- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Chromosome Aberrations in United Kingdom
Total 593 results
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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RespireRxFRAXA Research FoundationCompletedFragile X Syndrome | AutismUnited States
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Neuren Pharmaceuticals LimitedCompleted
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Alcobra Ltd.CompletedFragile X SyndromeUnited States, Israel
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Hoffmann-La RocheCompleted
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Ultragenyx Pharmaceutical IncActive, not recruitingAngelman SyndromeUnited States, United Kingdom, Canada, Australia, France, Germany, Spain, Israel
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis PharmaceuticalsCompleted
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingTurner SyndromeUnited States
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Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
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Eunice Kennedy Shriver National Institute of Child...RecruitingAutism Spectrum Disorder | Fragile X Syndrome | Developmental Delay | Genetic Disorder | Asperger DisorderUnited States
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Seaside Therapeutics, Inc.Completed
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Oregon Health and Science UniversityTerminated
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Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Italy, Argentina, France, Spain, Mexico, Canada, New Zealand, Singapore, United Kingdom
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ACADIA Pharmaceuticals Inc.RecruitingHyperphagia in Prader-Willi SyndromeUnited States, Canada, United Kingdom
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Progenity, Inc.UnknownDown Syndrome | DiGeorge Syndrome | Turner Syndrome | Klinefelter Syndrome | Edwards Syndrome | Patau Syndrome | Perinatal InfectionsUnited States
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Soleno Therapeutics, Inc.Active, not recruitingPrader-Willi SyndromeUnited States, United Kingdom
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University of Southern CaliforniaNational Institute on Aging (NIA); Alzheimer's Therapeutic Research Institute; Alzheimer's Clinical Trials ConsortiumRecruitingDementia | Alzheimer Disease | Down SyndromeUnited States, Spain, United Kingdom
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University of Colorado, DenverCompletedMarfan Syndrome | Turner Syndrome | Loeys-Dietz Syndrome | Thoracic Aortic Aneurysm and Dissection Syndromes | Ehlers-Danlos Type IV SyndromeUnited States
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Enrolling by invitationIntellectual Disability | Down Syndrome | Attention Deficit Hyperactivity Disorder | Fragile X SyndromeUnited States
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Novo Nordisk A/SRecruitingTurner Syndrome | Noonan Syndrome | SGA | ISSKorea, Republic of, Malaysia, Netherlands, Spain, United States, Poland
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UMC UtrechtChildren's Hospital of Philadelphia; Netherlands Brain FoundationUnknownChromosome 22q11.2 Deletion SyndromeUnited States, Netherlands
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Noonan Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Adult Growth Hormone Deficiency | Genetic Disorder | Foetal Growth Problem | Small for Gestational AgeIsrael, Saudi Arabia, Spain, Argentina, Russian Federation, Germany, Netherlands, Italy, Belgium, United Kingdom, Slovenia, Ireland, Sweden, Denmark, Hungary, Finland, Norway, France, Czechia, Lithuania, Luxembourg, Serbia, Switzerland
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Novo Nordisk A/SRecruitingSGA, Turner Syndrome, Noonan Syndrome, ISSKorea, Republic of, United States, Ireland, United Kingdom, Finland, France, Netherlands, Japan, Thailand, Belgium, China, Israel, Brazil, India, Portugal, Austria, Bulgaria, Canada, Croatia, Germany, Greece, Malaysia, Poland, Saudi Arabia and more
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Boston Children's HospitalCompletedAngelman SyndromeUnited States
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The Emmes Company, LLCBoston Children's Hospital; Ionis Pharmaceuticals, Inc.CompletedAngelman SyndromeUnited States
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Northwestern UniversityArchieMDCompletedPregnancy | Down SyndromeUnited States
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University of California, DavisUniversity of Alberta; St. Justine's HospitalCompletedNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXS | Mental Retardation, X LinkedUnited States, Canada
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Boston University Charles River CampusBoston Children's HospitalNot yet recruiting
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Eunice Kennedy Shriver National Institute of Child...Recruiting
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Children's Hospital Medical Center, CincinnatiWithdrawn
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Oregon Health and Science UniversityCompletedDown SyndromeUnited States
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University of Puget SoundCompleted
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National Human Genome Research Institute (NHGRI)CompletedHoloprosencephalyUnited States
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National Cancer Institute (NCI)CompletedPrimary Myelofibrosis | Chronic Myelomonocytic Leukemia | Previously Treated Myelodysplastic Syndrome | Recurrent Adult Acute Myeloid Leukemia | Secondary Acute Myeloid Leukemia | Recurrent Disease | Recurrent Adult Acute Lymphoblastic Leukemia | Secondary Myelodysplastic Syndrome | de Novo Myelodysplastic... and other conditionsUnited States, Canada, New Zealand
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Massachusetts General HospitalRecruiting
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University of PittsburghEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDown SyndromeUnited States
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University of Wisconsin, MadisonOffice of the Vice Chancellor for Research and Graduate Education; Wisconsin...Completed
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University of South FloridaCompleted
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Vanda PharmaceuticalsUnknownSmith Magenis SyndromeUnited States
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University of Nevada, Las VegasEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingDown SyndromeUnited States
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University of Nevada, Las VegasCompleted
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HealthPartners InstituteCompleted
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University of MichiganCompleted
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Soleno Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, United Kingdom
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AC Immune SAWorldwide Clinical TrialsRecruitingAlzheimer's Disease | Prodromal Alzheimer's Disease | Amyloid Plaque | Beta-Amyloid | Alzheimer's Disease in Down SyndromeUnited States, Spain, United Kingdom