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Clinical Trials on Carnitine Palmitoyltransferase I Deficiency
Total 150 results
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Université de SherbrookeInstitut de Recherches Cliniques de MontrealRecruitingLipoprotein Lipase DeficiencyCanada
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University of Colorado, DenverCompletedLipoprotein Lipase Deficiency
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis I | Mucopolysaccharidosis VI | Mannosidosis | Mucolipidosis Type II (I-cell Disease)United States
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University of CatanzaroUnknownAndrogen Receptor Abnormal | Insulin-Like Growth Factor I Deficiency | Insulin Receptor, Defect inItaly
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National Institute of Neurological Disorders and...Recruiting
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Genzyme, a Sanofi CompanyCompletedCerebroside Lipidosis Syndrome | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease Type I | Clucocerebrosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States
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Amsterdam Molecular TherapeuticsThe Clinical Trial CompanyUnknown
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Catabasis PharmaceuticalsCompletedHypertriglyceridemia | Hyperlipoproteinemia Type I | Lipoprotein Lipase Deficiency, Familial | Chylomicronemia, FamilialCanada
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Dr. Loges & Co. GmbHBioTeSys GmbHCompletedEndothelial Dysfunction | Hyperhomocysteinemia | Hypertension Grade I, Subgroup "Borderline" (WHO)Germany
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University of Alabama at BirminghamNational Institutes of Health (NIH); Mereo BioPharmaCompletedEmphysema or COPD | Alpha-1 Antitrypsin Deficiency (AATD) | Pi*ZZ, Pi*SZ, Pi*Null, Another Rare Phenotype/Genotype Known to be Associated With Either Low or Functionally Impaired AAT Including F or I MutationsUnited States
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National Institute of Neurological Disorders and...CompletedTropical Spastic Paraparesis | Spinal Cord Disease | HTLV-I InfectionUnited States
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NYU Langone HealthDyax Corp.WithdrawnHereditary Angioedema Types I and IIUnited States
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CSL BehringParexelCompletedHereditary Angioedema Types I and IIUnited States, Germany
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Germany, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
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CSL BehringCompletedHereditary Angioedema Types I and IIBulgaria, Hungary, Poland, Romania
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CSL BehringCompletedHereditary Angioedema Types I and IIGermany
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
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UniQure Biopharma B.V.CompletedLipoprotein Lipase Deficiency | Familial Hyperlipoproteinemia Type 1 | Familial HyperchylomicronemiaGermany
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Children's Memorial Health Institute, PolandDepartment of Internal Medicine, Hypertension and Vascular Diseases, The...Not yet recruitingGlucose 6 Phosphatase DeficiencyPoland
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Cliniques universitaires Saint-Luc- Université...UnknownGlucose 6 Phosphatase Deficiency | Glycogen Storage Disease Type IBelgium
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University of WashingtonNational Cancer Institute (NCI)CompletedPain | Arthralgia | Stage I Breast Cancer | Stage II Breast Cancer | Stage IIIA Breast Cancer | Stage IIIB Breast Cancer | Stage IIIC Breast Cancer | Recurrent Breast Cancer | Musculoskeletal ComplicationsUnited States
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ANRS, Emerging Infectious DiseasesNot yet recruiting
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Stealth BioTherapeutics Inc.Active, not recruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial Complex I Deficiency | Mitochondrial Pathology | Mitochondrial DNA Depletion | Mitochondrial DNA Mutation | Mitochondrial DNA Deletion | Mitochondrial Metabolism DefectSpain, United States, Italy, Netherlands, Australia, Germany, Hungary, New Zealand, Norway, United Kingdom
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development...WithdrawnUrea Cycle Disorders, Inborn | Inborn Errors of Metabolism | Propionic Acidemia | Methylmalonic Acidemia | Carbamyl Phosphate Synthetase Deficiency
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Vir Biotechnology, Inc.Bill and Melinda Gates FoundationCompletedHIV I InfectionUnited States
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1United States, Canada, Germany, Israel, Italy, South Africa, Spain, United Kingdom, Brazil, France, Netherlands
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1Canada
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ViiV HealthcareGlaxoSmithKlineTerminatedInfection, Human Immunodeficiency Virus IUnited States, Canada, Puerto Rico
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ViiV HealthcareGlaxoSmithKlineCompleted
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ViiV HealthcareGlaxoSmithKline; ShionogiCompletedInfection, Human Immunodeficiency Virus IUnited States, Spain, Germany, Australia, Canada, Belgium, Denmark, Netherlands, United Kingdom, France, Italy, Romania
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ViiV HealthcareGlaxoSmithKlineCompletedInfection, Human Immunodeficiency Virus IUnited States, Spain, Canada, Russian Federation, Romania, Belgium, South Africa
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Hospices Civils de LyonTerminatedSelection of Farnesoid X Receptor (FXR) Ligands on the Reactivation of Latent HIV Proviruses (FXR#2)Human Immunodeficiency Virus I InfectionFrance
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Fred Hutchinson Cancer CenterUniversity of WashingtonCompleted
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GlaxoSmithKlineCompletedInfection, Human Immunodeficiency Virus I
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ViiV HealthcareGlaxoSmithKlineCompletedInfection, Human Immunodeficiency Virus I
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Vancouver Infectious Diseases CentreUnknownDrug Use | Human Immunodeficiency Virus I InfectionCanada
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Université Catholique de LouvainCliniques universitaires Saint-Luc- Université Catholique de LouvainCompletedHuman Immunodeficiency Virus I InfectionBelgium
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ViiV HealthcareGlaxoSmithKline; ShionogiCompletedInfection, Human Immunodeficiency Virus IGermany, Spain, France, Australia, United States, Canada, United Kingdom, Italy, Russian Federation
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ViiV HealthcareGlaxoSmithKlineCompletedInfection, Human Immunodeficiency Virus IUnited States, Puerto Rico
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ViiV HealthcareGlaxoSmithKlineWithdrawnInfection, Human Immunodeficiency Virus IUnited States
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Nova Southeastern UniversityNational Institute of Mental Health (NIMH)CompletedHuman Immunodeficiency Virus I InfectionUnited States
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MRC/UVRI and LSHTM Uganda Research UnitInternational AIDS Vaccine InitiativeRecruitingAcute Human Immunodeficiency Virus Type I InfectionUganda
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Shenzhen Immuno Cure Biomedical Company LimitedShenzhen Third People's HospitalActive, not recruitingHuman Immunodeficiency Virus | Human Immunodeficiency Virus I InfectionChina
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CENTOGENE GmbH RostockWithdrawnLipoprotein Lipase Deficiency | Inborn Error of Lipid Metabolism | Corneal ArcusGermany, India, Sri Lanka
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University of Texas Southwestern Medical CenterCure SPG50RecruitingMicrocephaly | Spasticity, Muscle | Growth Retardation | Intellectual Deficiency | SPG50 | Spastic ParaplegiaUnited States
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Institut National de la Santé Et de la Recherche...RecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multiple Sulfatase Deficiency Disease | Mucopolysaccharidosis IXFrance
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ViiV HealthcareTerminatedHIV Infection | Infection, Human Immunodeficiency Virus IUnited States, France, Canada, Germany, Italy, Belgium, United Kingdom, Portugal, Spain
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GlaxoSmithKlineCompletedHIV Infection | Infection, Human Immunodeficiency Virus IGermany, Belgium, United Kingdom, Spain, Ireland, Italy, France, Austria, Denmark, Netherlands, Switzerland, Portugal, Latvia