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Clinical Trials on Cartilage-hair Hypoplasia
Total 2528 results
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Washington University School of MedicineIsotrace TechnologiesCompletedBreast Cancer | Head and Neck Cancer | Diffuse Large B-cell LymphomaUnited States
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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University Hospital, ToursTerminatedAsthma | Mucoviscidosis | Bronchopulmonary Ignition | Condensate of Exhaled AirFrance
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Rocket Pharmaceuticals Inc.UnknownFanconi Anemia Complementation Group AUnited States
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Children's Hospital Medical Center, CincinnatiAmgenCompleted
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Rocket Pharmaceuticals Inc.Enrolling by invitationFanconi Anemia | Fanconi Anemia Complementation Group ASpain
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Children's Hospitals and Clinics of MinnesotaM.D. Anderson Cancer Center; Washington University School of Medicine; Dana-Farber... and other collaboratorsRecruitingNeuroblastoma | Thyroid Carcinoma | Pineoblastoma | Wilms Tumor | Embryonal Rhabdomyosarcoma | Ovarian Sarcoma | Sertoli-Leydig Cell Tumor | Pleuropulmonary Blastoma | Gynandroblastoma | DICER1 Syndrome | Cystic Nephroma | Renal Sarcoma | Nodular Hyperplasia of Thyroid | Nasal Chondromesenchymal Hamartoma | Ciliary Body... and other conditionsUnited States
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Peking University Cancer Hospital & InstituteUnknownPerformance of White Light, NBI and Iodine Staining Endoscopy in the Diagnosis of Esophageal LesionsEsophageal Squamous Cell Carcinoma | Mild Dysplasia of Esophagus | Moderate Dysplasia of Esophagus | Severe Dysplasia of Esophagus | Carcinoma in Situ of EsophagusChina
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Jason Robert GotlibCelgene CorporationTerminatedLeukemia | Anemia | Myelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML)United States
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Cambridge University Hospitals NHS Foundation TrustActive, not recruitingGiant Cell Arteritis | Polyarteritis Nodosa | Takayasu Arteritis | Cryoglobulinemic Vasculitis | IgA Vasculitis | Cogan Syndrome | Relapsing Polychondritis | Cutaneous Polyarteritis Nodosa | Primary Angiitis of Central Nervous SystemUnited Kingdom
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedFanconi Anemia | Severe Aplastic AnemiaUnited States
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China Medical University HospitalUnknownBronchopulmonary Dysplasia | Extremely Premature Infants | Severe BPD That Conventional Therapies Has Failed | No Severe Congenital Anomalies | no Severe IVH Neither Cystic PVLTaiwan
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Fundacion para la Investigacion Biomedica del Hospital...University of Alcala; Hospital Universitario Ramon y Cajal; Instituto de Salud... and other collaboratorsRecruitingPolycystic Ovary Syndrome | Hyperandrogenism | Type 1 Diabetes | Hirsutism | Oligomenorrhea | Ovulation DisorderSpain
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMultiple Myeloma | Waldenstrom Macroglobulinemia | Leukemia, Lymphocytic, Chronic, B-Cell | Leukemia, Hairy Cell | Lymphoma, Mantle-cellUnited States
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Hospital Universitario La PazHospital Universitario La Princesa; Hospital Privado de ComunidadCompletedLung Diseases | Pediatric Disorder | Atelectasis | Lung Collapse | Atelectasis Without Respiratory Distress Syndrome | Atelectases, Resorption | Air TestSpain, Argentina
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University of Southern CaliforniaKaiser PermanenteCompletedObesity | Physical Activity | Insulin Resistance | Genetics | Air Pollution | Gestational Diabetes | Nutrition | Diabetes Type 2 | Adipokines | Beta Cell Function
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Dana-Farber Cancer InstituteRecruitingObesity | Endometrial Carcinoma | Endometrial Cancer Stage I | Endometrial Intraepithelial Neoplasia | EINUnited States
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States, United Kingdom, Germany
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Hospital Clinic of BarcelonaNot yet recruitingBronchopulmonary Dysplasia | Prematurity | Respiratory Distress Syndrome in Premature Infant
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University of British ColumbiaRecruitingHip Dislocation, Congenital | Congenital Hip Dysplasia | Congenital Dysplasia of the Hip | Congenital Hip Dislocation | Hip Dysplasia, Congenital, Nonsyndromic | Congenital Hip Displacement | Dislocation Of Hip, Congenital | Dislocation, Congenital Hip | Displacement, Congenital Hip | Dysplasia, Congenital... and other conditionsCanada
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Brigham and Women's HospitalCVS CaremarkCompletedDepression | Epilepsy | Cardiovascular Disease | Diabetes | Breast Cancer | Parkinson's Disease | Mental Health Disorder | Prostatic Hypertrophy, BenignUnited States
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedFanconi Syndrome | Cystinosis
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Porteus, Matthew, MDRecruiting
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Russian Academy of Medical SciencesBlokhin's Russian Cancer Research CenterRecruitingMelanoma | Nevus | Nevus, Pigmented | Melanoma (Skin) | Mucosal Melanoma | Moles | Dysplastic Nevus Syndrome | Nevus, Blue | Nevus, Spitz | Nevi, Spindle Cell | Nevi, Dysplastic | Mucosal MelanosisRussian Federation
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Fred Hutchinson Cancer CenterNational Heart, Lung, and Blood Institute (NHLBI); Rocket Pharma LimitedTerminated
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Sanguine BiosciencesTerminated
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)Completed
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Assistance Publique - Hôpitaux de ParisCompleted
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Unspecified Adult Solid Tumor, Protocol Specific | Fanconi AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedNeoplasms | Myelodysplastic Syndromes | Hematologic Diseases | Leukemia | Severe Combined Immunodeficiency | Fanconi Anemia | Anemia, Aplastic | Hematopoietic Stem Cell Transplantation
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University of RochesterWithdrawnObstructive Sleep Apnea Syndrome | Hypoplastic Left Heart Syndrome | Single Ventricle PhysiologyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Rigshospitalet, DenmarkCompletedPain, Postoperative | Carcinoma, Non-Small-Cell Lung | Atrial Fibrillation | Postoperative Nausea and Vomiting | Infection | Air LeakageDenmark
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de... and other collaboratorsCompletedFanconi AnemiaSpain
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital Neutropenia | Diamond-blackfan AnemiaUnited States
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University Hospital in KrakowCompletedMicrobial Colonization | Dysbiosis | COVID-19 Respiratory Infection | HAI | VAP - Ventilator Associated PneumoniaPoland
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Children's Hospital Medical Center, CincinnatiRecruiting
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain, United Kingdom
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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Talaris Therapeutics Inc.Duke UniversityWithdrawnAnemia, Sickle Cell | Thalassemia | Beta-Thalassemia | Bone Marrow Failure Syndromes | Diamond-Blackfan Anemia | Alpha-Thalassemia | Complex and Transfusion-dependent HemoglobinopathiesUnited States
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The University of Texas Medical Branch, GalvestonCompletedPremature Birth | Pulmonary Hypertension | Bronchopulmonary Dysplasia | Chronic Lung Disease of Prematurity | Bronchopulmonary Dysplasia Associated Pulmonary HypertensionUnited States
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Boston Children's HospitalTerminatedFanconi Anemia | Dyskeratosis CongenitaUnited States
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Columbia UniversityUnknownSevere Combined Immunodeficiency | Fanconi Anemia | Bone Marrow Failure | OsteopetrosisUnited States