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Clinical Trials on Congenital Sucrase-isomaltase Deficiency in Japan
Total 8 results
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Novo Nordisk A/SCompletedObservational Study on Safety and Efficacy of NovoSeven® in Subjects With Congenital FVII DeficiencyCongenital Bleeding Disorder | Congenital FVII DeficiencyJapan
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TakedaActive, not recruitingCongenital Protein C DeficiencyJapan
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Novo Nordisk A/SEnrolling by invitationCongenital Bleeding Disorder | Congenital FXIII DeficiencyJapan
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic DisorderJapan
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Kyowa Kirin Co., Ltd.CompletedTumor-Induced Osteomalacia or Epidermal Nevus SyndromeJapan, Korea, Republic of
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Spain, Japan, Canada, United Kingdom, Korea, Republic of, Ireland, Thailand, Italy, Turkey, Denmark, Brazil, France, Germany, Netherlands, Switzerland
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Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, Spain, Switzerland, Turkey, Germany, France, United Kingdom, Japan, Netherlands, Brazil, Canada, Czechia, Denmark, Italy, Korea, Republic of, Thailand