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Clinical Trials on Congenital Disorders of Glycosylation in South Africa
Total 391 results
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Center for International Blood and Marrow Transplant...University of PittsburghActive, not recruitingQuality of LifeUnited States
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IpsenCompletedMuscle Spasticity | Cerebrovascular AccidentAustralia
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rEVO BiologicsCompletedAntithrombin Deficiency, CongenitalFrance, United Kingdom, Germany, United States, Sweden, Italy
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingCardiovascular Disease | Williams Syndrome | Supravalvular Aortic StenosisUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AFrance, United States, Switzerland, Malaysia, Brazil, Canada, Japan, United Kingdom, Israel, Portugal, Ukraine, Greece, Lithuania, Puerto Rico, Turkey, Italy
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Marinus PharmaceuticalsRecruitingTuberous Sclerosis ComplexUnited States, Spain, Israel, United Kingdom, Germany, Canada, France, Italy
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AvadelCompletedNarcolepsy | Cataplexy | Excessive Daytime SleepinessUnited States, Germany, Australia, Canada, Czechia, France
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TakedaTakeda Development Center Americas, Inc.CompletedHealthy Volunteers | Narcolepsy Type 1United States
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Novo Nordisk A/SCompletedObesity | Metabolism and Nutrition DisorderFrance, United States, Turkey, Italy, Australia, New Zealand, Canada, Netherlands
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Marinus PharmaceuticalsEnrolling by invitationTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, Australia, China, Italy, Israel, Germany, France, Canada, Belgium
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DT MedTech, LLCRecruitingOsteoarthritis Ankle | Post-Traumatic Osteoarthritis of Ankle | Osteoarthritis of Ankle Secondary to Inflammatory Arthritis (Disorder)United States
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Novartis PharmaceuticalsCompletedTuberous Sclerosis | Subependymal Giant Cell AstrocytomaUnited States, Belgium, Canada, Germany, Italy, Russian Federation, Netherlands, Poland, Australia, United Kingdom
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ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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THERAPIM PTY LTDNovotech (Australia) Pty LimitedTerminatedOvarian Cancer | Fallopian Tube Cancer | Primary Peritoneal Carcinoma | High Grade Serious or Endometrioid Carcinoma of the Ovary, Fallopian Tube, or Primary Peritoneal CancerAustralia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Denmark, Austria, Spain, Japan, Brazil, Algeria, Lithuania, Portugal, Russian Federation, Serbia, Turkey, Greece, Hong Kong, Puerto Rico, Hungary, China, Poland
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Zynerba Pharmaceuticals, Inc.Enrolling by invitationFragile X SyndromeUnited States, United Kingdom, New Zealand, Australia
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Jazz PharmaceuticalsCompletedNarcolepsyUnited States, France, Germany, Switzerland
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Jazz PharmaceuticalsRecruitingTuberous Sclerosis Complex | Dravet Syndrome | Lennox Gastaut SyndromeUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Spain, Australia, France, Thailand, Italy, Malaysia, Austria, Greece, Japan, Taiwan, Canada, Israel, Algeria, Argentina, Bulgaria, Germany, Romania
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Seoul National University HospitalAsan Medical Center; Johannes Gutenberg University Mainz; Gyeongsang National... and other collaboratorsActive, not recruitingIntracerebral Hemorrhage | Cerebral Cavernous MalformationKorea, Republic of
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Axsome Therapeutics, Inc.CompletedNarcolepsy | Excessive Sleepiness | Cataplexy NarcolepsyUnited States
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Sequenom, Inc.RecruitingDown Syndrome | Fetal AneuploidyUnited States, Canada
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AvadelCompletedSleep Wake Disorders | Sleep Disorder | Sleep Disturbance | Narcolepsy | Cataplexy | Excessive Daytime SomnolenceUnited States, Canada
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Switzerland, Germany, Australia, Canada, Denmark, France, Italy, Spain, United Kingdom
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston... and other collaboratorsCompletedPrader-Willi Syndrome | Rett Syndrome | Angelman Syndrome | Sleep ProblemsUnited States
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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Sequenom, Inc.PRA Health SciencesCompletedPregnancy | Down Syndrome | Aneuploidy | Edwards SyndromeUnited States, France
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Ultragenyx Pharmaceutical IncActive, not recruitingAngelman SyndromeUnited States, United Kingdom, Canada, Australia, France, Germany, Spain, Israel
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Royal North Shore HospitalCompleted
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PfizerCompletedNarcolepsy | Excessive Daytime SleepinessUnited States
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Bristol-Myers SquibbRecruitingPsoriasisUnited States, Puerto Rico
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Novartis PharmaceuticalsCompletedTuberous Sclerosis Complex-associated Refractory SeizuresUnited States, Colombia, Belgium, France, Japan, Taiwan, Turkey, Spain, Thailand, Korea, Republic of, Australia, Hungary, United Kingdom, Canada, Norway, Germany, Italy, Russian Federation, Denmark, Argentina, Netherlands, Greece, P... and more
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Oligo Medic Pty LtdMobius Medical Pty Ltd.RecruitingChondral Defect | Articular Cartilage Disorder of Knee | Articular Cartilage DefectAustralia, Canada
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Jazz PharmaceuticalsCompleted
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
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Sydney Children's Hospitals NetworkJohns Hopkins University; Children's Hospital of Philadelphia; University of... and other collaboratorsUnknownCharcot-Marie-Tooth DiseaseUnited States, Australia, Italy
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Massachusetts General HospitalNational Comprehensive Cancer NetworkActive, not recruitingQuality of Life | Non Small Cell Lung Cancer | Coping SkillsUnited States
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Trans Tasman Radiation Oncology GroupNational Health and Medical Research Council, Australia; Canadian Cancer Trials...CompletedEsophagus CancerAustralia, Canada, New Zealand, United Kingdom
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NLS PharmaceuticsCompletedNarcolepsy | Narcolepsy Without Cataplexy | Narcolepsy With CataplexyUnited States
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NLS PharmaceuticsCompletedNarcolepsy | Excessive Daytime Sleepiness | Cataplexy NarcolepsyUnited States
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Millennium Pharmaceuticals, Inc.CompletedA Study of a Single Intravenous Infusion Dose of TAK-925 in Participants With Idiopathic HypersomniaIdiopathic HypersomniaUnited States, Japan
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Evotec Neurosciences GmbHCompletedSleep Initiation and Maintenance DisordersUnited States
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Jazz PharmaceuticalsCompletedNarcolepsy With CataplexyUnited States, Netherlands, France, Italy
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CephalonCompletedExcessive SleepinessUnited States
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Prevail TherapeuticsEli Lilly and CompanyRecruitingFrontotemporal DementiaUnited States, Australia, Belgium, Spain, United Kingdom, France
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Eisai Inc.PfizerTerminated
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Neuren Pharmaceuticals LimitedCompleted
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ISTO Technologies, Inc.TerminatedDefect of Articular Cartilage | Articular Cartilage Disorder | Degeneration; Articular Cartilage | Chronic Cartilage Injury | Acute Cartilage InjuryUnited States