- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Congenital Myasthenic Syndromes in United Kingdom
Total 16766 results
-
Johns Hopkins UniversityBristol-Myers SquibbTerminated
-
Johns Hopkins UniversityCompleted
-
Northwestern UniversityTerminatedMyasthenia GravisUnited States
-
Baltimore VA Medical CenterUniversity of MarylandUnknown
-
Muscular Dystrophy AssociationUnknownMyasthenia GravisUnited States
-
Manchester University NHS Foundation TrustRecruitingAdrenal Hyperplasia, CongenitalUnited Kingdom
-
University of RochesterNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedAndersen-Tawil Syndrome | Andersen SyndromeUnited States, Canada, Italy, United Kingdom
-
University of Kansas Medical CenterTerra Biological LLCNot yet recruiting
-
HealthPartners InstituteCompleted
-
The Leeds Teaching Hospitals NHS TrustUnknownCubital Tunnel SyndromeUnited Kingdom
-
University College, LondonKing's College London; King's College Hospital NHS Trust; University of Oxford; Great Ormond Street Hospital for Children NHS Foundation TrustRecruitingEpilepsy | Lennox-Gastaut Syndrome, IntractableUnited Kingdom
-
St. Louis UniversityCSL BehringTerminated
-
Imperial College LondonRecruitingMay-Thurner SyndromeUnited Kingdom
-
Guy's HospitalUnknownCongenital Heart DiseaseUnited Kingdom
-
Great Ormond Street Hospital for Children NHS Foundation...GOSHCCCompletedTypically Developing Children | Talipes Equino Varus | Paediatric Orthopaedic | Paediatric NeurologicalUnited Kingdom
-
Sheffield Teaching Hospitals NHS Foundation TrustSociety for Endocrinology; The Clinical Endocrinology TrustCompletedCongenital Adrenal HyperplasiaUnited Kingdom
-
Great Ormond Street Hospital for Children NHS Foundation...University College, LondonNot yet recruitingCongenital Heart Disease | Children, OnlyUnited Kingdom
-
Oxford University Hospitals NHS TrustUnknownMyelodysplastic Syndromes | LeukemiaUnited Kingdom
-
Novo Nordisk A/SCompleted
-
Yale UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National Center...CompletedMyasthenia GravisUnited States
-
University of PortsmouthPortsmouth Hospitals NHS TrustNot yet recruitingCompartment Syndrome Nontraumatic Lower ExtremityUnited Kingdom
-
AllerganTerminatedDry Eye SyndromesUnited Kingdom
-
King's College Hospital NHS TrustSt George's, University of LondonActive, not recruitingCongenital Diaphragmatic HerniaUnited Kingdom
-
Mirum Pharmaceuticals, Inc.Completed
-
Mirum Pharmaceuticals, Inc.CompletedAlagille SyndromeUnited Kingdom
-
Cambridge University Hospitals NHS Foundation TrustRecruitingAcute Coronary SyndromesUnited Kingdom
-
Ad scientiamRecruitingMyasthenia GravisUnited States, France
-
King's College LondonKing's College Hospital NHS TrustUnknown
-
Liminal BioSciences Ltd.TerminatedAlström SyndromeUnited Kingdom
-
argenxCompletedGeneralized Myasthenia GravisUnited States, Belgium, Canada, Czechia, Denmark, France, Georgia, Germany, Hungary, Italy, Japan, Netherlands, Poland, Russian Federation, Serbia, United Kingdom
-
University of LeicesterRecruitingCongenital Heart DiseaseUnited Kingdom
-
King's College Hospital NHS TrustCompleted
-
Mazen Dimachkie, MDCSL BehringCompletedMyasthenia GravisUnited States, Canada
-
University of Alabama at BirminghamNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMyasthenia GravisThailand, Canada, Germany, Italy, Netherlands, Brazil, United States, Argentina, Australia, Chile, Japan, Mexico, Poland, Portugal, South Africa, Spain, Taiwan, United Kingdom
-
University of California, San FranciscoNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital NeutropeniaUnited States
-
London School of Economics and Political ScienceUniversity College, London; Bambino Gesù Hospital and Research Institute; German...CompletedCardiovascular Disease | Congenital Heart Disease | Aortic CoarctationUnited Kingdom
-
Imperial College LondonThe Drummond Foundation (RAMC charity)RecruitingCompartment Syndrome of Leg | Limb IschemiaUnited Kingdom
-
Encoded TherapeuticsRecruiting
-
Barts & The London NHS TrustCancer Research UK; AmgenUnknownMyelodysplastic SyndromeUnited Kingdom
-
NHS Greater Glasgow and ClydeUniversity of GlasgowCompletedHeart Defects, CongenitalUnited Kingdom
-
Yale UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National Center...RecruitingMyasthenia GravisUnited States
-
St. Jude Children's Research HospitalBaylor College of Medicine; Children's Hospital of Philadelphia; Dana-Farber... and other collaboratorsRecruitingMyelodysplastic Syndromes | Sickle Cell Disease | Fanconi Anemia | Severe Congenital Neutropenia | Bone Marrow Failure Syndromes | Blood Coagulation Disorder | Erythrocyte Disorder | Leukocyte Disorder | Hemostasis | Dyskeratosis Congenita | Diamond-Blackfan Anemia | Congenital Thrombocytopenia | Myeloproliferative...United States
-
Emory UniversityChildren's Healthcare of AtlantaTerminatedSickle Cell Disease | Fanconi Anemia | Thalassemia | Severe Congenital Neutropenia | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Leukocyte Adhesion Deficiency | Dyskeratosis-congenita | Chediak-Higashi Syndrome | Chronic-granulomatous Disease | Schwachman-Diamond...United States
-
Bellicum PharmaceuticalsTerminatedLymphoma, Non-Hodgkin | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Myelodysplastic Syndrome | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Osteopetrosis | Leukemia, Acute Myeloid (AML), ChildUnited Kingdom, Italy
-
UCB Biopharma S.P.R.L.CompletedMyasthenia GravisUnited States, Belgium, Canada, Czechia, Denmark, Germany, Spain
-
St George's, University of LondonSt George's University Hospitals NHS Foundation TrustActive, not recruitingCMV | Congenital Cmv | Maternal Infections Affecting Fetus or Newborn | Shedding VirusUnited Kingdom
-
Cardiff UniversityNovartisUnknownTuberous SclerosisUnited Kingdom
-
NHS Greater Glasgow and ClydeUniversity of Central LancashireCompletedFoot Ankle Injuries | Foot Injury | Foot Deformity | Foot Sprain | Feet, FlatUnited Kingdom
-
Nano4Imaging GmbHCERES GmbHCompletedCongenital Heart DefectGermany, United Kingdom
-
University Hospital Birmingham NHS Foundation TrustCompletedCompartment SyndromeUnited Kingdom