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Clinical Trials on Congenital Bone Marrow Failure Syndromes in United Kingdom
Total 6968 results
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Prof. Janet DunnKing's College Hospital NHS Trust; University of Manchester; University of Birmingham and other collaboratorsRecruitingMyelodysplastic Syndromes (MDS)United Kingdom
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The Cleveland ClinicCompletedAplastic AnemiaUnited States
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M.D. Anderson Cancer CenterCompletedAplastic AnemiaUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)Terminated
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Fred Hutchinson Cancer CenterUniversity of California, Los Angeles; Oregon Health and Science University; Ohio... and other collaboratorsCompletedAnemia, AplasticUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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Medical Research CouncilCompletedMyelodysplastic Syndromes | LeukemiaUnited Kingdom
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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Gilead SciencesCalifornia Institute for Regenerative Medicine (CIRM)CompletedAcute Myeloid Leukemia | Myelodysplastic SyndromeUnited Kingdom
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Radboud University Medical CenterRecruitingMyelodysplastic Syndromes (MDS)Denmark, Switzerland, Serbia, Austria, Croatia, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Romania, Spain, Sweden, United Kingdom
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The Cleveland ClinicAstellas Pharma US, Inc.Terminated
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Mayo ClinicCompletedAnemia, AplasticUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedAplastic AnemiaUnited States
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St. Jude Children's Research HospitalCompleted
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Columbia UniversityCompletedMyelodysplastic Syndromes | Sickle Cell Disease | Aplastic Anemia | Transfusional Iron Overload | Thalassemia MajorUnited States
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital NeutropeniaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Zimmer BiometCompletedBone Marrow Edema | Bone Marrow LesionsGermany, Netherlands, Italy, Spain, United Kingdom
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Roswell Park Cancer InstituteCompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Fanconi Anemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Aplastic AnemiaUnited States
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European Society for Blood and Marrow TransplantationCHUGAI sanofi-aventisTerminatedAplastic AnaemiaFrance, Netherlands, Germany, United Kingdom, Switzerland, Italy, Sweden, Greece, Czechia
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Sidney Kimmel Comprehensive Cancer Center at Johns...RecruitingPrimary Immune Deficiency Disorder | Bone Marrow Failure | Immune Deficiency DiseaseUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Aplastic | Anemia, HypoplasticUnited States
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Relation TherapeuticsBarts & The London NHS Trust; Royal Free Hospital NHS Foundation Trust; Chelsea... and other collaboratorsRecruitingOsteoarthritis | Bone Diseases | Osteoporosis | Bone Marrow Disease | Bone FractureUnited Kingdom
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknown
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CelgeneCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited States, United Kingdom
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Riverside Haematology GroupUnknownMyelodysplastic Syndromes | LeukemiaUnited Kingdom
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National Institute of Environmental Health Sciences...Completed
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Christopher DvorakNo longer availableAcute Myeloid Leukemia | Leukocyte Disorders | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Cytopenias | Immune Deficiency | Lymphomas | Bone Marrow Failure | Osteopetrosis | Hemoglobinopathy | Anemia Due to Intrinsic Red Cell AbnormalityUnited States
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King's College LondonKing's College Hospital NHS TrustUnknownAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Myelodysplastic SyndromeUnited Kingdom
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Wake Forest University Health SciencesTerminatedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Immune Deficiency | Lymphomas | Bone Marrow Failure | Osteopetrosis | HemoglobinopathyUnited States
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Northside Hospital, Inc.RecruitingSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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Barts & The London NHS TrustLiverpool Heart and Chest Hospital NHS Foundation Trust; Aortic Dissection...RecruitingMarfan Syndrome | Marfan Syndrome Cardiovascular ManifestationsUnited Kingdom
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndromes (MDS)United States, Australia, Canada, France, Germany, Italy, United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia, Refractory | Severe Aplastic Anemia, RelapseUnited States
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Benjamin TomlinsonRecruitingMyelodysplastic Syndromes | MDS/MPN Crossover SyndromesUnited States
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Institute of Child HealthNational Institute for Health Research, United Kingdom; Great Ormond Street...CompletedGastrostomy | Stem Cell Transplant Complications | Enteral Feeding Intolerance | Bone Marrow Disease | Gastrostomy Complications | Experiences, LifeUnited Kingdom
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Cardiff UniversityCompleted
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University of Alabama at BirminghamCompletedLymphoma | Leukemia | Myelofibrosis | Myelodysplastic Syndrome | Severe Aplastic Anemia | Allogeneic TransplantUnited States
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Barts & The London NHS TrustLiverpool Heart and Chest Hospital NHS Foundation Trust; Aortic Dissection...CompletedMarfan Syndrome | Marfan Syndrome Cardiovascular ManifestationsUnited Kingdom
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MedImmune LLCCompletedMyelodysplastic SyndromeUnited States, United Kingdom, France, Germany
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Sidney Kimmel Comprehensive Cancer Center at Johns...TerminatedSevere Aplastic AnemiaUnited States
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CelgeneCompletedMyelodysplastic SyndromesItaly, United Kingdom, Germany, Australia, Bulgaria, France, Greece, Hungary, Netherlands, Poland, Spain
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA)United States
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National Institutes of Health Clinical Center (CC)National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA)United States