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Clinical Trials on Cerebellar Ataxia Ectodermal Dysplasia
Total 327 results
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Shenzhen Beike Bio-Technology Co., Ltd.The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical... and other collaboratorsUnknown
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University of Sao Paulo General HospitalUnknownCerebellar AtaxiaBrazil
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S. Andrea HospitalAgenzia Italiana del FarmacoCompleted
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BiogenNot yet recruiting
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University of FloridaNational Institutes of Health (NIH); National Center for Advancing Translational... and other collaboratorsRecruiting
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European Friedreich's Ataxia Consortium for Translational...RecruitingFriedreich's AtaxiaAustria, Germany, Italy, Spain, Belgium, Czechia, France, Greece, Ireland, United Kingdom
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Murdoch Childrens Research InstituteCompleted
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Design Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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RWTH Aachen UniversityAssistance Publique - Hôpitaux de ParisWithdrawnFriedreich AtaxiaSpain, Italy, Austria, Germany, United Kingdom, France
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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University of MinnesotaCompleted
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Children's Hospital of PhiladelphiaUniversity of California, Los Angeles; University of FloridaCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Vidara Therapeutics Research LtdCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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PTC TherapeuticsCompletedFriedreich's AtaxiaUnited States
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University Hospital, MontpellierNeurogenetic department, CHU Bordeaux; Genetic Department , CHU Montpellier-France and other collaboratorsUnknown
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IpsenCompleted
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Ralitza GavrilovaCardero Therapeutics, Inc.Completed
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Azienda Policlinico Umberto ICompleted
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University of Colorado, DenverCompleted
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, United Kingdom, Belgium, France, Germany
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, Germany, United Kingdom
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Federico II UniversityFriedreich's Ataxia Research Alliance; Associazione Italiana per la lotta alle...Completed
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University of South FloridaPfizer; Friedreich's Ataxia Research AllianceTerminatedFriedreich's AtaxiaUnited States
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National Human Genome Research Institute (NHGRI)CompletedFriedreich AtaxiaUnited States
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National Institute of Neurological Disorders and...CompletedFriedreich AtaxiaUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingLeukoencephalopathies | Genetic Disease | White Matter Disease | Ataxia, Cerebellar | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate ElevationUnited States
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Second Affiliated Hospital, School of Medicine,...Recruiting
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Johann Wolfgang Goethe University HospitalUnknownGrowth Failure | Ataxia TelangiectasiaGermany
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Friedreich's Ataxia Research AllianceRecruitingFriedreich AtaxiaUnited States, Canada, New Zealand, Australia, France, Austria, Belgium, Brazil, Czechia, Germany, Greece, Ireland, Italy, Spain, United Kingdom, India, Netherlands
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Institut National de la Santé Et de la Recherche...Imagine InstituteRecruiting
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Reata, a wholly owned subsidiary of BiogenAbbVie; Friedreich's Ataxia Research AllianceActive, not recruitingFriedreich AtaxiaUnited States, Australia, Austria, Italy, United Kingdom
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Larimar Therapeutics, Inc.Enrolling by invitationFriedreich AtaxiaUnited States
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Larimar Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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Monash UniversityChildren's Hospital of Philadelphia; McGill University; University of Florida; University... and other collaboratorsActive, not recruitingFriedreich AtaxiaUnited States, Canada, Australia, Brazil, Germany
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Berta AlemanyInstitut d'Investigació Biomèdica de Girona Dr. Josep Trueta; Universitat de... and other collaboratorsCompleted
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IRCCS Eugenio MedeaUniversity of Rome Tor VergataCompleted
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Neurocrine BiosciencesTakedaCompletedFriedreich AtaxiaUnited States
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research AllianceCompleted
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research AllianceCompleted
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Institut National de la Santé Et de la Recherche...Completed
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Larimar Therapeutics, Inc.Children's Hospital of PhiladelphiaCompletedFriedreich AtaxiaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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H. Lundbeck A/SCompletedFriedreich's AtaxiaGermany, Austria, Italy
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Assistance Publique - Hôpitaux de ParisCompletedEffect of Pioglitazone Administered to Patients With Friedreich's Ataxia: Proof of Concept (ACTFRIE)Friedreich's AtaxiaFrance