- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Bulbo-Spinal Atrophy, X-Linked
Total 1857 results
-
University of ZurichCompletedLeft Ventricular Noncompaction | Isolated Noncompaction of the Ventricular MyocardiumSwitzerland
-
AvigenThe University of Texas Health Science Center, Houston; Children's Hospital... and other collaboratorsTerminatedHemophilia BUnited States
-
University of MichiganNational Institute on Disability, Independent Living, and Rehabilitation...CompletedSpinal Cord Diseases | Spinal Stenosis | Spinal Cord Injury | Spina Bifida | Syringomyelia | Spinal Neoplasms | Transverse Myelitis | Spinal Cord Involvement | Polio and Post-polio SyndromeUnited States
-
University of AberdeenCompletedType 2 Diabetes Mellitus | Sarcopenia | Metabolic Syndrome XUnited Kingdom
-
University of Roma La SapienzaCompletedCognitive Impairment | Insulin-like Growth Factor 1Italy
-
University of MichiganNational Institute of Dental and Craniofacial Research (NIDCR)Not yet recruitingHealing Wound | Alveolar Bone Loss | Image | Dent Disease | Alveolar; Wound
-
ResMedClinical Trial Center North Hamburg Germany; CRI-The Clinical Research Institute...TerminatedPulmonary Disease, Chronic Obstructive | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Duchenne Muscular Dystrophy | Myotonic Dystrophy | Spinal Cord Injury | Obesity Hypoventilation Syndrome | Kyphoscoliosis | Congenital Central Hypoventilation Syndrome | MyopathiesGermany
-
Chang Gung UniversityCompleted
-
CSL BehringRecruiting
-
CSL BehringRecruiting
-
Institute of Hematology & Blood Diseases HospitalEast China University of Science and TechnologyActive, not recruiting
-
Skane University HospitalIndiana Hemophilia &Thrombosis Center, Inc.; Bioverativ Therapeutics Inc.; Swedish...Active, not recruitingFactor IX DeficiencyUnited States
-
Baxalta now part of ShireCompletedHemophilia BColombia, Bulgaria, Chile, Poland, Romania, Argentina, Brazil, Czechia, Russian Federation, Ukraine
-
Spark TherapeuticsChildren's Hospital of Philadelphia; Royal Prince Alfred Hospital, Sydney,... and other collaboratorsCompleted
-
Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
-
Bio Products LaboratoryCompletedHaemophilia BUnited Kingdom, Poland
-
Bio Products LaboratoryCompletedHaemophilia BPoland, Romania, Russian Federation
-
PfizerCompleted
-
Georgetown UniversitySolstice NeurosciencesCompletedStroke | Brain Injury | Tumor | Spinal Cord Injury (SCI) | Spasticity Secondary to Either a Disorder or TraumaUnited States
-
Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BGermany
-
Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia BUnited States, Italy, Ireland, New Zealand, United Kingdom, Australia, Netherlands, Denmark, Poland, Sweden, France
-
Baxalta now part of ShireCompletedRecombinant Factor VIIa BI (rFVIIa BI) Treatment of Acute Bleeding Episodes Per an On-demand RegimenHemophilia A | Hemophilia BJapan, Russian Federation, Spain, United States, Poland, Romania, Serbia, Taiwan, Ukraine
-
BayerCompletedHemophilia A; Hemophilia BIsrael
-
Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedErythropoietic Protoporphyria | EPP | X-linked Protoporphyria | XLPUnited States
-
Novo Nordisk A/SCompletedHaemophilia A | Haemophilia BUnited States
-
Dana-Farber Cancer InstituteBrigham and Women's HospitalCompletedHemophilia A | Hemophilia BUnited States
-
Centre Hospitalier Universitaire de Saint EtiennePfizer; Ecole Normale Supérieure des Mines de Saint-EtienneCompletedHaemophilia A | Haemophilia BFrance
-
Affiliated Hospital of Guangdong Medical UniversityNot yet recruitingHemophilia B Without Inhibitor
-
PfizerRecruitingHemophilia A | Hemophilia BDenmark, Taiwan, Canada, Turkey, Spain, China, United Kingdom, South Africa, Italy, Saudi Arabia, Israel, Korea, Republic of, Austria, Germany, Japan, Australia, India, Slovakia, France, United States, Brazil, Argentina
-
ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BSpain, Taiwan, United Kingdom, Italy, Germany, United States, South Africa, Australia, Poland, Armenia, France, India, Canada, Brazil, Turkey, Egypt
-
Goethe UniversitySociety for Thrombosis and Haemostasis Research (Germany)RecruitingHemophilia A | Hemophilia B | Children | Drug Specific AntibodiesGermany
-
PfizerCompleted
-
Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedHemophilia BUnited States, United Kingdom, South Africa, Netherlands, Ireland, Australia
-
The Hospital for Sick ChildrenCompletedHemophilia A | Hemophilia BCanada, Brazil
-
Leigh R. Hochberg, MD, PhD.National Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Dysarthria | Brain Stem Infarctions | Locked in Syndrome | AnarthriaUnited States
-
Holland Bloorview Kids Rehabilitation HospitalThe Hospital for Sick Children; University of Toronto; University of Ottawa; Social... and other collaboratorsCompletedCerebral Palsy | Muscular Dystrophy | Physical Disability | Spinal Cord Injury | Spina Bifida | Juvenile ArthritisCanada
-
University of KansasCompletedStroke | Multiple Sclerosis | Cerebral Palsy | Arthritis | Muscular Dystrophy | Amputation | Spinal Cord Injury | Spina BifidaUnited States
-
Zhejiang UniversityNot yet recruitingHemophilia B Without Inhibitor
-
Hasan Kalyoncu UniversityNot yet recruitingHemophilia B | Hemophilia | Hemophilia A, SevereTurkey
-
ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia B | Hemophilia B With InhibitorUnited States, Spain, Australia, Taiwan, France, United Kingdom, Italy, Turkey, Armenia, India, Germany
-
Yuzuncu Yıl UniversityHasan Kalyoncu University; University of Gaziantep; Acıbadem Adana HospitalRecruiting
-
PfizerActive, not recruitingHemophilia BGermany, United Kingdom, Canada, Australia, Taiwan, Japan, France, Turkey, Korea, Republic of, United States, Brazil, Greece, Saudi Arabia, Sweden
-
PfizerActive, not recruitingHemophilia A | Hemophilia BUnited States, Spain, Canada, China, Korea, Republic of, Hong Kong, Serbia, Taiwan, Turkey, France, Oman, Saudi Arabia, Japan, India, South Africa, Mexico, Croatia, Italy, Bulgaria, Russian Federation
-
Novo Nordisk A/SEnrolling by invitationHaemophilia A | Haemophilia BJapan
-
Assistance Publique - Hôpitaux de ParisUnknown
-
Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, France, Germany
-
Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BFrance, Germany, Italy, Spain, Sweden, Belgium, United Kingdom
-
TiumBio Co., Ltd.RecruitingHemophilia A | Hemophilia B | Blood Coagulation DisordersKorea, Republic of
-
Assistance Publique - Hôpitaux de ParisCompletedHypohidrotic Ectodermal DysplasiaFrance