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Clinical Trials on Congenital Myasthenic Syndromes in United Kingdom
Total 16764 results
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QT Medical, Inc.University of California, Irvine; Lundquist Institute for Biomedical Innovation...Unknown
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Imperial College LondonWithdrawnAntiphospholipid SyndromeUnited Kingdom
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Ethicare GmbHUnknownHeart Failure | Dilated Cardiomyopathy | Congenital Heart DiseaseAustria, United Kingdom, Netherlands, Serbia, Hungary
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Imperial College LondonHomerton University Hospital NHS Foundation TrustWithdrawnPusher SyndromeUnited Kingdom
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DePuy InternationalTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Traumatic Femoral FracturesIndia, United Kingdom
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University of MiamiRecruitingHypoplastic Left Heart SyndromeUnited States
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Timothy J Nelson, MD, PhDMayo Clinic; Children's Hospital of Philadelphia; University of OklahomaCompletedHypoplastic Left Heart SyndromeUnited States
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University of CambridgeCambridge University Hospitals NHS Foundation Trust; Oxford University Hospitals... and other collaboratorsRecruitingCraniosynostoses | Synostosis | Skull DeformityUnited Kingdom
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University of PennsylvaniaCompletedCongenital Heart DiseaseUnited States
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Thryv Therapeutics, Inc.Recruiting
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndromes (MDS)United States, Australia, Canada, France, Germany, Italy, United Kingdom
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AlbireoCompletedAlagille SyndromeUnited States, United Kingdom, France, Germany, Canada, Netherlands, Italy, Malaysia, Belgium, Israel, New Zealand, Poland, Turkey
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Emory UniversityCompletedCongenital Heart DiseaseUnited States
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University Hospital Plymouth NHS TrustCompletedAcute Aortic SyndromeUnited Kingdom
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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University of OklahomaCompletedInflammation | Inflammatory Response | Cardiopulmonary Bypass | Congenital Heart Defect | Low Cardiac Output SyndromeUnited States
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Mirum Pharmaceuticals, Inc.Active, not recruitingCholestatic Liver Disease | Alagille Syndrome | Progressive Familial Intrahepatic CholestasisUnited States, United Kingdom, France, Belgium, Poland, Brazil, Mexico
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Mayo ClinicRecruitingHematologic Neoplasms | Myeloid Malignancy | Cytopenia | Bone Marrow Failure Syndrome | Clonal Cytopenia of Undetermined Significance | Clonal Hematopoiesis of Indeterminate Potential | Low Risk Myelodysplastic Syndrome | Inherited Bone Marrow Failure Syndrome | Clonal Expansion | Hereditary Neoplastic... and other conditionsUnited States
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Orthofix s.r.l.Not yet recruitingFractures, Bone | Deformity; Bone | Impending FractureUnited Kingdom
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Imperial College LondonMedical Research CouncilCompletedChronic Fatigue SyndromeUnited Kingdom
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ViiV HealthcareGlaxoSmithKlineCompletedHIV Infections | Infection, Human Immunodeficiency VirusUnited Kingdom
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Baylor College of MedicineCompletedCardiac Output, LowUnited States
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NovartisTerminatedHypertension With Metabolic SyndromeUnited Kingdom
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Manchester University NHS Foundation TrustNorthern Care Alliance NHS Foundation Trust; National Institute for Health... and other collaboratorsCompletedSubacromial Impingement Syndrome | Shoulder Impingement SyndromeUnited Kingdom
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Aneurin Bevan University Health BoardUnknownSubacromial Impingement SyndromeUnited Kingdom
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ViiV HealthcareCompletedInfections, Human Immunodeficiency Virus and HepatitisUnited Kingdom
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University of MichiganMedical University of South Carolina; Emory University; Medical College of Wisconsin and other collaboratorsCompletedCongenital Heart Disease | Hypoplastic Left Heart Syndrome | Hypoplastic Right Heart Syndrome | d-Transposition of the Great ArteriesUnited States, Australia
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Leukemia Research FundCompletedMyelodysplastic Syndromes | Leukemia | Myelodysplastic/Myeloproliferative NeoplasmsUnited Kingdom
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University of NottinghamUnknownReversible Cerebral Vasoconstriction SyndromeUnited Kingdom
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Children's National Research InstituteEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationChild Development | Congenital Zika Syndrome | Zika Virus | Congenital InfectionUnited States, Colombia
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Guy's and St Thomas' NHS Foundation TrustKing's College LondonRecruitingPost Thrombotic Syndrome | Venous Thrombosis Deep (Limbs)United Kingdom
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Imperial College LondonCompletedSleep Apnea Syndromes | Bronchiectasis | Asthma | COPD | Interstitial Lung DiseasesUnited Kingdom
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Guy's and St Thomas' NHS Foundation TrustFight for SightUnknownEye Diseases | Dry Eye | Eye Pain | Meibomian Gland Dysfunction | Dry Eye Syndrome | Blepharitis | Tear Film Insufficiency | Kerato Conjunctivitis Sicca | Punctate Epithelial Keratitis | Punctate KeratitisUnited Kingdom
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Oxford University Hospitals NHS TrustCompletedObesity | Obesity Hypoventilation SyndromeUnited Kingdom
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Rocket Pharmaceuticals Inc.Enrolling by invitationLeukocyte Adhesion DeficiencySpain, United States, United Kingdom
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Jazz PharmaceuticalsRecruitingTuberous Sclerosis Complex | Dravet Syndrome | Lennox Gastaut SyndromeUnited States
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Palvella Therapeutics, Inc.RecruitingPachyonychia CongenitaUnited States, United Kingdom
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Children's Hospital Medical Center, CincinnatiRecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello Syndrome | SYNGAP1-Related Intellectual Disability | DLG4 | RAS Mutation | Noonan Syndrome With Multiple Lentigines | Noonan Neurofibromatosis Syndrome | Smith-Kingsmore Syndrome | MTOR Gene Mutation | GATOR-1 Gene... and other conditionsUnited States
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University of UlsterEnrolling by invitationVisual Stress | Meares-Irlen Syndrome | Reading DifficultiesUnited Kingdom
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Hoffmann-La RocheCompletedDown SyndromeUnited States, France, Italy, Canada, United Kingdom, Argentina, Spain
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Gilead SciencesCompleted
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Institute of Child HealthCompletedRecurrent Neural Tube DefectsUnited Kingdom
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedVon Hippel-Lindau SyndromeUnited States
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M.D. Anderson Cancer CenterNovartisTerminated
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Manchester University NHS Foundation TrustUniversity of LeedsCompletedNeonatal Respiratory Distress SyndromeUnited Kingdom
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The Cleveland ClinicMetroHealth Medical CenterCompleted
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National Center for Research Resources (NCRR)CompletedRetinitis Pigmentosa | Usher Syndrome | Congenital Hearing ImpairmentUnited States
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Timothy J Nelson, MD, PhDMayo Clinic; Children's Hospital of Philadelphia; Children's Hospital Colorado; University of Oklahoma and other collaboratorsCompletedHypoplastic Left Heart SyndromeUnited States
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Zealandina AgencyCompleted
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University College, LondonUniversity of IowaUnknownCharcot-Marie-Tooth Disease, Type IA | Charcot-Marie-Tooth Disease Type 2A | Charcot-Marie-Tooth Disease, Type IB | Charcot-Marie-Tooth Disease, Type XUnited Kingdom