, Poland, Portugal, Spain, Sweden, United Kingdom
-
University of Erlangen-Nürnberg Medical SchoolAdrian RegensburgerRecruitingCystic Fibrosis | Liver Fibrosis | Gastrointestinal Transport Disorder | DiosGermany
-
Nova BiomedicalOcean Wellness CenterCompletedDiabetes Mellitus | Ketosis, DiabeticUnited States, Germany
-
University Hospital HeidelbergGerman Cancer Research CenterCompletedType2 Diabetes | Fatty Acid Deficiency | Alteration of Mitochondrial MembraneGermany
-
BioMarin PharmaceuticalCompletedHyperphenylalaninemia (HPA) Due to Phenylketonuria (PKU) or Tetrahydrobiopterin (BH4) DeficiencySweden, France, Italy, Spain, Germany, Netherlands, Austria, Slovakia, Portugal
-
Pascoe Pharmazeutische Praeparate GmbHRecruitingChronic Disease | Acute Disease | Vitamin C DeficiencyGermany
-
Wuerzburg University HospitalKyowa Kirin, Inc.Completed
-
Kinderkrankenhaus auf der BultTerminatedType 1 Diabetes | Diabetic KetoacidosisGermany
-
University of JenaJena University HospitalCompletedAmyotrophic Lateral Sclerosis | Dietary Habits | Disorder of Fatty Acid MetabolismGermany
-
University of RostockUnknownGrowth Disorders | Hypophosphatemic Rickets | Somatropin TherapyGermany
-
Wuerzburg University HospitalKyowa Kirin, Inc.Active, not recruiting
-
Ultragenyx Pharmaceutical IncTerminatedGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)United States, Spain, France, Germany, Italy, United Kingdom
-
AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
-
Johann Wolfgang Goethe University HospitalMedical University of Graz; University Hospital, Angers; Medical University of... and other collaboratorsCompletedIron-deficiency | Anemia | Vitamin B 12 Deficiency | Folic Acid Deficiency | Anaemia of Renal Disease | Anemia of Chronic InflammationGermany
-
Westfälische Wilhelms-Universität MünsterICON plcUnknownPseudoxanthoma Elasticum | Generalized Arterial Calcification in Infancy | Autosomal Recessive Hypophosphatemic RicketsGermany
-
CENTOGENE GmbH RostockWithdrawnHypophosphatemia | Photophobia | Renal Fanconi SyndromeGermany, India, Sri Lanka