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Clinical Trials on Bulbo-Spinal Atrophy, X-Linked
Total 1859 results
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Federal Research Institute of Pediatric Hematology...UnknownChronic Granulomatous DiseaseRussian Federation
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National Institute of Allergy and Infectious Diseases...Terminated
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University Hospital, GrenobleTerminatedChronic Granulomatous DiseaseFrance
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous DiseaseUnited States
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Leigh R. Hochberg, MD, PhD.National Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Dysarthria | Brain Stem Infarctions | Locked-in Syndrome | AnarthriaUnited States
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Netherlands, United States, Germany
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Assistance Publique - Hôpitaux de ParisCompleted
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University of Colorado, DenverCompletedChronic Granulomatous DiseaseUnited States
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Radboud University Medical CenterCompletedChronic Granulomatous DiseaseNetherlands
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Federal Research Institute of Pediatric Hematology...CompletedChronic Granulomatous DiseaseRussian Federation
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StemCells, Inc.CompletedPelizaeus-Merzbacher DiseaseUnited States
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Universidad del AzuayCompletedHemophilia A | Hemophilia B | Von Willebrand DiseaseEcuador
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University of ZurichGoethe UniversityCompletedChronic Granulomatous DiseaseSwitzerland
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University of CalgaryInternational Collaboration on Repair DiscoveriesUnknownSpinal Cord Injuries | Autonomic Dysreflexia | Orthostatic Hypotension, DysautonomicCanada
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Jiangsu Gensciences lnc.RecruitingHemophilia | Hemophilia A With Inhibitor | Male | Hemophilia B With InhibitorChina
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Baxalta now part of ShireTerminatedHemophilia A | Hemophilia B | Bone Mineral DensityUnited States
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Children's Hospital of Fudan UniversityTerminated
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Helixmith Co., Ltd.UnknownChronic Granulomatous DiseaseKorea, Republic of
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Baylor College of MedicineCompletedChronic Granulomatous DiseaseUnited States
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Seoul National University HospitalUnknownChronic Granulomatous DiseaseKorea, Republic of
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous DiseaseUnited States
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Johann Wolfgang Goethe University HospitalGerman Federal Ministry of Education and ResearchUnknown
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Assistance Publique - Hôpitaux de ParisRecruitingAdrenoleukodystrophy | Adrenomyeloneuropathy | Metachromatic Leukodystrophy | Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaFrance
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Masonic Cancer Center, University of MinnesotaTerminatedSickle Cell Disease | Thalassemia | Cerebral Adrenoleukodystrophy | Inherited Metabolic Disorders | High Risk Hematologic DisordersUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...CompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Hemophagocytic Lymphohistiocytosis (HLH) | Non Hodgkins Lymphoma | Familial Hemophagocytic Lymphohistiocytosis (FLH) | Viral-associated Hemophagocytic Syndrome (VAHS) | X-linked Lymphoproliferative...United States
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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University College, LondonRecruitingOrnithine Transcarbamylase DeficiencyUnited Kingdom
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous DiseaseUnited States
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BSweden, Finland, Denmark
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National Cancer Institute (NCI)CompletedDyskeratosis Congenita | Telomere Biology DisordersUnited States
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Spark TherapeuticsCompletedHematologic Diseases | Hemophilia A | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Blood Coagulation Disorder | Factor VIII DeficiencyUnited States, Australia, Thailand, Canada
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Arcturus Therapeutics, Inc.Active, not recruitingOrnithine Transcarbamylase DeficiencyUnited States
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Catalyst BiosciencesCompletedHemophilia A With Inhibitor | Hemophilia B With InhibitorArmenia, Georgia, South Africa, Poland, Russian Federation
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CSL BehringTerminatedHemophilia A With Inhibitors | Hemophilia B With InhibitorsGeorgia, Italy, Malaysia, Russian Federation, South Africa, Spain, Thailand, Ukraine, United Kingdom
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The Hospital for Sick ChildrenCanadian Hemophilia SocietyCompletedHemophilia A | Hemophilia B | Factor IX Deficiency | Factor VIII DeficiencyCanada
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Karolinska University HospitalKarolinska Institutet; The Swedish Society of MedicineUnknownHemophilia A | Hemophilia B | Von Willebrand's DiseaseSweden
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StemCells, Inc.CompletedPelizaeus-Merzbacher Disease | PMDUnited States
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Virginia Commonwealth UniversityCSL BehringCompletedHemophilia A | Hemophilia B | Vitamin D DeficiencyUnited States
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Assistance Publique - Hôpitaux de ParisTerminatedNephrolithiasis | Dent's DiseaseFrance
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Turkish Society of Pediatric Gastroenterology,...CompletedDuchenne Muscular Dystrophy | Pompe Disease (Late-onset)Turkey
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease | CGDUnited States
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Region StockholmKarolinska InstitutetRecruitingBipolar Disorder | Bipolar Depression | Bipolar I Disorder | Bipolar II Disorder | Bipolar Affective Disorder; Remission in | Bipolar Affective Disorder, Currently Depressed, ModerateSweden
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Sanguine BiosciencesTerminatedChronic Granulomatous DiseaseUnited States
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Arcturus Therapeutics, Inc.CompletedOrnithine Transcarbamylase DeficiencyNew Zealand
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Freeline TherapeuticsCompletedHemophilia B | Blood Coagulation Disorders, Inherited | Blood Coagulation Disorder | Haematologic DiseaseUnited States, United Kingdom, Australia, Netherlands, Austria, France, Ireland, Italy, Turkey, Canada, Germany, South Africa
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Catalyst BiosciencesTerminatedHemophilia A With Inhibitor | Hemophilia B With InhibitorUnited States, United Kingdom, Taiwan, Italy, Spain, India, Turkey, Malaysia, Russian Federation, Armenia, Georgia, Hungary, Mexico, Poland, South Africa, Ukraine
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Novo Nordisk A/SCompletedHaemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BFrance, United States, India, Mexico, United Kingdom, Netherlands, Sweden, Korea, Republic of, Spain, Switzerland, Serbia, Turkey, Bulgaria, Italy, Japan, Poland, South Africa, Croatia, Algeria, Australia, Bosnia and Herzegovina, ... and more