- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Congenital Myasthenic Syndromes in Australia
Total 1139 results
-
Murdoch Childrens Research InstituteCompletedHeart Defects, Congenital | Hypoplastic Left Heart Syndrome | Pediatric DisorderAustralia
-
NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
-
Regeneron PharmaceuticalsRecruitingGeneralized Myasthenia GravisKorea, Republic of, Japan, Spain, United States, Germany, Italy, Canada, Georgia, India, Belgium, Poland, Taiwan, Australia, Denmark, France, Turkey, Serbia, United Kingdom, Czechia
-
argenxRecruitingGeneralized Myasthenia GravisUnited Kingdom, Spain, United States, Austria, Germany, Belgium, Italy, Netherlands, France, Georgia, Poland, Canada
-
University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
-
argenxActive, not recruitingGeneralized Myasthenia GravisGeorgia, United States, Austria, Belgium, Canada, France, Germany, Italy, Netherlands, Poland, Spain
-
The University of QueenslandRecruitingPulmonary Fibrosis | Dyskeratosis Congenita | Telomere Shortening | Telomere DiseaseAustralia
-
Alexion PharmaceuticalsCompletedRefractory Generalized Myasthenia GravisKorea, Republic of, United States, Spain, Canada, Netherlands, Belgium, Czechia, Denmark, Italy, Australia, Finland, Turkey, Germany, Greece, Brazil, Argentina, Japan, United Kingdom, Hungary, France, Sweden
-
Peter MacCallum Cancer Centre, AustraliaNational Health and Medical Research Council, Australia; University of MelbourneRecruitingHematologic Diseases | Inherited Platelet Disorder | Inherited BMF SyndromeAustralia
-
The University of QueenslandRoyal Brisbane and Women's HospitalUnknown
-
Hoffmann-La RocheChugai PharmaceuticalRecruitingGeneralized Myasthenia GravisFrance, Korea, Republic of, China, Argentina, Spain, Brazil, Russian Federation, Japan, Denmark, Australia, Italy, Turkey, Germany, United States, Netherlands, Taiwan, Poland, Canada
-
Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Basal Cell CarcinomaAustralia
-
Alexion Pharmaceuticals, Inc.RecruitingGeneralized Myasthenia GravisChina, United States, Spain, United Kingdom, Korea, Republic of, Italy, Germany, Japan, Brazil, France, Netherlands, Taiwan, Turkey, Israel, Poland, Austria, Denmark, Portugal, Canada, Serbia, Argentina, Switzerland
-
AlexionCompletedGeneralized Myasthenia GravisUnited States, Spain, Korea, Republic of, Austria, Canada, Czechia, Denmark, France, Germany, Israel, Italy, Japan, Netherlands, Portugal, Switzerland
-
Zydus Lifesciences LimitedCompletedCryopyrin Associated Periodic SyndromeAustralia
-
Erasmus Medical CenterRecruitingPulmonary Hypertension | Hernias, Diaphragmatic, Congenital | Hernia; Diaphragm Defect, CongenitalBelgium, Sweden, Austria, Australia, Germany, Netherlands, Italy
-
Foundation for Angelman Syndrome Therapeutics,...Queensland University of TechnologyRecruiting
-
Encoded TherapeuticsRecruiting
-
University of MichiganMedical University of South Carolina; Emory University; Medical College of Wisconsin and other collaboratorsCompletedCongenital Heart Disease | Hypoplastic Left Heart Syndrome | Hypoplastic Right Heart Syndrome | d-Transposition of the Great ArteriesUnited States, Australia
-
Inflazome UK LtdCompletedHealthy Volunteers | Cryopyrin Associated Periodic SyndromeAustralia
-
Nacuity Pharmaceuticals, Inc.Foundation Fighting BlindnessActive, not recruitingUsher SyndromesAustralia
-
Kirby InstituteBristol-Myers Squibb; GlaxoSmithKline; Merck Sharp & Dohme LLC; Roche Pharma AG; Boehringer... and other collaboratorsCompleted
-
Foundation for Cardiovascular Research, ZurichAbbott Medical DevicesUnknownHeart Septal Defects, Atrial | Embolism, ParadoxicalAustralia, Austria, Belgium, Switzerland
-
Zynerba Pharmaceuticals, Inc.Completed22Q Deletion SyndromeUnited States, Australia
-
Auregen Biotherapeutics, SAEnrolling by invitation
-
Janssen Research & Development, LLCRecruitingMyasthenia GravisUnited States, Korea, Republic of, Japan, Taiwan, Denmark, Germany, Czechia, China, Spain, Belgium, Canada, Mexico, Poland, Italy, France, Australia, Sweden
-
Peter MacCallum Cancer Centre, AustraliaGlaxoSmithKline; Celgene CorporationCompletedMyelodysplastic Syndromes (MDS) | Acute Myeloid Leukaemia (AML)Australia
-
CelgeneCompletedMyelodysplastic Syndromes | Beta-thalassemiaAustria
-
The University of New South WalesCompleted
-
The University of New South WalesCompleted
-
University of Alabama at BirminghamNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMyasthenia GravisThailand, Canada, Germany, Italy, Netherlands, Brazil, United States, Argentina, Australia, Chile, Japan, Mexico, Poland, Portugal, South Africa, Spain, Taiwan, United Kingdom
-
Insel Gruppe AG, University Hospital BernSwiss National Science FoundationCompletedHeart Defects, Congenital | Transposition of Great Vessels With Ventricular InversionSwitzerland, Austria
-
Imago BioSciences, Inc., a subsidiary of Merck...CompletedAcute Myeloid Leukemia | Myelodysplastic SyndromeAustralia
-
Deakin UniversityCompleted
-
Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
-
Murdoch Childrens Research InstituteCompletedTransposition of Great Vessels | Low Cardiac Output SyndromeMalaysia, Australia, Canada, Indonesia
-
Garvan Institute of Medical ResearchCompletedPrader-Willi SyndromeAustralia
-
Neuren Pharmaceuticals LimitedRecruiting
-
Novo Nordisk A/SCompletedAcquired Bleeding Disorder | Cardiac Surgery Requiring Cardiopulmonary BypassAustralia
-
Otsuka Australia Pharmaceutical Pty LtdCompletedMyelodysplastic Syndrome (MDS)Australia
-
Medical University of ViennaCroma-Pharma GmbHCompleted
-
AbbVieCelgene; Genentech, Inc.CompletedMyelodysplastic Syndromes (MDS)United States, Australia, Germany
-
Eloxx Pharmaceuticals, Inc.Recruiting
-
Novartis PharmaceuticalsCompletedTreatment for Basal Cell Carcinomas (BCCs) in Gorlin Syndrome PatientsAustria, Switzerland
-
Medical University of ViennaCompleted
-
Medical University of ViennaCompleted
-
Gerhard GarhoferCroma-Pharma GmbHCompleted
-
Medical University of ViennaCompletedCentral Venous Catheter | Congenital Heart Disease in Children | Wireless UltrasoundAustria
-
Medical University of ViennaTerminatedNontraumatic Compartment Syndrome of LegAustria