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Clinical Trials on Bile Acid Malabsorption in New Zealand
Total 311 results
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OncoC4, Inc.Avance Clinical; OncoC4 AU Pty LtdRecruitingMelanoma | Renal Cell Carcinoma | Cervical Cancer | Hepatocellular Carcinoma | Gastric Cancer | Colorectal Cancer | Esophageal Cancer | Fallopian Tube Cancer | Non Small Cell Lung Cancer | Bile Duct Cancer | Bladder Cancer | Endometrial Cancer | Head and Neck Squamous Cell Carcinoma | Anal Cancer | Primary Peritoneal... and other conditionsAustralia
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Target PharmaSolutions, Inc.Active, not recruitingBiliary Cirrhosis, PrimaryUnited States
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Intercept PharmaceuticalsTerminatedLiver Cirrhosis, BiliaryUnited States, Spain, Canada, United Kingdom, France, Germany, Austria, Netherlands
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Mirum Pharmaceuticals, Inc.Active, not recruitingProgressive Familial Intrahepatic Cholestasis (PFIC)United States, Argentina, France, Singapore, United Kingdom, Belgium, Turkey, Austria, Brazil, Canada, Colombia, Germany, Italy, Lebanon, Mexico, Poland
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Elevation OncologyActive, not recruitingSarcoma | Kidney Cancer | Breast Cancer | Head and Neck Cancer | Colorectal Cancer | Pancreatic Cancer | Esophageal Cancer | Ovarian Cancer | Lung Cancer | Prostate Cancer | Cholangiocarcinoma | Bile Duct Cancer | Bladder Cancer | Metastatic Solid Tumor | Gallbladder Cancer | Uterine Cancer | Locally Advanced Solid TumorUnited States, Korea, Republic of, Australia, Canada
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)Italy, United States, Argentina, France, Singapore, United Kingdom, Austria, Brazil, Mexico, Lebanon, Germany, Turkey, Poland, Belgium, Canada, Colombia, Hungary
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Michael Pulsipher, MDRecruiting
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
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Instituto Bioclon S.A. de C.V.University of Arizona; Universidad Nacional Autonoma de MexicoCompleted
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BioMarin PharmaceuticalApproved for marketing
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BioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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CymaBay Therapeutics, Inc.TerminatedPrimary Biliary Cirrhosis (PBC)Germany, United States, Canada, United Kingdom, Poland
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Center Trials & TreatmentOleg MartynenkoTerminatedCOVID-19 | SARS-CoV-2 | Furin | RGMc Processing | Paired Basic Amino Acid Cleaving Enzyme (PACE)India, United States, Ukraine
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Axcella Health, IncCompletedSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | To Assess the Safety and Tolerabiltiy of an Amino Acid Composition in Subjects With Sickle Cell Disease | Sickle Cell DisordersUnited States
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Novartis PharmaceuticalsCompletedPrimary Biliary CholangitisUnited States, Germany, Russian Federation, Canada, United Kingdom, Poland
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GenfitCompletedPrimary Biliary Cholangitis (PBC)United States, United Kingdom, France, Germany, Spain
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Cytonet GmbH & Co. KGTerminatedUrea Cycle DisordersUnited States, Canada
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Tricida, Inc.CompletedMetabolic AcidosisUnited States, Bulgaria, Croatia, Georgia, Hungary, Serbia, Slovenia, Ukraine
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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IpsenActive, not recruitingPrimary Biliary CirrhosisUnited States, France, Spain, Belgium, Germany, Switzerland, Brazil, United Kingdom, Argentina, Canada, Chile, Italy, South Africa, Turkey
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National Institute of Allergy and Infectious Diseases...Completed
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Michio HiranoSanthera PharmaceuticalsCompletedMELAS SyndromeUnited States
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AmgenCompletedType II Refractory Celiac Disease (RCD-II) | In-situ Small Bowel T-cell LymphomaSpain, United States, Finland, France, Netherlands
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SynlogicCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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GlaxoSmithKlineCompletedCholestasisUnited States, Australia, France, Spain, Germany, Canada, Japan, United Kingdom, Italy, Poland
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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BioMarin PharmaceuticalCompletedPhenylketonuria | HyperphenylalaninaemiaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Gilead SciencesTerminatedPrimary Biliary CholangitisUnited States, Canada, Austria, United Kingdom
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Elicio TherapeuticsActive, not recruitingColorectal Cancer | Ovarian Cancer | Cholangiocarcinoma | Bile Duct Cancer | Non-small Cell Lung Cancer | Pancreatic Ductal Adenocarcinoma | Minimal Residual Disease | Gallbladder Carcinoma | KRAS G12D | KRAS G12R | NRAS G12D | NRAS G12RUnited States
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Johnson & Johnson Pharmaceutical Research & Development...CompletedMalabsorption Syndromes | Cystic Fibrosis | Steatorrhea | Exocrine Pancreatic InsufficiencyUnited States, Canada
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BioMarin PharmaceuticalCompleted
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Mirum Pharmaceuticals, Inc.RecruitingPrimary Biliary Cholangitis | PBCUnited States, United Kingdom, Israel, Germany, Italy, France
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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Travere Therapeutics, Inc.Active, not recruiting
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Uta Lichter-KoneckiMedical College of Wisconsin; Children's National Research InstituteCompletedUrea Cycle Disorders | Organic AcidemiasUnited States
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
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Arcturus Therapeutics, Inc.Active, not recruitingOrnithine Transcarbamylase DeficiencyUnited States
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
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Mirum Pharmaceuticals, Inc.Clinigen, Inc.Approved for marketingAlagille SyndromeUnited States
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Aeglea BiotherapeuticsTerminatedHomocystinuria Due to Cystathionine Beta-Synthase DeficiencyUnited States, United Kingdom, Australia
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Homology Medicines, IncTerminated
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EndoStim Inc.TerminatedGastroesophageal Reflux | Reflux, Gastroesophageal | Gastroesophageal Reflux Disease (GERD) | Acid RefluxUnited States, Belgium, Netherlands, United Kingdom
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia