Clinical Trials on Carnitine Palmitoyltransferase II Deficiency in Belgium

Total 3 results

  • Centre Hospitalier Universitaire de Liege
    Sanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaborators
    Recruiting
    Baby Detect : Genomic Newborn Screening
    Congenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditions
    Belgium
  • Genzyme, a Sanofi Company
    Completed
    Safety and Efficacy Evaluation of Repeat neoGAA Dosing in Late Onset Pompe Disease Patients.
    Pompe Disease | Glycogen Storage Disease Type II (GSD II) | Acid Maltase Deficiency
    United States, Belgium, Denmark, France, Germany, Netherlands, United Kingdom
  • Genzyme, a Sanofi Company
    Recruiting
    Pompe Pregnancy Sub-Registry
    Pompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Glycogenesis 2 Acid Maltase Deficiency
    Croatia, United States, Italy, Belgium, Czechia

Sponsors and Collaborators

Medical Conditions

Drug Interventions

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CROs in South Korea

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Rare Diseases

Drug Interventions

Dietary Supplements

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