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Clinical Trials on Autosomal Dominant Optic Atrophy
Total 240 results
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Erasmus Medical CenterRecruitingAutosomal Dominant Polycystic KidneyNetherlands
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Changlin MeiThe First Affiliated Hospital with Nanjing Medical University; The First Affiliated... and other collaboratorsCompletedPolycystic Kidney, Type 1 Autosomal Dominant DiseaseChina
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University of Erlangen-Nürnberg Medical SchoolRecruitingAutosomal Dominant Polycystic Kidney Disease | Uncontrolled Hypertension | Renal DenervationGermany
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Taipei Medical University Shuang Ho HospitalUniversity of Southern CaliforniaEnrolling by invitationChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney DiseaseTaiwan
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University Hospital, RouenNot yet recruiting
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Mario Negri Institute for Pharmacological ResearchCompleted
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Genzyme, a Sanofi CompanyTerminatedPolycystic Kidney, Autosomal DominantBelgium, Germany, Czechia, United States, Italy, Poland, Argentina, Australia, Austria, Canada, China, Denmark, France, Israel, Japan, Korea, Republic of, Netherlands, Portugal, Romania, Spain, Taiwan, Turkey, United Kingdom
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University of Texas Southwestern Medical CenterWithdrawnFamilial HypercholesterolemiaUnited States
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McMaster UniversityCompletedPolyuria | Autosomal Dominant Polycystic KidneyCanada
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingBethlem Myopathy | Ullrich Congenital Muscular Dystrophy 1, Digenic, Col6A1/Col6A2 | Ullrich Congenital Muscular Dystrophy 1, Autosomal Recessive | Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant | Bethlem Myopathy 1, Autosomal Recessive | UCMD | BTHLM1United Kingdom
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Genzyme, a Sanofi CompanyCompletedHealthy Volunteers | Polycystic Kidney, Autosomal DominantUnited States
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldCompletedPolycystic Kidney, Autosomal Dominant
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Mayo ClinicRecruitingAutosomal Dominant Polycystic Kidney | Autosomal Dominant Polycystic Liver Disease | Renal Cyst | Hepatic CystUnited States
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Regeneron PharmaceuticalsSanofiCompletedHypercholesterolemiaFrance, United States
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University Hospital, RouenCompletedAutosomal Dominant Cases of Alzheimer 's DiseaseFrance
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University of Colorado, DenverCompletedPolycystic Kidney, Autosomal DominantUnited States
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GenSight BiologicsNo longer availableLeber Hereditary Optic Neuropathy (Optic, Atrophy, Hereditary, Leber)
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Ludwig-Maximilians - University of MunichCompletedInclusion Body Myositis, Sporadic | Inclusion Body Myopathy, Autosomal-recessive | Inclusion Body Myopathy, Autosomal-dominant | Congenital Cataracts, Facial Dysmorphism, And NeuropathyGermany
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The Rogosin InstituteWeill Medical College of Cornell UniversityCompletedAutosomal Dominant Polycystic KidneyUnited States
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Reata, a wholly owned subsidiary of BiogenTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, United Kingdom, Australia, France, Japan, Germany, Belgium, Czechia, Italy
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Calcilytix Therapeutics, Inc., a BridgeBio companyCompletedAutosomal Dominant Hypocalcemia (ADH)United States
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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Mahidol UniversityCompletedOptic Atrophy, Hereditary, LeberThailand
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Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
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TC Erciyes UniversityTerminatedPolycystic Kidney, Autosomal DominantTurkey
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University of Colorado, DenverMayo Clinic; National Institute of Diabetes and Digestive and Kidney Diseases...RecruitingOverweight and Obesity | Autosomal Dominant Polycystic KidneyUnited States
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Regional Hospital HolstebroCompletedPolycystic Kidney, Autosomal DominantDenmark
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Alexandria UniversityCompleted
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Mayo ClinicHopital du Sacre-Coeur de MontrealRecruitingAutosomal Dominant Polycystic Kidney Disease | Nephrogenic Diabetes Insipidus | Acquired Nephrogenic Diabetes Insipidus | Congenital Nephrogenic Diabetes InsipidusUnited States
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Azienda Ospedaliero-Universitaria Consorziale Policlinico...Institute of Biomembranes, Bioenergetics and Molecular Biotechnologies; Istituti... and other collaboratorsCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD) | IgA Nephropathy (IgAN) | Diabetic Kidney Disease (DKD) | Advanced-Chronic Kidney Disease (CKD)Italy
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Hannover Medical SchoolBoehringer IngelheimNot yet recruitingAutosomal Dominant Polycystic Kidney
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National Medical Research Center for Therapy and...Moscow State University of Medicine and DentistryRecruitingMedication Adherence | Adherence, Medication | Treatment Adherence | Familial Hypercholesterolemia | Motivational Interviewing | Adherence, Patient | Treatment Adherence and Compliance | Patient Compliance | Adherence | Hypercholesterolemia, Familial | Patient Adherence | Hypercholesterolemia, Autosomal Dominant and other conditionsRussian Federation
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ShireNational Institutes of Health (NIH)CompletedAutosomal Dominant Hypocalcemia (ADH)United States
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Chaitanya Hospital, PuneUnknown
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National Institute of Allergy and Infectious Diseases...TerminatedAutosomal-dominant Hyper-IgE SyndromeUnited States
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University of Colorado, DenverCompletedPolycystic Kidney, Autosomal Dominant | Polycystic Kidney Disease, AdultUnited States
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Assistance Publique - Hôpitaux de ParisMinistry of Health, FranceCompletedAutosomal Dominant Hypocalcemia OR Primary Hypoparathyroidism Related to Other Cause But Complicated by Hypercalciuria Under TreatmentFrance
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University Hospital, MontpellierMinistry of Health, FranceCompletedAutosomal Dominant Retinitis PigmentosaFrance
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney, Autosomal DominantUnited States
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States
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Neurophth Therapeutics IncActive, not recruitingLeber Hereditary Optic Neuropathy (LHON)United States
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)United States, United Kingdom, Spain, Poland, Austria, Belgium, Bulgaria, Germany, Italy, Portugal
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)Belgium, Netherlands, France, Germany, Norway, United Kingdom, Italy
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Wake Forest University Health SciencesCompleted
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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Wuhan Neurophth Biotechnology Limited CompanyRecruitingLeber's Hereditary Optic Neuropathy (LHON)China
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Medical College of WisconsinTerminatedLeber's Hereditary Optic Neuropathy (LHON)United States
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University Hospital, AngersUnknownLeber Hereditary Optic NeuropathyFrance
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Santhera PharmaceuticalsWithdrawnLeber's Hereditary Optic Neuropathy