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Clinical Trials on Angioedemas, Hereditary in New Zealand
Total 368 results
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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Immunovant Sciences GmbHRecruitingThyroid Eye DiseaseUnited States, Belgium, Latvia, Hungary, Spain, Slovakia, Puerto Rico, New Zealand, Turkey
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NYU Langone HealthRecruitingMLH1 Gene Mutation | RAD51C Gene Mutation | BRIP1 Gene Mutation | MSH6 Gene Mutation | PMS2 Gene Mutation | BRCA-Mutated Ovarian Carcinoma | MSH2 A636P | EPCAMUnited States
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Columbia UniversityActive, not recruitingAge-related Macular Degeneration | Retinitis Pigmentosa | Vitelliform Macular Dystrophy | Choroidal Ischemia | Central Serous RetinopathyUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedIntraocular RetinoblastomaUnited States, Canada, Australia, New Zealand, India
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4D Molecular TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Dana-Farber Cancer InstituteActive, not recruiting
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Second Sight Medical ProductsNational Eye Institute (NEI)CompletedRetinitis PigmentosaUnited States, United Kingdom, France, Mexico, Switzerland
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); St. Jude Children's Research HospitalRecruitingRetinoblastomaUnited States
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The National Institute of LymphologyThe DrMarga Practice Group; The Center for Restorative Breast Surgery, LLCUnknownBreast Cancer | Hereditary Breast/Ovarian Cancer (brca1, brca2) | Congenital Lymphedema | Acquired LymphedemaUnited States
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Belite Bio, IncActive, not recruitingStargardt Disease 1United States, Australia, Belgium, China, France, Germany, Hong Kong, Netherlands, Switzerland, Taiwan, United Kingdom
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Silkiss, Rona Z., M.D., FACSLauer, Simeon, M.D.; Reier, Alice M.D.; Coleman, Morton M.D.CompletedThyroid Related Orbitopathy | Graves' Dysthyroid OphthalmopathyUnited States
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE MyopathyUnited States, Israel
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Neurotech PharmaceuticalsCompletedRetinitis PigmentosaUnited States
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Columbia UniversityLudwig-Maximilians - University of Munich; Moorfields Eye Hospital NHS Foundation... and other collaboratorsRecruitingRetinitis Pigmentosa Associated With CNGB1 MutationsUnited States, France, Germany, United Kingdom
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TyrogenexInternational Drug Development Institute; SynteractHCRTerminatedEye Diseases | Macular Degeneration | Retinal Degeneration | Retinal Diseases | Age-Related Macular Degeneration (AMD) | Exudative Age-related Macular Degeneration | AMD | Macular Degeneration, Age-related, 10United States
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Georgetown UniversityHackensack Meridian HealthCompletedBreast Cancer | Hereditary Breast CancerUnited States
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New York Stem Cell Foundation Research InstituteCharcot-Marie-Tooth AssociationRecruitingHealthy | Charcot-Marie-Tooth DiseaseUnited States
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Johns Hopkins UniversityNational Cancer Institute (NCI); National Institutes of Health (NIH); ChiRhoClin...RecruitingLynch Syndrome | Pancreas Cancer | Gene Mutation | Peutz-Jeghers Syndrome (PJS) | Germline Mutation CarrierUnited States
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Memorial Sloan Kettering Cancer CenterEnrolling by invitationSurvivors of Unilateral RetinoblastomaUnited States
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NYU Langone HealthWithdrawnNausea | Vomiting | Familial DysautonomiaUnited States
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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Neurotech PharmaceuticalsCompletedRetinitis PigmentosaUnited States
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | Amyloidosis, Hereditary | Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | Amyloidosis, Hereditary, Transthyretin-Related | Familial Transthyretin Cardiac AmyloidosisUnited States, France, Italy, Spain, Canada, Germany, Belgium, Sweden, United Kingdom
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Second Sight Medical ProductsTerminatedRetinitis PigmentosaUnited States
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Clinical Research Consultants, Inc.HumanOptics AGRecruitingFull Aniridia | Partial AniridiaUnited States
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
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Nicholas GulatiCompleted
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NYU Langone HealthGenentech, Inc.Terminated
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NYU Langone HealthCompletedDysautonomia, Familial | Baroreflex Failure SyndromeUnited States
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Genzyme, a Sanofi CompanyCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Gene Therapy | Age-Related Maculopathies | Age-Related Maculopathy | Retinal Neovascularization | Maculopathies, Age-Related | Maculopathy, Age-Related | Therapy, GeneUnited States
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Unity Health TorontoNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingHereditary Hemorrhagic TelangiectasiaCanada, United States, Netherlands
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Audentes TherapeuticsCompletedCrigler-Najjar SyndromeIsrael, United States, United Kingdom
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Alnylam PharmaceuticalsTerminatedAcute Hepatic Porphyria | Acute Intermittent Porphyria (AIP) | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP) | Hepatic Porphyrias | Porphyria AcuteUnited States
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University of RochesterNot yet recruitingAge-Related Macular Degeneration | Retinitis Pigmentosa | Retinal Dystrophies | Alcohol Use Disorder | Stargardt DiseaseUnited States
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Janssen Research & Development, LLCCompletedInterstitial Cystitis | Pigmentary Retinopathy | Pigmentary MaculopathyUnited States
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NYU Langone HealthCompletedEpilepsy | Tuberous Sclerosis Complex | Focal Cortical DysplasiaUnited States
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Audentes TherapeuticsTerminatedCrigler-Najjar SyndromeIsrael, United States, United Kingdom
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Gynecologic Oncology GroupNational Cancer Institute (NCI)CompletedOsteoporosis | Ovarian Carcinoma | Hereditary Breast and Ovarian Cancer SyndromeUnited States
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NYU Langone HealthBristol-Myers SquibbCompletedFemale Patients With Behcet's SyndromeUnited States
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NYU Langone HealthUniversitätsklinikum Hamburg-EppendorfCompleted
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ACELYRIN Inc.RecruitingThyroid Eye DiseaseUnited States, Australia
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Cure HHTUnited States Department of Defense; Food and Drug Administration (FDA)RecruitingAnemia | Epistaxis | Hereditary Hemorrhagic Telangiectasia | HHT | NosebleedUnited States
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Opthea LimitedCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Retinal Diseases | Neovascularization, PathologicUnited States
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Clementia Pharmaceuticals Inc.TerminatedExostoses, Multiple HereditaryUnited States, Spain, Canada, Japan, Italy, Portugal, United Kingdom, Turkey, Australia, Belgium, France, Netherlands
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PfizerCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Age-Related Maculopathies | Age-Related MaculopathyUnited States
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Second Sight Medical ProductsTerminatedRetinitis Pigmentosa | Outer Retinal DegenerationGermany, Italy
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Memorial Sloan Kettering Cancer CenterActive, not recruitingHearing Loss | Intraocular RetinoblastomaUnited States
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State University of New York at BuffaloEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruiting