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Clinical Trials on Anemia diseritropoyética congénita tipo 1
Total 1606 results
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedSickle Cell Anemia | Thalassemia | HemoglobinopathyUnited States
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Instituto Estadual de Hematologia Arthur de Siqueira...UnknownAnemia, Sickle Cell | Anemia; Sickle-Cell, With CrisisBrazil
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Agios Pharmaceuticals, Inc.TerminatedAnemia | Anemia, Hemolytic | Pyruvate Kinase Deficiency | Pyruvate Kinase Deficiency AnemiaUnited States, United Kingdom, Italy, Spain, Netherlands
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Brown UniversityNational Heart, Lung, and Blood Institute (NHLBI); NovartisRecruitingSickle Cell Disease | Sickle Cell Anemia in ChildrenAngola
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Fanconi's Anemia | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle Cell | Blood Disease
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle Cell | Blood Disease
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Sickle Cell-Beta0-ThalassemiaUnited States
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CSL BehringTerminated
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Steven J. HardyCompletedAnemia, Sickle CellUnited States
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Prolong PharmaceuticalsCompletedAnemia, Sickle CellColombia, Panama, Dominican Republic, Honduras
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Duke UniversityNational Institute of Nursing Research (NINR); National Institutes of Health...Completed
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The Hospital for Sick ChildrenThe Physicians' Services Incorporated FoundationCompleted
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Sohag UniversityAssiut UniversityActive, not recruiting
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Massachusetts General HospitalAgios Pharmaceuticals, Inc.RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Myeloproliferative Neoplasm | Myelodysplastic/Myeloproliferative Neoplasm | Clonal Cytopenia of Undetermined Significance | Pyruvate Kinase Deficiency | Pyruvate Kinase Deficiency Anemia | Hereditary Hemolytic Anemia | Clonal Myeloid Neoplasm | Other... and other conditionsUnited States
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Children's Hospital Los AngelesNovartisNot yet recruiting
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University of PittsburghRecruitingSickle Cell DiseaseUnited States
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Children's Hospital Medical Center, CincinnatiUniversity of Colorado, Denver; Children's Hospital of Philadelphia; Duke University and other collaboratorsRecruitingSickle Cell Disease | Sickle Cell AnemiaUnited States
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Case Comprehensive Cancer CenterCompletedSickle Cell Disease | Sickle Cell Anemia | SCDUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Disease | Sickle Cell AnemiaUnited States
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Children's Hospital Medical Center, CincinnatiCaribbean Institute for Health Research (CAIHR)Active, not recruiting
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PfizerPfizerCompletedSickle Cell Disease | Sickle Cell AnemiaUnited States
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Loyola UniversityUniversity of Illinois at Chicago; University of IbadanCompletedSickle Cell Disease | Sickle Cell AnemiaNigeria
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Imara, Inc.CompletedSickle Cell DiseaseUnited States, United Kingdom
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Indiana UniversityChildren's Hospital Medical Center, Cincinnati; Makerere University; Université... and other collaboratorsCompleted
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VersitiDana-Farber Cancer Institute; University of Illinois at Chicago; Medical College... and other collaboratorsUnknownSickle Cell Disease | Sickle Cell AnemiaUnited States
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Emmaus Medical, Inc.CompletedSickle Cell Anemia | Sickle ß0-ThalassemiaUnited States
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BloodworksUniversity of WashingtonCompletedSickle Cell Disease | Sickle Cell AnemiaUnited States
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Centre Hospitalier Universitaire de Pointe-a-PitreCompletedSickle Cell DiseaseGuadeloupe
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Assistance Publique - Hôpitaux de ParisCompletedSickle Cell AnemiaFrance
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HaEmek Medical Center, IsraelCompletedSickle Cell Anemia | Sickle Cell ThalassemiaIsrael
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The University of Hong KongCompletedHomozygous αº-thalassemia | Hb Bart's DiseaseChina
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St. Jude Children's Research HospitalBioLineRx, Ltd.Not yet recruiting
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Novartis PharmaceuticalsNot yet recruiting
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RTI InternationalRecruitingSickle Cell DiseaseUnited States
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Children's Hospital Medical Center, CincinnatiMakerere University; Ministry of Health, Uganda; Mulago Hospital, UgandaRecruiting
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Bioray LaboratoriesInstitute of Hematology & Hospital of Blood Diseases, Chinese Academy of...Not yet recruiting
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Emory UniversityNational Center for Complementary and Integrative Health (NCCIH)Recruiting
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Medical University of South CarolinaNational Institute of Nursing Research (NINR)Recruiting
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Ahmadu Bello University Teaching HospitalCyprus Institute of Neurology and GeneticsNot yet recruiting
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The University of The West IndiesRecruiting
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Forma Therapeutics, Inc.Emory UniversityNot yet recruitingSickle Cell DiseaseUnited States
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Children's Hospital Medical Center, CincinnatiJinja Regional Referral Hospital (JRRH), Sickle Cell Clinic, Jinja, UgandaRecruiting
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Beam Therapeutics Inc.RecruitingSickle Cell DiseaseUnited States
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PfizerPfizerRecruitingSickle Cell DiseaseUnited States, Nigeria, Kenya, Lebanon
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David WilliamsNational Heart, Lung, and Blood Institute (NHLBI); bluebird bio; California Institute... and other collaboratorsRecruitingA Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN 2001) (GRASP)Sickle Cell DiseaseUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...Recruiting
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Hoffmann-La RocheRecruitingSickle Cell DiseaseSpain, United States, Brazil, United Kingdom, Italy, Turkey, Kenya, Netherlands, France, South Africa, Lebanon