- ICH GCP
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Clinical Trials on Anticipation, Genetic in Ireland
Total 397 results
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AstraZenecaCompletedAtopic DermatitisUnited States, Germany, Australia, Spain, United Kingdom, Poland
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, United Kingdom, Canada, Germany
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Ascendis Pharma A/SActive, not recruitingAchondroplasiaUnited States, Australia, Austria, Denmark, Germany, Ireland, New Zealand, Portugal
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National Cancer Institute (NCI)RecruitingCancer | HIV | Chronic Granulomatous Disease | Dock 8 DeficiencyUnited States
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Daiichi Sankyo, Inc.CompletedAtopic DermatitisUnited States
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ShionogiCompletedAtopic DermatitisUnited States
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States, Canada, Australia, United Kingdom, Germany, Ireland, Israel, Sweden
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European Friedreich's Ataxia Consortium for Translational...RecruitingFriedreich's AtaxiaAustria, Germany, Italy, Spain, Belgium, Czechia, France, Greece, Ireland, United Kingdom
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Mayo ClinicRecruitingCystinuria | Hyperoxaluria | Dent Disease | Lowe Syndrome | Adenine Phosphoribosyltransferase DeficiencyUnited States, Canada, Iceland, Israel
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Women and Infants Hospital of Rhode IslandSequenom, Inc.CompletedDown Syndrome | Trisomy 21United States, Canada, Israel, Hungary, Ireland, Argentina, Australia, Czech Republic, Italy, Spain
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SanofiRecruiting
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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PharmaxisCompletedCystic FibrosisAustralia, New Zealand
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Q32 Bio Inc.RecruitingAtopic DermatitisUnited States
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Ralexar Therapeutics, Inc.CompletedAtopic Dermatitis | Eczema, AtopicUnited States
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VA Office of Research and DevelopmentNot yet recruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Cord Injury | Brain Stem Infarctions | Locked-in SyndromeUnited States
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Eli Lilly and CompanyActive, not recruiting
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Vertex Pharmaceuticals IncorporatedActive, not recruitingAlpha-1 Antitrypsin DeficiencyUnited States, United Kingdom, Germany, Ireland
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Daiichi Sankyo, Inc.CompletedAtopic DermatitisUnited States
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Vanda PharmaceuticalsCompletedAtopic DermatitisUnited States
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PfizerRecruitingAtopic DermatitisUnited States, Canada, Japan
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Sequenom, Inc.CompletedDown Syndrome | AneuploidyUnited States
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Santhera PharmaceuticalsTerminatedDuchenne Muscular Dystrophy (DMD)United States, Spain, Netherlands, Sweden, Germany, France, Belgium, United Kingdom, Italy, Ireland, Switzerland, Austria, Bulgaria, Hungary, Israel
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Incyte CorporationCompletedAtopic DermatitisUnited States, Canada
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Actavis Inc.CompletedAtopic DermatitisUnited States
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Rhythm Pharmaceuticals, Inc.Active, not recruitingGenetic ObesityUnited States, Spain, Netherlands, Germany, United Kingdom, Canada, Israel, Greece
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GlaxoSmithKlineCompletedDermatitis, AtopicUnited States, Canada, Japan
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Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, United Kingdom, Netherlands, Canada, Denmark, France, Italy, Ireland, Thailand
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Annexon, Inc.CompletedHuntington DiseaseUnited States
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited Kingdom, France, Germany, Australia, Switzerland, Ireland, Belgium, Denmark, Poland
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Acrotech Biopharma Inc.Active, not recruitingAtopic DermatitisUnited States
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States, Canada, Germany, Poland
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Freeline TherapeuticsCompletedHemophilia B | Blood Coagulation Disorders, Inherited | Blood Coagulation Disorder | Haematologic DiseaseUnited States, United Kingdom, Australia, Netherlands, Austria, France, Ireland, Italy, Turkey, Canada, Germany, South Africa
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada, Australia, Ireland, United Kingdom
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Novartis PharmaceuticalsCompletedCystic FibrosisSpain, Germany, Switzerland, United Kingdom, Ireland
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada, Australia, Ireland, United Kingdom
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Dermavant Sciences GmbHCompletedAtopic DermatitisUnited States, Canada
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Eli Lilly and CompanyIncyte CorporationTerminatedAtopic DermatitisUnited States, Puerto Rico, Canada
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada, United Kingdom, Australia, Ireland
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Arcutis Biotherapeutics, Inc.CompletedAtopic Dermatitis EczemaUnited States, Canada
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Galderma R&DCompletedAtopic DermatitisUnited States, France, Poland, Germany, Australia, Canada
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Vanda PharmaceuticalsTerminatedAtopic DermatitisUnited States
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AbbVieEnrolling by invitationAtopic DermatitisUnited States, Australia, Austria, Belgium, Canada, China, Czechia, France, Germany, Greece, Hong Kong, Hungary, Ireland, Israel, Italy, Japan, Netherlands, New Zealand, Norway, Puerto Rico, Slovakia, Spain, Sweden, United Kingdom
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Eli Lilly and CompanyTerminatedAtopic DermatitisSpain, Puerto Rico, United States, Canada, Japan, Italy, Argentina, Austria, Czechia, France, Germany, Hungary, Mexico
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PfizerCompletedAtopic DermatitisUnited States, Canada, Australia, Germany, Hungary
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CelgeneCompletedEczema | Dermatitis, AtopicUnited States, Canada, Japan, Poland, China, Czechia
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PfizerCompletedAtopic DermatitisGermany, United States, Canada, Denmark, Hungary, Australia, Latvia, Poland, Bulgaria, Japan