- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Brain Diseases, Metabolic
Total 380587 results
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ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia
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ProtalixCompleted
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ISU Abxis Co., Ltd.Withdrawn
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Genzyme, a Sanofi CompanyCompleted
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ProtalixCompleted
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University Hospital, Clermont-FerrandUnknown
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Brigham and Women's HospitalGenzyme, a Sanofi CompanyUnknown
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ProtalixCompleted
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Brendan LeeCompleted
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Lumos DiagnosticsAptatek BiosciencesRecruiting
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SanofiRecruiting
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Children's Hospital of Fudan UniversityHedu Biotechnology (Shanghai) Co., LTDRecruiting
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University Hospital, GrenobleRecruitingMetabolic Diseases | PhenylketonuriaFrance
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APR Applied Pharma Research s.a.Recruiting
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University Children's Hospital, ZurichUniversity Children's Hospital Basel; UChildrenVienna; Insel Gruppe AG, University...RecruitingPhenylketonuriasSwitzerland
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University Hospital, LilleNot yet recruiting
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Emory UniversityBioMarin PharmaceuticalRecruitingPhenylketonuriasUnited States
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdJohannes Gutenberg University Mainz; Kreiskliniken ReutlingenCompleted
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Klaus ParhoferTerminated
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Nutricia UK LtdCompletedPKU | TyrosinemiasUnited Kingdom
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BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Spain, United Kingdom, Germany
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Rubius TherapeuticsTerminated
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Ludwig-Maximilians - University of MunichEuropean UnionCompletedPhenylketonuriaGermany, Italy, Spain, United Kingdom
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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SynlogicCompletedHealthy | PhenylketonuriaUnited States
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Assiut UniversityUnknown
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Boston Children's HospitalBrigham and Women's HospitalCompletedPhenylketonuriaUnited States
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Washington University School of MedicineUniversity of Missouri-Columbia; BioMarin PharmaceuticalCompleted
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
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University of Missouri-ColumbiaBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States, Canada
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Emory UniversityAtlanta Clinical and Translational Science InstituteCompleted
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The University of Texas Health Science Center,...BioMarin PharmaceuticalTerminatedPhenylketonuria | HyperphenylalaninemiaUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
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The University of Texas Health Science Center,...BioMarin PharmaceuticalCompleted
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Emory UniversityTerminated
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Merck KGaA, Darmstadt, GermanyCompleted
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BioMarin PharmaceuticalCompleted
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Shoji YanoBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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BioMarin PharmaceuticalApproved for marketing
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BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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NGGT (Suzhou) Biotechnology Co., Ltd.Not yet recruitingPhenylketonurias
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States, Australia
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APR Applied Pharma Research s.a.RecruitingPhenylketonuriasUnited Kingdom
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan