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Clinical Trials on Birt-Hogg-Dube Syndrome in New Zealand
Total 846 results
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Merck Sharp & Dohme LLCActive, not recruitingPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)United States, Australia, Brazil, Italy, United Kingdom
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Neurocrine BiosciencesCompletedTourette SyndromeUnited States
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Dana-Farber Cancer InstituteNovartis PharmaceuticalsCompletedTuberous Sclerosis Complex | TSC1 | TSC2 | MTORUnited States
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Kedrion S.p.A.CompletedPrimary Immunodeficiency DiseaseUnited States
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University of CologneCompletedTransient Tachypnoea of the NewbornGermany
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Beth Israel Deaconess Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)CompletedAcute Respiratory Distress SyndromeUnited States, Canada
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Soleno Therapeutics, Inc.Active, not recruitingPrader-Willi SyndromeUnited States, United Kingdom
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Chiesi Farmaceutici S.p.A.CompletedRespiratory Distress Syndrome, NewbornUnited States
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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Mirum Pharmaceuticals, Inc.Clinigen, Inc.Approved for marketingAlagille SyndromeUnited States
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Barbara J. CoffeyCompletedTourette's DisorderUnited States
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Massachusetts General HospitalCompletedSepsis | Critical Illness | Respiratory Failure | Acute Respiratory Distress SyndromeUnited States
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVATaiwan, United States, Italy, United Kingdom
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...Unknown
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Austria, Netherlands, Portugal
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NYU Langone HealthTourette Association of AmericaCompleted
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NICHD Neonatal Research NetworkEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsTerminatedRespiratory Insufficiency | Pulmonary Hypertension | Respiratory Distress Syndrome, Newborn | PrematurityUnited States
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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TakedaRecruiting
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Yale UniversityUniversity of South Florida; New York University; Icahn School of Medicine at... and other collaboratorsCompleted
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Children's Hospital Medical Center, CincinnatiRecruitingHypoplastic Left Heart Syndrome (HLHS)United States, United Kingdom, Canada
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National Heart, Lung, and Blood Institute (NHLBI)CompletedLung Diseases | Respiratory Distress Syndrome, AdultUnited States, Canada
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NICHD Neonatal Research NetworkNational Center for Research Resources (NCRR)CompletedSepsis | Respiratory Distress Syndrome, Newborn | Bronchopulmonary Dysplasia | Respiration, Artificial | Infant, Small for Gestational Age | Infant, Premature | Infant, Low Birth Weight | Infant, NewbornUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedSecondary Acute Myeloid Leukemia | Childhood Acute Erythroleukemia (M6) | Childhood Acute Megakaryocytic Leukemia (M7) | Childhood Acute Monoblastic Leukemia (M5a) | Childhood Acute Monocytic Leukemia (M5b) | Childhood Acute Myeloblastic Leukemia With Maturation (M2) | Childhood Acute Myeloblastic... and other conditionsUnited States, Canada, Australia, Puerto Rico
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Columbia UniversityRecruitingImmune Deficiency | Allergic Inflammation | Immune Dysregulation DisorderUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMedulloblastoma | Nevoid Basal Cell Carcinoma Syndrome | Desmoplastic/Nodular Medulloblastoma | Medulloblastoma With Extensive NodularityUnited States, Canada, Puerto Rico, Australia
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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Windtree TherapeuticsNational Heart, Lung, and Blood Institute (NHLBI)CompletedRespiratory Distress SyndromeUnited States
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Indian Council of Medical ResearchKing George's Medical University; Lady Hardinge Medical College; Postgraduate... and other collaboratorsCompletedRecurrence | Anti-bacterial Agents | Neonatal SEPSIS | Infant, NewbornIndia
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Northwell HealthFeinstein Institute for Medical Research; BioSymetricsCompleted
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UNC Lineberger Comprehensive Cancer CenterNational Cancer Institute (NCI)RecruitingLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Unspecified Adult Solid Tumor, Protocol Specific | Multiple Myeloma and Plasma Cell Neoplasm | Cognitive/Functional Effects | Lymphoproliferative Disorder | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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Verily Life Sciences LLCActive, not recruitingCOVID-19 | Acute Respiratory Distress SyndromeUnited States
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John Jay High SchoolUnknownNeurofibromatosis Type 1United States
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Novartis PharmaceuticalsCompletedHealthy Volunteers | Atopic Dermatitis | Netherton SyndromeNetherlands, United States
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ACADIA Pharmaceuticals Inc.RecruitingHyperphagia in Prader-Willi SyndromeUnited States, Canada, United Kingdom
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Anthera PharmaceuticalsCompletedSickle Cell Disease | Acute Chest Syndrome | Vaso-occlusive CrisisUnited States
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Baxalta now part of ShireCompletedPrimary Immunodeficiency Diseases (PID) | Immune Thrombocytopenic Purpura (ITP) | Kawasaki SyndromeUnited States
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Johns Hopkins UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAnhydramnios | Potter Syndrome | Lung Hypoplasia | Multicystic Dysplastic Kidney | Multicystic Renal Dysplasia, Bilateral | Lower Urinary Tract Obstructive Syndrome | Fetal Renal AnomalyUnited States
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Baxalta now part of ShireCompleted
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Unity Health TorontoCanadian Institutes of Health Research (CIHR); University of Toronto; Applied...RecruitingARDSFrance, Canada, Chile, Italy, Argentina, Spain, United States
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Soleno Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, United Kingdom
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NYU Langone HealthRecruitingMLH1 Gene Mutation | RAD51C Gene Mutation | BRIP1 Gene Mutation | MSH6 Gene Mutation | PMS2 Gene Mutation | BRCA-Mutated Ovarian Carcinoma | MSH2 A636P | EPCAMUnited States
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI)WithdrawnLymphoma | Myelodysplastic Syndromes | Leukemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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Ultragenyx Pharmaceutical IncActive, not recruitingAngelman SyndromeUnited States, United Kingdom, Canada, Australia, France, Germany, Spain, Israel
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Sequenom, Inc.PRA Health SciencesCompletedPregnancy | Down Syndrome | Aneuploidy | Edwards SyndromeUnited States, France
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage I Kidney Wilms Tumor | Stage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Adult Kidney Wilms Tumor | Beckwith-Wiedemann Syndrome | Childhood Kidney Wilms Tumor | Diffuse Hyperplastic Perilobar Nephroblastomatosis | Rhabdoid Tumor of the Kidney | Stage V Kidney...United States, Canada, Australia, New Zealand, Puerto Rico, Israel
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St. Justine's HospitalCompletedAcute Respiratory Distress Syndrome | Acute Lung InjuryFrance, Switzerland, Austria, United States, Spain, Canada, Belgium, Germany, Italy, Netherlands, Sweden, United Kingdom
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Neurocrine BiosciencesCompletedTourette SyndromeUnited States
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, Netherlands, United Kingdom, Germany