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Clinical Trials on CDKL5 Deficiency Disorder in United Kingdom
Total 63287 results
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Newcastle UniversityBill and Melinda Gates Foundation; Institute of Nutrition of Central America... and other collaboratorsUnknownVitamin A Deficiency | Vitamin A Toxicity | Hypervitaminosis AGuatemala, United Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingChronic Kidney Diseases | Hyperphosphatemia | Chronic Kidney Disease-Mineral and Bone Disorder | Pediatric Kidney Disease | CKD-MBDUnited Kingdom
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University of BathUniversity of NottinghamActive, not recruitingAdiposity | Metabolic Disturbance | Fasting | Energy Supply; DeficiencyUnited Kingdom
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Ultragenyx Pharmaceutical IncCompletedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD) | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine Palmitoyltransferase (CPT II) Deficiency | Longchain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) DeficiencyUnited States, United Kingdom
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Mayo ClinicArizona State UniversityCompletedPregnancy | Autistic Disorder | Folic Acid DeficiencyUnited States
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Alnylam PharmaceuticalsTerminatedZZ Type Alpha-1 Antitrypsin Deficiency Liver DiseaseUnited Kingdom
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Adnan SharifActive, not recruitingPhysical Activity | Hemodialysis Complication | Nutritional DeficiencyUnited Kingdom
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Liverpool John Moores UniversityAlliance for Potato Research and EducationCompletedEnergy Supply; Deficiency | Energy Balance | Energy AvailabilityUnited Kingdom
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University College, LondonRecruitingOrnithine Transcarbamylase DeficiencyUnited Kingdom
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Sheffield Teaching Hospitals NHS Foundation TrustCompletedAcquired Immune Deficiency Syndrome VirusUnited Kingdom
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Wirral University Teaching Hospital NHS TrustCompletedMeasures to Increase the Effectiveness of Fast Track Colorectal Clinics for Iron Deficiency Anaemia.Colorectal CancerUnited Kingdom
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Vitaflo International, LtdCompletedDeficiency of MicronutrientsUnited Kingdom
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Imperial College LondonTerminatedHereditary Haemorrhagic TelangiectasiaUnited Kingdom
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Rhythm Pharmaceuticals, Inc.CompletedLeptin Receptor Deficiency ObesityNetherlands, Germany, United Kingdom, Canada, France, Réunion
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Great Ormond Street Hospital for Children NHS Foundation...UnknownX-linked Severe Combined ImmunodeficiencyUnited Kingdom
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Rocket Pharmaceuticals Inc.Enrolling by invitationLeukocyte Adhesion DeficiencySpain, United States, United Kingdom
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St George's, University of LondonBill and Melinda Gates Foundation; York HospitalsTerminatedHIV Infections | Acquired Immune Deficiency SyndromeUnited Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States, Israel, United Kingdom
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedRett Syndrome | CDKL5 Disorder | MECP2 Duplication dIsorder | FOXG1 SyndromeUnited States
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University of EdinburghNHS LothianWithdrawnBronchiectasis | Immunoglobulin Subclass DeficiencyUnited Kingdom
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Imperial College LondonNovo Nordisk A/SCompletedFatty Liver | Growth Hormone, RecombinantUnited Kingdom
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University of OxfordBritish Heart Foundation; National Institute for Health Research, United KingdomCompletedPulmonary Arterial Hypertension | Iron Deficiency | Lung HypoxiaUnited Kingdom
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Royal Surrey County Hospital NHS Foundation TrustCompletedColorectal Cancer | Sarcopenia | Surgery | Surgery--Complications | Surgical Site Infection | Nutritional Deficiency | Complication, Postoperative | Infected Wound | Phagocytic DysfunctionUnited Kingdom
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University Hospital Southampton NHS Foundation...Royal Marsden NHS Foundation Trust; University College London Hospitals; Cambridge... and other collaboratorsUnknownCOVID | Infection | Immune Deficiency | Immune Suppression | Children, AdultUnited Kingdom
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Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSevere Combined Immunodeficiency, X-LinkedUnited Kingdom
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Bio Products LaboratoryCompletedFactor X DeficiencyUnited Kingdom
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Tameside General HospitalCompletedCOVID-19 | Vitamin D DeficiencyUnited Kingdom
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingSuccinic Semialdehyde Dehydrogenase DeficiencyUnited States, United Kingdom, Germany, Spain
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National Heart and Lung InstituteWexham Park Hospital; 4th Military HospitalUnknownHeart Diseases | Anemia, Iron-Deficiency | Chronic Heart FailurePoland, United Kingdom
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University of California, San FranciscoCompletedVitamin D Deficiency | AutismUnited States
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University of NottinghamNottingham University Hospitals NHS Trust; Action for A-TCompleted
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Kemin Foods LCDSM Nutritional Products, Inc.Terminated
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rEVO BiologicsCompletedAntithrombin Deficiency, CongenitalFrance, United Kingdom, Germany, United States, Sweden, Italy
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Liverpool Women's NHS Foundation TrustUniversity of California, Davis; University of LiverpoolRecruitingPreterm | Nutritional Deficiency | Immune System and Related DisordersUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...Recruiting
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Ultragenyx Pharmaceutical IncCompletedCarnitine Palmitoyltransferase (CPT I or CPT II) Deficiency | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Long-chain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine-acylcarnitine Translocase (CACT) DeficiencyUnited States, United Kingdom
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HealthCore-NERIBayer; Besins HealthcareCompletedMale Hypogonadism | Testosterone Deficiency | Androgen DeficiencyItaly, United Kingdom, Spain, Netherlands, Germany, Sweden
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Bio Products LaboratoryCompletedPrimary or Secondary Antibody DeficiencyUnited Kingdom
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Institute of Child HealthGreat Ormond Street Hospital for Children NHS Foundation TrustCompletedAtaxia Telangiectasia (AT)United Kingdom
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The Christie NHS Foundation TrustTerminatedSevere Adult Growth Hormone DeficiencyUnited Kingdom
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Leiden University Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; Horizon...RecruitingSevere Combined Immunodeficiency Due to RAG1 DeficiencySpain, Netherlands, Italy, Poland, Australia, Turkey, United Kingdom
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Sidney Kimmel Comprehensive Cancer Center at Johns...RecruitingPrimary Immune Deficiency Disorder | Bone Marrow Failure | Immune Deficiency DiseaseUnited States
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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Johns Hopkins All Children's HospitalRecruitingMetabolic Disease | Primary Immune Deficiency DisordersUnited States
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Novo Nordisk A/SCompletedGrowth Hormone Disorder | Growth Hormone Deficiency in ChildrenIsrael, Denmark, Belgium, Spain, Macedonia, The Former Yugoslav Republic of, Turkey, United Kingdom, France, Slovenia, Czech Republic
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University of LiverpoolPfizerUnknownGrowth Hormone DeficiencyUnited Kingdom
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Wave Life Sciences Ltd.RecruitingAlpha-1 Antitrypsin DeficiencyUnited Kingdom
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Guy's and St Thomas' NHS Foundation TrustKing's College London; Newcastle University; University of CambridgeCompletedXeroderma PigmentosumUnited Kingdom