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Clinical Trials on Arthrogryposis Multiplex Congenita (AMC) in New Zealand
Total 192 results
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The Rogosin InstituteWeill Medical College of Cornell University; Rockefeller UniversityCompletedChronic Kidney Disease | Polycystic Kidney, Autosomal DominantUnited States
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney, Autosomal DominantUnited States
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Yale UniversityTerminatedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Kadmon, a Sanofi CompanyCompletedAutosomal Dominant Polycystic Kidney | ADPKDUnited States
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The Rogosin InstituteWeill Medical College of Cornell University; New York Presbyterian HospitalWithdrawnAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Kadmon, a Sanofi CompanyCompletedPolycystic Kidney, Autosomal DominantUnited States
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The Rogosin InstituteWeill Medical College of Cornell UniversityCompletedAutosomal Dominant Polycystic KidneyUnited States
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Otsuka Pharmaceutical Development & Commercialization...CompletedPolycystic Kidney, Autosomal DominantBelgium, Germany, Italy, Spain, Sweden, United States, Canada, Australia, Netherlands, Czechia, Poland, Denmark, Israel, Hungary, Russian Federation, South Africa, United Kingdom, Romania, Argentina, Norway
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ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
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Weill Medical College of Cornell UniversityThe Rogosin InstituteEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Palvella Therapeutics, Inc.RecruitingPachyonychia CongenitaUnited States
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Regulus Therapeutics Inc.CompletedPolycystic Kidney Disease, Autosomal DominantUnited States
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PfizerCompletedPolycystic Kidney, Autosomal DominantUnited States, Canada, Australia, Sweden, Spain, Poland, Korea, Republic of, Switzerland, United Kingdom, Moldova, Republic of, Italy, Czech Republic, Hungary, Lithuania, Romania, Slovakia, Turkey
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, Hungary, United Kingdom, Australia, Bulgaria, Poland, Turkey
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Palladio BiosciencesCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Australia, Belgium, Germany, Italy, Poland, Romania, United Kingdom, Argentina, Canada, France, Netherlands, Russian Federation
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Taipei Medical University Shuang Ho HospitalUniversity of Southern CaliforniaEnrolling by invitationChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney DiseaseTaiwan
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney Disease, Autosomal DominantUnited States, Belgium, United Kingdom, Russian Federation, France, Australia, Netherlands, Italy, Japan, Denmark, Romania, Poland, Canada, Argentina, Germany
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Argentina, Australia, Belgium, Brazil, Canada, Czech Republic, France, Germany, Italy, Japan, Netherlands, Norway, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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Palvella Therapeutics, Inc.RecruitingPachyonychia CongenitaUnited States, United Kingdom
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Reata, a wholly owned subsidiary of BiogenTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, United Kingdom, Australia, France, Japan, Germany, Belgium, Czechia, Italy
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Palvella Therapeutics, Inc.UnknownPachyonychia CongenitaUnited States
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AlbireoCompletedAlagille SyndromeUnited States, United Kingdom, France, Germany, Canada, Netherlands, Italy, Malaysia, Belgium, Israel, New Zealand, Poland, Turkey
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Otsuka Pharmaceutical Development & Commercialization...CompletedChronic Kidney Disease | Autosomal Dominant Polycystic Kidney DiseaseAustralia, Belgium, Italy, Spain, Sweden, United States, Canada, Netherlands, Czechia, Poland, Germany, Russian Federation, Hungary, Israel, Puerto Rico, Argentina, Denmark, South Africa, United Kingdom, Norway, France, Romania
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ArQule, Inc. (a wholly owned subsidiary of Merck...Worldwide Clinical TrialsTerminatedPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus SyndromeUnited States, Australia, Italy, Spain
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Northwestern UniversityIcahn School of Medicine at Mount SinaiCompletedNetherton Syndrome | Ichthyosis | Lamellar Ichthyosis | Autosomal Recessive Congenital Ichthyosis | Congenital Ichthyosiform Erythroderma | Epidermolytic IchthyosisUnited States
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant Hypocalcemia (ADH)United States, Australia, United Kingdom, Denmark, Italy, France, Japan, Taiwan, Canada, Czechia, Netherlands
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Northwestern UniversityIcahn School of Medicine at Mount Sinai; Galderma R&DRecruiting
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Regulus Therapeutics Inc.RecruitingPolycystic Kidney, Autosomal Dominant | Autosomal Dominant Polycystic Kidney Disease | ADPKDUnited States
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Azitra Inc.Not yet recruiting
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Spain, Canada, New Zealand, Argentina, Mexico, Singapore
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Novo Nordisk A/SCompletedObesity | Metabolism and Nutrition DisorderFrance, United States, Turkey, Italy, Australia, New Zealand, Canada, Netherlands
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant HypocalcemiaUnited States, France, Denmark, Australia, Japan, Belgium, Canada, Italy, Netherlands, United Kingdom, Portugal, Finland, Germany
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Premier Specialists, AustraliaRecruitingKeratosis PilarisAustralia
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Icahn School of Medicine at Mount SinaiCompletedPolycystic Kidney DiseaseUnited States
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Merck Sharp & Dohme LLCActive, not recruitingPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)United States, Australia, Brazil, Italy, United Kingdom
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State University of New York - Upstate Medical...Terminated
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Italy, Argentina, France, Spain, Mexico, Canada, New Zealand, Singapore, United Kingdom
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Columbia UniversityCompleted
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National Center for Research Resources (NCRR)Completed
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Rutgers, The State University of New JerseyCompletedObesity | Prader-Willi SyndromeUnited States
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Neuren Pharmaceuticals LimitedRecruiting
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National Center for Research Resources (NCRR)CompletedRetinitis Pigmentosa | Usher Syndrome | Congenital Hearing ImpairmentUnited States
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Carelon ResearchNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedDown Syndrome | Congenital Heart DiseaseUnited States, Canada
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NYU Langone HealthEnrolling by invitation
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Dermatology Specialties Limited PartnershipCompletedTuberous Sclerosis | Facial AngiofibromaUnited States, Taiwan, Serbia, Spain, Australia, Czechia, Hungary, New Zealand, Slovakia
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Albert Einstein College of MedicineNational Heart, Lung, and Blood Institute (NHLBI)RecruitingDiGeorge Syndrome | 22q11.2 Deletion SyndromeUnited States
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Natera, Inc.CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Vanishing TwinUnited States