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Clinical Trials on Autosomal Dominant Cerebellar Ataxia
Total 456 results
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University Medical Center GroningenRadboud University Medical CenterRecruitingAutosomal Dominant Polycystic Kidney | Polycystic Liver DiseaseNetherlands
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Erasmus Medical CenterRecruitingAutosomal Dominant Polycystic KidneyNetherlands
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Changlin MeiThe First Affiliated Hospital with Nanjing Medical University; The First Affiliated... and other collaboratorsCompletedPolycystic Kidney, Type 1 Autosomal Dominant DiseaseChina
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Samsung Medical CenterCompletedSpinocerebellar Ataxias | Multiple System Atrophy, Cerebellar Variant (Disorder)Korea, Republic of
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Assistance Publique - Hôpitaux de ParisRecruitingSpinocerebellar Ataxias | Inherited Movement Disorders | Hyperkinetic DisordersFrance
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Johann Wolfgang Goethe University HospitalCompletedAtaxia TelangiectasiaGermany
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University of PlymouthRecruitingAtaxia Telangiectasia | Ataxia Telangiectasia in ChildrenUnited Kingdom
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Taipei Medical University Shuang Ho HospitalUniversity of Southern CaliforniaEnrolling by invitationChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney DiseaseTaiwan
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University of Erlangen-Nürnberg Medical SchoolRecruitingAutosomal Dominant Polycystic Kidney Disease | Uncontrolled Hypertension | Renal DenervationGermany
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University Hospital, RouenNot yet recruiting
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Mario Negri Institute for Pharmacological ResearchCompleted
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Radboud University Medical CenterA-T Children's Project; Twan foundation (https://twanfoundation.nl)CompletedAtaxia Telangiectasia | ATM Gene MutationNetherlands
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Federal Research Institute of Pediatric Hematology...CompletedAtaxia Telangiectasia | DysmetriaRussian Federation
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Genzyme, a Sanofi CompanyTerminatedPolycystic Kidney, Autosomal DominantBelgium, Germany, Czechia, United States, Italy, Poland, Argentina, Australia, Austria, Canada, China, Denmark, France, Israel, Japan, Korea, Republic of, Netherlands, Portugal, Romania, Spain, Taiwan, Turkey, United Kingdom
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University of Texas Southwestern Medical CenterWithdrawnFamilial HypercholesterolemiaUnited States
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IntraBio IncRecruitingAtaxia Telangiectasia | Louis Bar SyndromeSpain, United States, Germany, United Kingdom
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Santhera PharmaceuticalsCompletedFreidreich's AtaxiaGermany, Netherlands, France, Austria, Belgium
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McMaster UniversityCompletedPolyuria | Autosomal Dominant Polycystic KidneyCanada
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Institut National de la Santé Et de la Recherche...Not yet recruiting
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Stealth BioTherapeutics Inc.Active, not recruitingFriedreich AtaxiaUnited States
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Metro International Biotech, LLCChildren's Hospital of PhiladelphiaCompleted
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Design TherapeuticsCompleted
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Minoryx Therapeutics, S.L.CompletedFriedreich AtaxiaSpain, Belgium, France, Germany
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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ShireCompletedFriedreich's AtaxiaUnited States
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National Institute of Neurological Disorders and...Completed
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University of South FloridaFriedreich's Ataxia Research Alliance; Edison Pharmaceuticals IncCompleted
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University of South FloridaUnknownFriedreich's AtaxiaUnited States
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Penwest Pharmaceuticals Co.CompletedFriedreich's AtaxiaUnited States
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Federico II UniversityCompleted
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National Institute of Neurological Disorders and...Completed
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Dr. Rebecca SchuleGerman Research Foundation; German Center for Neurodegenerative Diseases (DZNE)RecruitingSpastic AtaxiaCanada, France, Germany, Italy, Netherlands, Turkey, United Kingdom
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Quince Therapeutics S.p.A.CompletedGenetic Syndrome | Nervous System DiseaseIndia, United States, Australia, Germany, Italy, Norway, Poland, Spain, Tunisia, United Kingdom, Israel, Belgium
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Shenzhen Beike Bio-Technology Co., Ltd.The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical... and other collaboratorsUnknown
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University of Sao Paulo General HospitalUnknownCerebellar AtaxiaBrazil
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S. Andrea HospitalAgenzia Italiana del FarmacoCompleted
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Genzyme, a Sanofi CompanyCompletedHealthy Volunteers | Polycystic Kidney, Autosomal DominantUnited States
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldCompletedPolycystic Kidney, Autosomal Dominant
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Mayo ClinicRecruitingAutosomal Dominant Polycystic Kidney | Autosomal Dominant Polycystic Liver Disease | Renal Cyst | Hepatic CystUnited States
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Regeneron PharmaceuticalsSanofiCompletedHypercholesterolemiaFrance, United States
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University Hospital, RouenCompletedAutosomal Dominant Cases of Alzheimer 's DiseaseFrance
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingLeukoencephalopathies | Genetic Disease | White Matter Disease | Ataxia, Cerebellar | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate ElevationUnited States
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BiogenNot yet recruiting
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University of FloridaNational Institutes of Health (NIH); National Center for Advancing Translational... and other collaboratorsRecruiting
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European Friedreich's Ataxia Consortium for Translational...RecruitingFriedreich's AtaxiaAustria, Germany, Italy, Spain, Belgium, Czechia, France, Greece, Ireland, United Kingdom
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Murdoch Childrens Research InstituteCompleted