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Clinical Trials on Congenital Muscular Dystrophy Type 1A in United Kingdom
Total 4065 results
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St. Joseph's Hospital and Medical Center, PhoenixTranslational Genomics Research Institute; The Joe Niekro FoundationActive, not recruiting
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Medical College of WisconsinChildren's Hospital and Health System Foundation, WisconsinTerminated
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University College, LondonUniversity College London HospitalsUnknown
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Baylor College of MedicineUnknownHeart Failure | Muscular Dystrophy | Dilated CardiomyopathyUnited States
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Stanford UniversityRecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Abeona Therapeutics, IncCompletedEpidermolysis Bullosa | Recessive Dystrophic Epidermolysis BullosaUnited States
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Castle Creek Biosciences, LLC.Active, not recruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencySpain, United States, Canada, Italy, United Kingdom, Hungary
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Imperial College LondonRecruitingChronic Kidney Diseases | Renal Failure | End Stage Renal DiseasesUnited Kingdom
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University of KansasCompletedStroke | Multiple Sclerosis | Cerebral Palsy | Arthritis | Muscular Dystrophy | Amputation | Spinal Cord Injury | Spina BifidaUnited States
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Medtronic Neurovascular Clinical AffairsMicro Therapeutics Inc.CompletedBrain Arteriovenous MalformationsUnited States
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University of California, San FranciscoCompletedBrain Arteriovenous MalformationUnited States
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A | Haemophilia BUnited Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A | Haemophilia BUnited Kingdom
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Gilead SciencesTerminatedLong QT Syndrome Type 3United States, Germany, Canada, Netherlands, Italy, France, Israel, United Kingdom
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Castle Creek Biosciences, LLC.TerminatedEpidermolysis Bullosa Dystrophica, RecessiveUnited States
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A | Haemophilia BUnited Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A | Haemophilia BUnited Kingdom
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Wake Forest University Health SciencesTerminatedEquinus ContractureUnited States
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Nemours Children's ClinicRecruitingCharcot-Marie-Tooth Disease | Motor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Muscular Atrophy | Neuromuscular Disease | Spinal Muscular Atrophy With Respiratory Distress 1 | Peroneal Muscular AtrophyUnited States
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ProQR TherapeuticsTerminatedEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, United Kingdom
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University of New MexicoCompletedRetinitis Pigmentosa | Age Related Macular Degeneration | Congenital Stationary Night Blindness | ColorblindnessUnited States
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University of AberdeenCompletedType 2 Diabetes Mellitus | Sarcopenia | Metabolic Syndrome XUnited Kingdom
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Abeona Therapeutics, IncRecruitingEpidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | RDEBUnited States
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MD Stem CellsUnknownGlaucoma | Macular Degeneration | Retinal Disease | Hereditary Retinal Dystrophy | Optic Nerve DiseaseUnited States
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National Cancer Institute (NCI)CompletedSkin Diseases | Virus Diseases | Healthy | Retinal Degeneration | Muscular DystrophyUnited States
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Liverpool University Hospitals NHS Foundation TrustWithdrawnDupuytren ContractureUnited Kingdom
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Neurotech PharmaceuticalsCompletedA Study to Determine the Safety and Efficacy of NT-501 in Macular Telangiectasia Type 2 - Protocol AMacular Telangiectasia Type 2United States, United Kingdom, Australia, France
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Hoffmann-La RocheCompleted
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis | Eye Diseases, Hereditary | Retinal Dystrophies | Vision Disorders | Retinal Disease | Autosomal Dominant Retinitis Pigmentosa | Vision TunnelUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited Kingdom, Malaysia
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Johns Hopkins UniversityTerminatedUrinary Incontinence | Bladder ExstrophyUnited States
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Hoffmann-La RocheAssociation Française contre les Myopathies (AFM), ParisCompletedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type III Non AmbulantGermany, Italy, France, Belgium, Poland, Netherlands, United Kingdom
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University of ArkansasGenentech, Inc.RecruitingArteriovenous Malformations (Extracranial)United States
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GlaxoSmithKlineCompletedAtherosclerosisUnited Kingdom
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Boston UniversityNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingBicuspid Aortic Valve Disease | Thoracic Aortic Disease in Patients With a Bicuspid Aortic ValveUnited States, Spain, United Kingdom, Canada, Italy
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University of LeedsMerck Sharp & Dohme LLC; Celgene; AmgenUnknown
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National Institute of Nursing Research (NINR)Completed
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PellePharm, Inc.CompletedBasal Cell Nevus SyndromeUnited Kingdom
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Temple UniversityUnknownDiabetes | Equinus Contracture of the AnkleUnited States
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Manchester University NHS Foundation TrustManchester Metropolitan UniversityCompletedMuscle Weakness | Neurofibromatosis Type 1United Kingdom
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King's College Hospital NHS TrustHemabRecruiting
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King's College Hospital NHS TrustCompleted
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RTI InternationalUniversity of North Carolina, Chapel HillEnrolling by invitationTuberous Sclerosis | Down Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Rett Syndrome | Turner Syndrome | Williams Syndrome | Angelman Syndrome | Chromosome 22q11.2 Deletion Syndrome | Klinefelter Syndrome | Phelan-McDermid Syndrome | Dup15Q Syndrome | Smith Magenis SyndromeUnited States
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University of EdinburghChief Scientist Office of the Scottish GovernmentActive, not recruitingMyocardial Infarction Type 2United Kingdom
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University College, LondonCompleted
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Children's Healthcare of AtlantaTerminated
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Cure CMDUniversity of Chicago; Boston Children's Hospital; Valerion Therapeutics, LLC; Congenital...Completed
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University of NottinghamCompletedTuberous Sclerosis | LymphangioleiomyomatosisUnited Kingdom