- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Complement Deficiencies in United States
Total 1024 results
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldCompleted
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CytokineticsCompletedAmyotrophic Lateral SclerosisUnited States
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ShireTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, France, Netherlands, Spain, Hungary, Italy, Canada, Poland, Japan, Germany
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ShireCompletedHereditary AngioedemaUnited States
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Genentech, Inc.Quotient ClinicalCompletedAmyotrophic Lateral SclerosisUnited Kingdom
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US Department of Veterans AffairsNew York State Department of HealthCompletedALS (Amyotrophic Lateral Sclerosis)United States
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Knopp BiosciencesBiogenCompleted
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Denali Therapeutics Inc.Active, not recruitingAmyotrophic Lateral SclerosisUnited States, Netherlands
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Baylor College of MedicinePharmacosmos Therapeutics, Inc.RecruitingAnemia, Iron Deficiency | Uterine BleedingUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingRestless Legs Syndrome | Iron-deficiency | ADHD | Periodic Limb Movement Sleep DisorderUnited States
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Johns Hopkins UniversityNational Institutes of Health (NIH); National Institute on Deafness and Other...CompletedPrimary Progressive Aphasia | MCI | FTDUnited States
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Johns Hopkins UniversitySuspendedStroke | Primary Progressive Aphasia | AphasiaUnited States
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Johns Hopkins UniversityCompletedPrimary Progressive Aphasia | PPAUnited States
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Mayo ClinicNational Cancer Institute (NCI)CompletedMultiple Myeloma and Plasma Cell NeoplasmUnited States
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Anelixis Therapeutics, LLCCompletedAmyotrophic Lateral SclerosisUnited States, Canada
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Massachusetts General HospitalRecruitingAmyotrophic Lateral Sclerosis | Alzheimer Disease | Mild Cognitive ImpairmentUnited States
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HealthPartners InstituteTerminatedFrontotemporal Dementia, Behavioral VariantUnited States
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
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Sheffield Teaching Hospitals NHS Foundation TrustCompleted
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BiogenCompletedAmyotrophic Lateral SclerosisUnited States
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ShireCompletedHereditary Angioedema (HAE)Germany, Spain, United Kingdom, France, Italy, Belgium
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Austria, Czechia, Germany, Hungary, Italy, Netherlands, North Macedonia, Poland, United Kingdom
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CSL BehringActive, not recruitingHereditary AngioedemaAustralia, Canada, United States, New Zealand, Germany, Hong Kong, Netherlands, Taiwan, Czechia, Israel, Hungary, Japan, Russian Federation, Spain
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ShireJerini AGCompletedHereditary AngioedemaSpain, Argentina, Austria, Denmark, France, Germany, Israel, Italy, Switzerland, United Kingdom
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CSL BehringChiltern International Inc.CompletedIncludes: Hereditary AngioedemaUnited States, Denmark, Germany, Switzerland
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Nazem AtassiState University of New York - Upstate Medical University; ALS Therapy AllianceCompletedAmyotrophic Lateral SclerosisUnited States
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PfizerTerminatedHeart Failure With Preserved Ejection Fraction | Transthyretin Amyloid CardiomyopathySpain, United States, Japan, Canada, France, Italy, Poland, United Kingdom
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ShireCompletedHereditary Angioedema (HAE)United States, Canada, Australia, Austria, Colombia, Germany, Hungary, Israel, Italy, Spain
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Mayo ClinicNational Cancer Institute (NCI)CompletedMultiple Myeloma and Plasma Cell NeoplasmUnited States
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University of MichiganEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHealthy | Cerebral Palsy | Amyotrophic Lateral Sclerosis | Spinal Cord Injury | Neuromuscular DiseaseUnited States
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University of PennsylvaniaRecruitingPrimary Progressive AphasiaUnited States
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Johns Hopkins UniversityNational Institute on Aging (NIA)RecruitingPrimary Progressive Aphasia | Logopenic Progressive AphasiaUnited States
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Mayo ClinicActive, not recruitingAmyloidosis | Peripheral Neuropathy | Chronic Inflammatory Demyelinating Polyradiculoneuropathy | Vasculitic Neuropathy (Disorder) | Hereditary Neuropathy | Sarcoid NeuropathyUnited States
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Johns Hopkins UniversityActive, not recruitingPrimary Progressive AphasiaUnited States
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Auerbach Hematology Oncology Associates P CAMAG Pharmaceuticals, Inc.CompletedRestless Legs Syndrome | Iron Deficiency AnemiaUnited States
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NYU Langone HealthCompletedPrimary Progressive AphasiaUnited States
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Columbia UniversityAlzheimer's Drug Discovery FoundationCompletedFrontotemporal Dementia (FTD)United States
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Sherif S. FaragWithdrawnMultiple Myeloma | Amyloidosis | Mucositis | Oral MucositisUnited States
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The Cleveland ClinicCompletedCarpal Tunnel Syndrome | Amyloidosis | Transthyretin Amyloidosis | Cardiomyopathy | Senile Systemic AmyloidosisUnited States
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University of PennsylvaniaCompletedPrimary Progressive AphasiaUnited States
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Cara DonohueWithdrawnRespiration Disorders | Amyotrophic Lateral Sclerosis | Dysphagia | DyspneaUnited States
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Johns Hopkins UniversityWithdrawnDementiaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedMultiple Myeloma and Plasma Cell NeoplasmUnited States
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Eidos Therapeutics, a BridgeBio companyCompletedHeart Diseases | Amyloidosis | Cardiomyopathies | Transthyretin Amyloidosis | Amyloid CardiomyopathyUnited States, Netherlands, Ireland, Canada, Italy, Spain, Belgium, New Zealand, Israel, Australia, Portugal, Brazil, Poland, Czechia, Denmark, Greece, Korea, Republic of, United Kingdom
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University of AlbertaUniversity of British Columbia; McGill University; University of Miami; University... and other collaboratorsRecruitingMotor Neuron Disease | Amyotrophic Lateral SclerosisCanada, United States
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David WilsonRio pharmaceuticals Inc.RecruitingDementia | Alzheimer Disease | Frontotemporal DementiaUnited States
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Tammie L. S. Benzinger, MD, PhDWithdrawn
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ShireCompletedHereditary AngioedemaUnited States
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
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Ionis Pharmaceuticals, Inc.Active, not recruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)United States, Australia, Spain, Canada, Germany, Japan, Italy, Israel, Argentina, France, Portugal, Austria, Brazil, Greece, United Kingdom, Czechia, Sweden, Belgium, Denmark, Poland, Puerto Rico