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- US Clinical Trials Registry
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Clinical Trials on Brain Metabolism in Canada
Total 5256 results
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University of British ColumbiaVitaflo International, LtdUnknown
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ShireTerminated
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University of British ColumbiaRare Disease Foundation, Vancouver, Canada; Saudi Arabian Cultural Bureau,...Completed
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Hamilton Health Sciences CorporationChildren's Hospital of Eastern Ontario; McMaster Children's Hospital; BioMarin...CompletedPhenylketonuria | HyperphenylalaninemiaCanada
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University of British ColumbiaRare Disease Foundation, Vancouver, CanadaCompleted
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The Hospital for Sick ChildrenBioMarin PharmaceuticalCompletedPhenylketonuria | Mild HyperphenylalaninemiaCanada
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The Hospital for Sick ChildrenCompletedGangliosidoses, GM2 | Tay-Sachs Disease | Sandhoff DiseaseCanada
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The Hospital for Sick ChildrenActelionCompletedGangliosidoses GM2Canada
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Aeglea BiotherapeuticsTerminatedArginase I Deficiency | HyperargininemiaCanada
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McGill University Health Centre/Research Institute...March of DimesCompleted
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Dr. Anupam SehgalTaysha Gene Therapies, Inc.; GlycoNetActive, not recruitingInfantile GM2 Gangliosidosis (Disorder)Canada
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Université de MontréalGenzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseCanada, Russian Federation, Tunisia
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McGill University Health Centre/Research Institute...RecruitingMitochondrial Diseases | Mitochondrial Encephalomyopathy | Mitochondrial Encephalopathy | Mitochondrial DNA Depletion | Mitochondrial Metabolism DisordersCanada
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University of WashingtonCompleted
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University of British ColumbiaMedical University of Graz; Hospital de Clinicas de Porto AlegreUnknownMorquio B Disease | GM1 Gangliosidosis Type IIICanada
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University Health Network, TorontoUniversity of Colorado, Denver; Mayo Clinic; Icahn School of Medicine at Mount... and other collaboratorsRecruiting
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Resverlogix CorpWithdrawn
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M.A.G.I.C. Clinic LTDHanalytics Solutions Inc.RecruitingMitochondrial Diseases | Fabry Disease | Metabolic Disease | Gaucher Disease | Pompe DiseaseCanada
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AVROBIOTerminatedType 1 Gaucher DiseaseUnited States, Canada
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Cytonet GmbH & Co. KGTerminatedUrea Cycle DisordersUnited States, Canada
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University of PennsylvaniaPassage Bio, Inc.RecruitingGM1 GangliosidosisUnited States, Turkey, Brazil, Canada, United Kingdom
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AVROBIOTerminatedGaucher DiseaseUnited States, Canada
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University Health Network, TorontoOzmosis Research Inc.Completed
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Exsar CorporationThe Hospital for Sick Children; NYU Langone Health; University Hospitals Cleveland...WithdrawnG(M2) Ganglioside | Tay-Sachs Disease Ganglioside | Sandhoff Disease GangliosideUnited States, Canada
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ShireCompleted
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The Hospital for Sick ChildrenCompletedZellweger Syndrome | Peroxisome Biogenesis DisordersCanada
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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McGill University Health Centre/Research Institute...CompletedFamilial Dysautonomia | Tay Sachs Disease | Canavan DiseaseCanada
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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The Hospital for Sick ChildrenCompleted
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Pacific Parkinson's Research CentreUniversity of British Columbia; Oregon Health and Science University; University... and other collaboratorsRecruitingParkinson Disease | Gaucher Disease | GBA Gene MutationUnited States, Canada
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States, Turkey, Canada, France, Germany, Italy, United Kingdom
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SynlogicTerminatedPhenylketonuriaUnited States, Canada, Georgia, Turkey
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Canadian Fabry Research ConsortiumNova Scotia Health AuthorityRecruiting
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Université de SherbrookeHospices Civils de LyonCompleted
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Mark BatshawEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsTerminatedUrea Cycle DisordersUnited States, Canada
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Andrea GropmanEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingBrain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Urea Cycle DisordersUnited States, Canada, Germany, Switzerland
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States, Canada
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McGill University Health Centre/Research Institute...Canadian Institutes of Health Research (CIHR)RecruitingZellweger Spectrum DisorderCanada
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InSightecActive, not recruitingParkinson's Disease | Movement Disorders | Tardive Dyskinesia | Dystonia | Essential Tremor | Huntington's Disease | Wilson's Disease | Holmes Tremor | Orofacial DyskinesiasCanada
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Sunnybrook Health Sciences CentreWithdrawnCerebral Amyloid AngiopathyCanada
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, United Kingdom, Bulgaria, Canada, Colombia, India, Israel, Lebanon, Mexico, Russian Federation, Serbia, Tunisia
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Passage Bio, Inc.SuspendedLeukodystrophy, Globoid CellUnited States, Brazil, Netherlands, United Kingdom, Canada, Israel