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Clinical Trials on Complement Deficiencies in United States
Total 1013 results
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St. Louis UniversityCompletedDepression | Amyotrophic Lateral SclerosisUnited States
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University of TennesseeCompletedMultiple Myeloma | Plasma Cell NeoplasmUnited States
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Barrow Neurological InstituteALS AssociationCompleted
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Pharming Technologies B.V.CompletedHereditary AngioedemaIsrael, Italy, United States, Czechia, Germany, Hungary, Poland, Romania, Slovakia, North Macedonia
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UniQure Biopharma B.V.Not yet recruitingAmyotrophic Lateral SclerosisUnited States
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Life Molecular Imaging GmbHpharmtrace klinische Entwicklung GmbHRecruitingAL Amyloidosis | Cardiac Amyloidosis | ATTR AmyloidosisUnited States, Spain, Germany, United Kingdom
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Massachusetts General HospitalALS Association; ALS Finding a CureCompletedCentral Nervous System Diseases | Nervous System Diseases | Sclerosis | Neuromuscular Diseases | Neurodegenerative Diseases | Motor Neuron Disease | Amyotrophic Lateral Sclerosis | Spinal Cord Diseases | ALSUnited States
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National Institute of Neurological Disorders and...Completed
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedMultiple Myeloma and Plasma Cell NeoplasmUnited States
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)Completed
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Johns Hopkins UniversityNational Institute of Nursing Research (NINR); University of ChicagoCompletedPancreatic Cancer | Amyotrophic Lateral Sclerosis | GI CancerUnited States
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Boston Medical CenterTerminatedMultiple Myeloma | Plasma Cell NeoplasmUnited States
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Temple UniversityCompletedMultiple Myeloma and Plasma Cell NeoplasmUnited States
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AMAG Pharmaceuticals, Inc.RecruitingIron Deficiency AnemiaUnited States, Lithuania, Poland
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Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated Amyloidosis | ATTR AmyloidosisIsrael, Italy, Netherlands, Spain, United States, France, Denmark, Germany, Portugal, Brazil, Taiwan
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Mayo ClinicNational Cancer Institute (NCI)Active, not recruitingAmyloidosis | Plasma Cell MyelomaUnited States
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Ascentage Pharma Group Inc.RecruitingMultiple Myeloma | AmyloidosisUnited States
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Knopp BiosciencesCompleted
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Helixmith Co., Ltd.CompletedAmyotrophic Lateral SclerosisUnited States, Korea, Republic of
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CSL BehringCompletedHereditary AngioedemaBulgaria, United States, Poland, Spain, Hungary, United Kingdom, Russian Federation, Macedonia, The Former Yugoslav Republic of, Argentina, Australia, Canada, Czech Republic, Israel, Romania, Sweden
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Massachusetts General HospitalPfizer; Akcea Therapeutics; Alnylam Pharmaceuticals; Eidos Therapeutics, a BridgeBio...RecruitingHeart Failure | Amyloidosis | Heart Failure, Diastolic | Transthyretin AmyloidosisUnited States
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The Cleveland ClinicCompletedAmyloidosis | Transthyretin Amyloidosis | Trigger Finger | Primary Amyloidosis of Light Chain TypeUnited States
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National Institutes of Health Clinical Center (CC)CompletedMotor Neuron Disease | Deglutition DisorderUnited States
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Intellia TherapeuticsActive, not recruitingHereditary AngioedemaFrance, New Zealand, Germany, United Kingdom, Netherlands, Australia
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Sangamo TherapeuticsCompletedAmyotrophic Lateral SclerosisUnited States
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Israel, Netherlands, Spain, United Kingdom, Australia, Germany, South Africa, Slovakia, Austria, New Zealand, Romania, Canada, Japan
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Barbara Ann Karmanos Cancer InstituteBristol-Myers Squibb; National Cancer Institute (NCI); Multiple Myeloma Research...Active, not recruitingRecurrent Primary AmyloidosisUnited States
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GlaxoSmithKlineCompletedAmyotrophic Lateral SclerosisUnited Kingdom, United States, France, Italy
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Ionis Pharmaceuticals, Inc.AstraZenecaRecruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)United States, Austria, Belgium, Canada, France, Germany, Israel, Italy, Portugal, Spain, Sweden, United Kingdom, Australia, Greece
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Eidos Therapeutics, a BridgeBio companyActive, not recruitingAmyloid Cardiomyopathy, Transthyretin-RelatedUnited States, Spain, Australia, Canada, Italy, Netherlands, Ireland, New Zealand, Belgium, Israel, Greece, Korea, Republic of, Czechia, Brazil, Denmark, Portugal, United Kingdom
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | PediatricSpain, Austria, Canada, France, Germany, Israel, Italy, Poland, Romania, United Kingdom
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Ionis Pharmaceuticals, Inc.ALS Association; Muscular Dystrophy AssociationCompletedFamilial Amyotrophic Lateral SclerosisUnited States
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, France, Netherlands, Spain, United Kingdom, Belgium, Bulgaria, Canada, Denmark, Germany, Israel, Italy, Poland, Turkey
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Weill Medical College of Cornell UniversityMuscular Dystrophy AssociationCompletedFamilial Amyotrophic Lateral SclerosisUnited States, Germany, Italy, Sweden
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Australia, Bulgaria, Canada, France, Germany, Greece, Hungary, Israel, Italy, Japan, Netherlands, New Zealand, North Macedonia, Poland, Portugal, Puerto Rico, Romania, Slovakia, Spain, United Kingdom
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TakedaTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, Spain, Netherlands, Hungary, Italy, Canada, Germany, France, Japan, Poland
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Amylyx Pharmaceuticals Inc.CompletedAmyotrophic Lateral SclerosisUnited States
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AZTherapies, Inc.TerminatedAmyotrophic Lateral SclerosisUnited States
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Life Molecular Imaging SACompletedDown Syndrome | Amyloid Beta-proteinUnited States
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Brigham and Women's HospitalBoston University; University of Pennsylvania; University of Michigan; Duke University and other collaboratorsCompletedAlzheimer Disease | Education | Neuroimaging | Risk Assessment | Neuropsychological Tests | Amyloid Beta-PeptidesUnited States
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ShireCompletedHereditary AngioedemaUnited States
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Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Bulgaria, Canada, Hungary, Israel, Italy, Macedonia, The Former Yugoslav Republic of, Poland, Romania, Serbia, South Africa
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Ionis Pharmaceuticals, Inc.RecruitingHereditary AngioedemaUnited States, Puerto Rico, Belgium, Bulgaria, Canada, France, Germany, Israel, Italy, Netherlands, Poland, Spain, Turkey, United Kingdom
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Midwest Heart & Vascular SpecialistsRecruitingAL Amyloidosis | Amyloid | Cardiac Amyloidosis | Amyloidosis Cardiac | Systemic Amyloidosis | ATTR Amyloidosis Wild Type | Infiltrative Cardiomyopathy, AmyloidUnited States
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Duke UniversityCReATe Consortium (funded by NIH/NCATS/NINDS)CompletedAmyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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University of RochesterCompletedLymphoma | Multiple Myeloma | Myelofibrosis | Solid Tumors | Hematological Disease | Immune DeficienciesUnited States
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
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CSL BehringCompletedHereditary AngioedemaUnited States, Germany, Japan, Hungary, Canada, Netherlands, Israel
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ShireDyax Corp.CompletedHereditary Angioedema (HAE)United States, Canada, Germany, Italy, Jordan, Puerto Rico, United Kingdom
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Germany, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom