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Clinical Trials on Congenital Bone Marrow Failure Syndromes in United Kingdom
Total 6968 results
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Elixirgen Therapeutics, Inc.RecruitingBone Marrow Failure | Telomere ShorteningUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Aplastic Anemia | de Novo Myelodysplastic SyndromeUnited States
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David Rizzieri, MDCompletedSickle Cell Anemia | Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic AnemiaUnited States
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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University College, LondonMedical Research CouncilRecruitingLymphoma | Myelodysplastic Syndromes | Leukemia | Myeloma | Graft Vs Host Disease | Severe Aplastic Anemia | Primary Immune DeficiencyUnited Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingModerate Aplastic Anemia | Unilineage Bone Marrow Failure DisordersUnited States
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Henry Ford Health SystemCompletedHematologic Disorders and Bone Marrow Failure, Hematopoietic Stem Cell Transplantation (HSCT) or Cellular Therapy (CART)United States
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St. Bartholomew's HospitalUnknownMyelodysplastic SyndromesUnited Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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Children's Hospital Medical Center, CincinnatiRecruiting
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Amegakaryocytic Thrombocytopenia | Paroxysmal Nocturnal Hemoglobinuria | Shwachman-Diamond Syndrome | Bone Marrow Failure Syndrome | Congenital Pure Red Cell Aplasia | Hereditary Sideroblastic Anemia | Hematologic Neoplasm With Germline GATA2 Mutation | Hematologic Neoplasm With Germline... and other conditionsUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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Oxford University Hospitals NHS TrustUnknownMyelodysplastic Syndromes | LeukemiaUnited Kingdom
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Cellphire Therapeutics, Inc.Department of Health and Human ServicesTerminatedMyelodysplastic Syndromes | Myeloproliferative Disorders | Thrombocytopenia | Hematologic Malignancy | Bone Marrow Aplasia | Platelet RefractorinessUnited States, Israel, Norway
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingMyelodysplastic Syndrome (MDS) | Severe Aplastic Anemia | Hypo-Plastic MDSUnited States
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI); National Institute of Allergy and Infectious... and other collaboratorsRecruitingLymphoma | Leukemia | Aplastic Anemia | Myelodysplastic Syndrome (MDS)United States
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European Society for Blood and Marrow TransplantationGenzyme, a Sanofi CompanyCompletedAplastic AnemiaSwitzerland, United Kingdom, Germany, Italy, France, Saudi Arabia
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Children's Hospital of PhiladelphiaNational Cancer Institute (NCI); University of Pennsylvania; City of Hope Medical... and other collaboratorsRecruitingMyelodysplastic Syndromes | Aplastic Anemia | Lymphoblastic Leukemia | Cancer SurvivorsUnited States
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Mitchell Horwitz, MDGenzyme, a Sanofi CompanyCompletedFailure of Bone Marrow GraftUnited States
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Barts & The London NHS TrustCancer Research UK; AmgenUnknownMyelodysplastic SyndromeUnited Kingdom
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedAplastic Anemia | Immunosuppression | Severe Aplastic Anemia | Bone Marrow FailureUnited States
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Fairview University Medical CenterCompletedMyelodysplastic Syndromes | Leukemia, Lymphocytic, Acute | Fanconi's Anemia | Leukemia, Nonlymphocytic, AcuteUnited States
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Emory UniversityChildren's Healthcare of AtlantaTerminatedSickle Cell Disease | Fanconi Anemia | Thalassemia | Severe Congenital Neutropenia | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Leukocyte Adhesion Deficiency | Dyskeratosis-congenita | Chediak-Higashi Syndrome | Chronic-granulomatous Disease | Schwachman-Diamond...United States
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Silence Therapeutics plcWithdrawnNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic SyndromeUnited Kingdom, Bulgaria
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King's College Hospital NHS TrustCompleted
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA) | Myelodysplastic Syndrome (MDS) With Refractory Anemia (RA)United States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Fanconi Anemia | Thalassemia | Hematologic Malignancies | Immune Deficiency | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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Joanne Kurtzberg, MDMiltenyi Biomedicine GmbHCompletedHematologic Malignancy | Aplastic Anemia | Myelodysplastic Syndrome (MDS)United States
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic Syndromes | Purpura, Thrombocytopenic | Anemia, Aplastic | Red-Cell Aplasia, Pure | Bone Marrow Failure Syndromes | Hemoglobinuria, Paroxysmal | Leukemia, LymphocyticUnited States
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King's College LondonCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited Kingdom
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Fanconi's Anemia | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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University of California, San FranciscoThrasher Research FundCompletedSickle Cell Disease | Hemoglobinopathies | Fanconi Anemia | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Fanconi's Anemia | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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King's College Hospital NHS TrustUnknownMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited Kingdom
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Genzyme, a Sanofi CompanyTerminatedMyelodysplastic Syndrome (MDS)Germany, United Kingdom, France, Netherlands
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedLeukemia | Thrombocytopenia | Fanconi Anemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital Neutropenia | Diamond-blackfan AnemiaUnited States
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King's College Hospital NHS TrustTerminatedMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited Kingdom
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Masonic Cancer Center, University of MinnesotaNational Institutes of Health (NIH)RecruitingFanconi Anemia | Oral Cavity Carcinoma | Alcohol-Related CarcinomaUnited States
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Children's Hospital Medical Center, CincinnatiHoxworth Blood CenterTerminatedBone Marrow Failure | Waning Donor Chimerism | Waning Immune Function | Primary Immunodeficiency Disease(s)United States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingFanconi Anemia | Squamous Cell CarcinomaUnited States
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Celgene CorporationICON Clinical ResearchCompletedMyelodysplastic SyndromesGermany, Israel, United Kingdom, Spain, Belgium, Italy, France, Netherlands, Sweden
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Single Lineage Cytopenias, T-LGL | Hypoplastic MDSUnited States
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European Society for Blood and Marrow TransplantationNovartis; PfizerCompletedSevere Aplastic AnemiaSwitzerland, Netherlands, France, Italy, Spain, United Kingdom
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Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
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M.D. Anderson Cancer CenterTerminatedLeukemia | Aplastic Anemia | Non Hodgkin's LymphomaUnited States
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Emory UniversityCompletedSickle Cell Disease | Fanconi Anemia | Hurler Syndrome | Chronic Granulomatous Disease | Severe Congenital Neutropenia | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Thalassemia Major | Leukocyte... and other conditionsUnited States
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Novartis PharmaceuticalsActive, not recruitingAplastic AnemiaThailand, Russian Federation, Portugal, United Kingdom, Hong Kong, United States