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Clinical Trials on Autosomal or Sex Linked Recessive Genetic Disease in Finland
Total 266 results
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Hospital for Children and Adolescents, FinlandEnrolling by invitationKallmann SyndromeFinland
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.Completed
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Novartis PharmaceuticalsTerminatedFragile X SyndromeGermany, United States, Switzerland, Australia, Canada, Denmark, France, Italy, United Kingdom, Spain
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Novartis PharmaceuticalsTerminatedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, Denmark, Italy, Netherlands, Spain, Sweden, United Kingdom, France
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Switzerland, Germany, Australia, Canada, Denmark, France, Italy, Spain, United Kingdom
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Hoffmann-La RocheCompletedFragile X SyndromeFrance, Spain, United States, Peru, Canada, United Kingdom, Chile, Argentina, Mexico, Sweden
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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NightstaRx Ltd, a Biogen CompanyCompletedChoroideremiaFinland, United States, Canada, Denmark, Netherlands, Germany, United Kingdom, Brazil, France
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, Hungary, United Kingdom, Australia, Bulgaria, Poland, Turkey
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BSweden, Finland, Denmark
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Argentina, Australia, Belgium, Brazil, Canada, Czech Republic, France, Germany, Italy, Japan, Netherlands, Norway, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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Orion Corporation, Orion PharmaCompleted
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Uute Scientific OyActive, not recruitingAtopic DermatitisFinland
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Johnson & Johnson Consumer Inc. (J&JCI)Infinant Health, Inc. (formerly known as Evolve BioSystems, Inc.)Active, not recruiting
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Helsinki University Central HospitalUnknownAtopic DermatitisFinland
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Novo Nordisk A/SEnrolling by invitationHaemophilia BCanada, United Kingdom, Czechia, Germany, Greece, Austria, Belgium, Croatia, Denmark, Finland, Norway, Portugal
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IpsenCompletedRenal Insufficiency, Chronic | Pituitary Diseases | Dwarfism | Turner SyndromeFrance, Germany, Finland, Spain, Belgium, Czechia, Denmark, Greece, Italy, Romania, Russian Federation, Slovakia, Ukraine, United Kingdom
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Petra LarmoCliniscan LtdTerminated
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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Turku University HospitalMead Johnson Nutrition; Academy of FinlandCompletedGut Microbiota | Skin Microbiota | Humoral Immune Responses | Severity of Atopic DermatitisFinland
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University of HelsinkiCompletedAtopic DermatitisFinland
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Women and Infants Hospital of Rhode IslandCompletedPregnancy Related | Aneuploidy | Genetic DiseaseUnited States
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BioCis Pharma LtdCompleted
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Noonan Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Adult Growth Hormone Deficiency | Genetic Disorder | Foetal Growth Problem | Small for Gestational AgeIsrael, Saudi Arabia, Spain, Argentina, Russian Federation, Germany, Netherlands, Italy, Belgium, United Kingdom, Slovenia, Ireland, Sweden, Denmark, Hungary, Finland, Norway, France, Czechia, Lithuania, Luxembourg, Serbia, Switzerland
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ShireCompletedFabry DiseaseFinland, Sweden, Germany, Belgium, Czechia, Denmark
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Sequenom, Inc.CompletedTurner Syndrome | Down Syndrome (Trisomy 21) | Patau Syndrome (Trisomy 13) | Edwards Syndrome (Trisomy 18)United States
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LEO PharmaCompleted
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Natural Resources Institute FinlandTampere UniversityRecruitingMicrobial Colonization | Atopic Dermatitis | Immune System and Related Disorders | Nature, HumanFinland
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ShireCompletedFabry DiseaseUnited States, Slovenia, Australia, Finland, Poland, Czechia, United Kingdom
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant HypocalcemiaUnited States, France, Denmark, Australia, Japan, Belgium, Canada, Italy, Netherlands, United Kingdom, Portugal, Finland, Germany
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National Cancer Institute (NCI)RecruitingCancer | HIV | Chronic Granulomatous Disease | Dock 8 DeficiencyUnited States
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ShireCompletedFabry DiseaseUnited States, United Kingdom, Australia, Czechia, Finland, Paraguay, Poland, Slovenia
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LEO PharmaCompletedAtopic DermatitisUnited Kingdom, Finland, Canada, Denmark
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Astellas Pharma IncCompletedDermatitis, AtopicUnited Kingdom, Finland, Ireland, Canada, Latvia
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Astellas Pharma IncCompletedDermatitis, AtopicUnited Kingdom, Finland, Ireland, Canada, Latvia
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University of TurkuUnknownUnverricht-Lundborg SyndromeFinland
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Novo Nordisk A/SRecruitingSGA, Turner Syndrome, Noonan Syndrome, ISSKorea, Republic of, United States, Ireland, United Kingdom, Finland, France, Netherlands, Japan, Thailand, Belgium, China, Israel, Brazil, India, Portugal, Austria, Bulgaria, Canada, Croatia, Germany, Greece, Malaysia, Poland, Saudi Arabia and more
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Tampere UniversityProfessor Lauri Lehtimäki; Professor Mika Mäkelä; Professor Sanna Toppila-Salmi; Professor Ilkka JunttilaNot yet recruitingAsthma | Allergy | Rhinitis, Allergic | Asthma in Children | Atopic Dermatitis | Allergen ImmunotherapyFinland
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University of HelsinkiMerck Sharp & Dohme LLCCompletedAsthma | Allergic Conjunctivitis | Seasonal Allergic Rhinitis | Atopic EczemaFinland
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ShireTerminatedFabry DiseaseSpain, Greece, Germany, Portugal, Canada, Finland, Poland, Sweden
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Serentis Ltd.CompletedAtopic DermatitisGermany, Bulgaria, Finland
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Reata, a wholly owned subsidiary of BiogenCompletedFocal Segmental Glomerulosclerosis | IgA Nephropathy | Autosomal Dominant Polycystic Kidney | CKD Associated With Type 1 DiabetesUnited States