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Clinical Trials on Congenital Muscular Dystrophy Type 1A in United Kingdom
Total 4065 results
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Cooperative International Neuromuscular Research...Completed
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterCompleted
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Sarepta Therapeutics, Inc.Completed
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Solid Biosciences Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
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University of Kansas Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedCardiomyopathy | Duchenne Muscular Dystrophy (DMD)United States
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King's College LondonUniversity College, LondonCompletedRecessive Dystrophic Epidermolysis BullosaUnited Kingdom
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsCompletedBecker Muscular Dystrophy | Healthy VolunteerUnited States
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Epirium Bio Inc.CompletedBecker Muscular DystrophyUnited States
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King's College LondonUnknownRecessive Dystrophic Epidermolysis BullosaUnited Kingdom
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Akashi TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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University of FloridaCompleted
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Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
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Processa PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States
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Capricor Inc.Active, not recruiting
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
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Skulpt, Inc.National Institute of Neurological Disorders and Stroke (NINDS)CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States
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Processa PharmaceuticalsTerminated
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Completed
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Washington University School of MedicineUniversity of California, Davis; Nationwide Children's Hospital; University of... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Wake Forest University Health SciencesMuscular Dystrophy AssociationCompletedMuscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)United States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Ohio State UniversityUniversity of Colorado, Denver; University of California, Los Angeles; Vanderbilt... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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Dart Therapeutics. LLCCompletedDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada