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Clinical Trials on Congenital Diaphragmatic Hernia in New Zealand
Total 968 results
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Novartis PharmaceuticalsRecruitingSickle Cell Disease (SCD)United States, Germany, Spain, Belgium, Italy, Lebanon, Brazil, Colombia, Oman, Switzerland, Turkey, United Kingdom, Canada, India, France
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University of Alabama at BirminghamCompletedSickle Cell DiseaseUnited States
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Gladwin, Mark, MDNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell DiseaseUnited States, France, Brazil
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Kadmon, a Sanofi CompanyCompletedAutosomal Dominant Polycystic Kidney | ADPKDUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Amegakaryocytic Thrombocytopenia | Paroxysmal Nocturnal Hemoglobinuria | Shwachman-Diamond Syndrome | Bone Marrow Failure Syndrome | Congenital Pure Red Cell Aplasia | Hereditary Sideroblastic Anemia | Hematologic Neoplasm With Germline GATA2 Mutation | Hematologic Neoplasm With Germline... and other conditionsUnited States
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Novartis PharmaceuticalsCompletedAnemia, Sickle CellUnited States
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IcagenCompletedSickle Cell Disease | Sickle Cell AnemiaUnited States
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Sequenom, Inc.RecruitingDown Syndrome | Fetal AneuploidyUnited States, Canada
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Anthera PharmaceuticalsCompletedSickle Cell Disease | Acute Chest Syndrome | Vaso-occlusive CrisisUnited States
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C. R. BardCompletedArteriovenous FistulaUnited States
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CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...RecruitingBeta-ThalassemiaUnited States, Turkey, Italy, Thailand, Germany, Greece, China, India, Lebanon
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TWi Biotechnology, Inc.RecruitingGeneralized Epidermolysis Bullosa SimplexUnited States, Taiwan, Australia, Philippines, Austria, Italy, Poland
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth DiseaseUnited States
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI)TerminatedHemoglobin SC DiseaseUnited States
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Marinus PharmaceuticalsCompletedTuberous SclerosisUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
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PfizerPfizerRecruitingSickle Cell DiseaseUnited States
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States
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Prof. Valérie Mc LinEuropean Society of Pediatric Gastroenterology, Hepatology and Nutrition; European... and other collaboratorsEnrolling by invitationCongenital Porto-Systemic Shunt (CPSS)Spain, United Kingdom, Canada, United States, Netherlands, France, Israel, Germany, Australia, Turkey, Switzerland, Japan, Belgium, Greece, Hungary, India, Italy
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Aldeyra Therapeutics, Inc.CompletedSjogren-Larsson SyndromeUnited States
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Manhattan Eye, Ear & Throat HospitalGenentech, Inc.CompletedPolypoidal Choroidal Vasculopathy | Pseudoxanthoma Elasticum | Pathological Myopia | Retinal Angiomatous Proliferation | Coats' Disease | Idiopathic Retinal Telangiectasia | Multi-focal Choroiditis | Rubeosis Iridis | Von Hippel Lindau Disease | BEST VITELLIFORM MACULAR DYSTROPHY, MULTIFOCAL (Disorder)United States
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Baxter Healthcare CorporationApatech, Inc.TerminatedDegenerative Disc Disease | Spinal Stenosis | Herniated Disc | Cervical Myelopathy | Spinal Cord Neoplasms | Spinal Deformity | Failed Back Surgery Syndrome | SpondylolithesisUnited States, Hungary, Netherlands
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyeloid Proliferations Associated With Down SyndromeUnited States, Canada, Australia, Puerto Rico
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The Radiosurgery SocietyVisionTreeRecruitingNeoplasms | Trigeminal Neuralgia | Arteriovenous Malformation of Central Nervous SystemUnited States, Australia
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Soleno Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, United Kingdom
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Women and Infants Hospital of Rhode IslandSequenom, Inc.CompletedDown Syndrome | Trisomy 21United States, Canada, Israel, Hungary, Ireland, Argentina, Australia, Czech Republic, Italy, Spain
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Soleno Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, United Kingdom
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney, Autosomal DominantUnited States
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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Hoffmann-La RocheRecruitingAngelman SyndromeUnited States, Australia, Spain, Italy, France, Germany
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle Cell | PriapismUnited States
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Progenity, Inc.CompletedDown Syndrome | Aneuploidy | DiGeorge Syndrome | Turner Syndrome | Klinefelter Syndrome | Chromosome Deletion | Edwards Syndrome | Patau SyndromeUnited States
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Novartis PharmaceuticalsCompletedNon-transfusion Dependent ThalassemiaGreece, Taiwan, Italy, United Kingdom, Lebanon, Turkey, Malaysia, Thailand, United States
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BayerCompletedHemophilia A, CongenitalSlovenia, Italy, Germany, France, United States, Belgium, Canada, Colombia, Greece, Luxembourg, Netherlands, Spain, Taiwan
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingTurner SyndromeUnited States
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Zimmer BiometActive, not recruitingOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Patellofemoral Osteoarthritis | Traumatic Arthritis | Varus Deformity | Valgus Deformity | Knee Pain Chronic | Polyarthritis | Flexion Deformity of the KneeUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedHematologic Diseases | Iron Overload | Hypertension, Pulmonary | Osteoporosis | Thalassemia | Beta-Thalassemia | Anemia, Cooley'sUnited States, Canada
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Helsinn Healthcare SAICON Clinical ResearchRecruitingRET-altered Solid Tumors | RET-altered Non Small Cell Lung CancerUnited States, Japan
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingAcute Myeloid Leukemia | Down Syndrome | Myelodysplastic Syndrome | Myeloproliferative Neoplasm | Myeloid Leukemia Associated With Down SyndromeUnited States, Canada, Saudi Arabia, Puerto Rico, Australia, New Zealand
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National Heart, Lung, and Blood Institute (NHLBI)TerminatedSickle Cell Disease | Pulmonary HypertensionUnited States, United Kingdom
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Myelodysplastic/Myeloproliferative NeoplasmsUnited States, Canada, Puerto Rico, Australia, Netherlands, New Zealand, Switzerland
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsFrance, United States, Spain, Brazil, Philippines, South Africa, Poland, Turkey, Romania, Bulgaria, Russian Federation, Argentina
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Novartis PharmaceuticalsCompletedIron Overload | Sickle Cell Disease | Hemolytic AnemiaUnited States, Canada
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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The University of QueenslandRecruitingAutosomal Dominant Polycystic Kidney DiseaseAustralia
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States