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Clinical Trials on Barth Syndrome
Total 55401 results
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National Cancer Institute (NCI)Active, not recruitingSoft Tissue Sarcoma | Osteosarcoma | Ewing Sarcoma | Malignant Glioma | Ependymoma | Rhabdoid Tumor | Advanced Malignant Solid Neoplasm | Refractory Malignant Solid Neoplasm | Rhabdomyosarcoma | Recurrent Malignant Solid Neoplasm | Recurrent Neuroblastoma | Refractory Neuroblastoma | Refractory Non-Hodgkin Lymphoma and other conditionsUnited States, Puerto Rico
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National Cancer Institute (NCI)TerminatedHIV Infection | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma | Recurrent Adult Lymphoblastic Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular... and other conditionsUnited States
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University of EdinburghRecruitingMyocarditis | Hypertrophic Cardiomyopathy | Cardiac Sarcoidosis | Heart Failure With Preserved Ejection Fraction | Hypertensive Heart Disease | Arrhythmogenic Right Ventricular Cardiomyopathy 1 | Tako Tsubo CardiomyopathyUnited Kingdom
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Qilu Hospital of Shandong UniversityRecruitingFabry Disease | Hypertrophic Cardiomyopathy | Left Ventricular HypertrophyChina
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University of California, San DiegoNew York University; Heinrich-Heine University, Duesseldorf; Universität TübingenRecruitingGenetic Disease | Mitochondrial Encephalomyopathies | Neonatal Encephalopathy | Mutation | Hereditary Spastic Paraplegia | White Matter Disease | Spastic ParaplegiaUnited States
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, United Kingdom
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Western Sydney Local Health DistrictRecruitingVentricular Tachycardia | Cardiomyopathy, Dilated | Heart Disease Structural Disorder | Sarcoidosis | Cardiomyopathy, Hypertrophic | Cardiomyopathy, Familial | Cardiomyopathy Ischemic | Arrhythmogenic Right Ventricular Cardiomyopathy 1 | Arrhythmogenic Left Ventricular CardiomyopathyAustralia
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Vascular Therapies, Inc.RecruitingEnd Stage Renal Disease | ESRD | End Stage Kidney Disease | Arteriovenous Fistula | Vascular Access Complication | Chronic Kidney Failure | Complication of Hemodialysis | Complication of Renal DialysisUnited States, United Kingdom
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University of AlbertaRecruitingParkinson Disease | Brain Tumor | Neuroendocrine Tumors | Lewy Body Disease | Neuroblastoma | Congenital HyperinsulinismCanada
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Mayo ClinicRecruitingChronic Kidney Diseases | Transplant | Neurogenic Bladder | Bladder Outlet Obstruction | Bladder Dysfunction | Bladder Exstrophy | Bladder Absence | Posterior Urethral Valve | Failure, KidneyUnited States
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University of California, San FranciscoDuke UniversityRecruitingWolman Disease | MPS IVA | Pompe Disease Infantile-Onset | Gaucher Disease, Type 2 | MPS VI | MPS I | Gaucher Disease, Type 3 | MPS II | Mps VIIUnited States
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University Hospital, MontpellierRecruiting
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National Cancer Institute (NCI)RecruitingSarcoma | Neuroblastoma | Retinoblastoma | Renal Cancer | Endocrine TumorsUnited States
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National Cancer Institute (NCI)CompletedFamilial Ovarian Cancer | Familial Breast Cancer | BRCA1-associate Malignancies | BRCA2-associated MalignanciesUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingUndifferentiated Pleomorphic Sarcoma | Recurrent Undifferentiated Pleomorphic Sarcoma | Dedifferentiated Liposarcoma | Resectable Dedifferentiated Liposarcoma | Resectable Undifferentiated Pleomorphic Sarcoma | Recurrent Dedifferentiated LiposarcomaUnited States
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Washington University School of MedicineCompletedDoxorubicin With Upfront Dexrazoxane for the Treatment of Advanced or Metastatic Soft Tissue SarcomaSoft Tissue Sarcoma | Sarcoma, Soft Tissue | Leiomyosarcoma | Fibrosarcoma | Liposarcoma | Angiosarcoma | Malignant Peripheral Nerve Sheath Tumor | Synovial Sarcoma | Undifferentiated Pleomorphic Sarcoma | Epithelioid Sarcoma | MyxofibrosarcomaUnited States
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University Hospital, ToulouseActive, not recruitingCerebral Amyloid AngiopathyFrance
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ActelionCompleted
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Vtesse, LLC, a Mallinckrodt Pharmaceuticals CompanyWithdrawnNiemann-Pick Disease, Type C
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IpsenCompletedCerebral Palsy | Cervical Dystonia | Muscle Spasticity | Cerebrovascular Accident | Equinus Deformity | Hemifacial Spasm | Blepharospasm | Spasmodic Torticollis | Facial Hyperdynamic LinesFrance, Germany, Russian Federation
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University of South FloridaUniversity of Miami; National Institutes of Health (NIH); University of KansasCompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia
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University of North Carolina, Chapel HillVitrolife; XVIVO PerfusionTerminatedBronchiectasis | Emphysema | Pulmonary Fibrosis | Cystic Fibrosis | Alpha-1 Antitrypsin Deficiency | Pulmonary Hypertension | Chronic Obstructive Pulmonary Disease (COPD) | SarcoidosisUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedSarcoma | Kidney Cancer | Brain and Central Nervous System Tumors | Retinoblastoma | Liver CancerUnited States
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Ludwig-Maximilians - University of MunichUnknownIschemic Stroke | Cerebral Amyloid Angiopathy | Intracerebral HemorrhageGermany
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Failure | Coronary Disease | Pulmonary Hypertension | Peripheral Artery Disease | Dilated Cardiomyopathy | Renal Artery Stenosis | Diabetes and Heart FailureUnited States
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DePuy InternationalWithdrawnOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral Fractures
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DePuy InternationalTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral FracturesUnited Kingdom
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Université de SherbrookeUnknownPathologic Processes | Respiratory Tract Infections | Respiratory Tract Diseases | Pneumonia | Hemorrhage | Bronchiectasis | Mycobacterium Infections | Signs and Symptoms, Respiratory | Lung Cancer | Tuberculosis | Lung Disease | Bronchitis | Pulmonary Embolism | Arteriovenous Fistula | Signs and Symptoms | Pulmonary Hemorrhage and other conditionsCanada
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National Cancer Institute (NCI)CompletedSarcoma | Lymphoma | Kidney Cancer | Leukemia | Neutropenia | Neuroblastoma | Infection | Fever, Sweats, and Hot FlashesUnited States
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Case Comprehensive Cancer CenterNational Cancer Institute (NCI)CompletedPain | Lymphoma | Leukemia | Fatigue | Small Intestine Cancer | Cancer Survivor | Anxiety Disorder | Psychosocial Effects of Cancer and Its Treatment | Lymphoproliferative Disorder | Long-term Effects Secondary to Cancer Therapy in AdultsUnited States
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SanofiPulse Infoframe Ltd.RecruitingNiemann-Pick Diseases | Acid Sphingomyelinase DeficiencyUnited States
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Chinese University of Hong KongHong Kong Children's Hospital; Hong Kong Young Women's Christian AssociationRecruitingGastrointestinal Diseases | Vascular Diseases | Urologic Diseases | Neurodevelopmental Disorders | Autism Spectrum Disorder | Cleft Lip and Palate | Attention Deficit Hyperactivity Disorder | Developmental DelayHong Kong
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SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)RecruitingGangliosidoses | Galactosialidosis | Sialidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Morquio B Disease | Gm2-Gangliosidosis, Variant B1 | GM2 Activator DeficiencyGermany
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King's College Hospital NHS TrustKing's College LondonCompletedLiver Failure | Cancer | Asthma | Renal Failure | Cystic Fibrosis | Chronic Heart Failure | Sickle Cell Disease | Interstitial Lung Disease | COPD | Dyspnea | Post COVID-19 | Bronchiectasis AdultUnited Kingdom
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Duke UniversityNational Cancer Institute (NCI)CompletedBurkitt Lymphoma | Retinoblastoma | Diffuse Large B-cell LymphomaTanzania
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Oslo University HospitalUniversity of Oslo; Ullevaal University Hospital; University Hospital, AkershusWithdrawnMicrocephaly | Hearing Loss | Mental Retardation | ChorioretinitisNorway
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CENTOGENE GmbH RostockTerminatedDeafness | Immunodeficiency | Mental Retardation | Gingival Hypertrophy | Skeletal Abnormalities | Facial DysmorphismGermany, Switzerland
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CENTOGENE GmbH RostockCompletedScoliosis | Muscular Atrophy | Duchenne Muscular Dystrophy | Lordosis | Muscular Weakness | Increased Lordosis/Scoliosis | Hyporeflexia | Red-Green Color BlindnessEgypt, India, Albania, Pakistan, Georgia, Lebanon, Romania, Sri Lanka
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Medical University of WarsawCompletedLiver Diseases | Liver Failure | Graves Ophthalmopathy | Graves Disease | Acute Liver Failure | Acute Liver Injury | Liver Dysfunction | Glucocorticoids Toxicity | Liver Injury | Liver Insufficiency | Acute Liver Injury, Drug Induced | Methylprednisolone Adverse Reaction | Dysthyroid Orbitopathy | Dysthyroid Ophthalmopathy
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI); Duke University; Vitrolife; XVIVO...CompletedBronchiectasis | Emphysema | Pulmonary Fibrosis | Cystic Fibrosis | Alpha-1 Antitrypsin Deficiency | Pulmonary Hypertension | Chronic Obstructive Pulmonary Disease (COPD) | SarcoidosisUnited States
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Alison WalkerCompletedRecurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Del(5q) | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13;q22) | Adult Acute Myeloid Leukemia With t(8... and other conditionsUnited States
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McGill University Health Centre/Research Institute...CompletedFamilial Dysautonomia | Tay Sachs Disease | Canavan DiseaseCanada
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DePuy InternationalTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Nonunion of Femoral FracturesSouth Africa
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DePuy InternationalCompletedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral FracturesSlovakia
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DePuy InternationalTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral FracturesCzech Republic
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DePuy InternationalTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral FracturesUnited Kingdom, Italy
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DePuy InternationalTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Traumatic Femoral Fractures | Nonunion of Femoral FracturesChina, Hong Kong, Italy, Korea, Republic of, New Zealand
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Vanderbilt UniversityNational Cancer Institute (NCI)WithdrawnSarcoma | Kidney Cancer | Leukemia | Solid Tumor | Brain and Central Nervous System Tumors | Neuroblastoma | Liver Cancer
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)WithdrawnExtranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma and other conditionsUnited States
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/Phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada