- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Congenital Muscular Dystrophy
Total 57690 results
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Rigshospitalet, DenmarkCompletedLimb-girdle Muscular DystrophyDenmark
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, United Kingdom
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Solid Biosciences Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Hoffmann-La RocheSarepta Therapeutics, Inc.Recruiting
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West China HospitalRecruiting
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Hacettepe UniversityNot yet recruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PepGen IncRecruitingDuchenne Muscular DystrophyCanada
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RecruitingDuchenne Muscular DystrophyUnited States
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Beni-Suef UniversityNot yet recruitingDuchenne Muscular Dystrophy
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingStudy of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small MutationsMuscular Dystrophy, DuchenneItaly
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Muş Alparlan UniversityHacettepe UniversityRecruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Medpace, Inc.; SYSNAV; ImagingNMDRecruitingBecker Muscular DystrophyUnited States, Netherlands, United Kingdom
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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Taiho Pharmaceutical Co., Ltd.RecruitingDuchenne Muscular DystrophyJapan
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GenethonRecruiting
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Halic UniversityIstanbul University; Biruni UniversityCompletedDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.Medpace, Inc.CompletedBecker Muscular DystrophyUnited States
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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Sarepta Therapeutics, Inc.Hansa Biopharma ABActive, not recruitingDuchenne Muscular DystrophySpain
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Wave Life Sciences Ltd.Active, not recruitingDuchenne Muscular DystrophyJordan, United Kingdom
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Hacettepe UniversityCompleted
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Çağtay MadenCompleted
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Hacettepe UniversityCompleted
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FibroGenActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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Kevin FlaniganSarepta Therapeutics, Inc.Completed
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Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States
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University Hospital, Basel, SwitzerlandCompletedDuchenne Muscular DystrophyFrance, Spain, Germany, Netherlands, Switzerland, United Kingdom
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Epirium Bio Inc.CompletedBecker Muscular DystrophyUnited States
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Roxanna Marie BendixenTerminatedDuchenne Muscular DystrophyUnited States
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedBecker Muscular DystrophyUnited States
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Hacettepe UniversityCompleted
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Mallinckrodt ARD LLCTerminatedMuscular Dystrophy, DuchenneSpain, Bulgaria, Italy, United States, Mexico, Israel, Serbia, Turkey
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Japan, Italy
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Sarepta Therapeutics, Inc.University College, London; Catholic University of the Sacred Heart; University... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited Kingdom, United States, France, Italy
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Processa PharmaceuticalsTerminated
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Centre d'Investigation Clinique et Technologique...Completed