- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Congenital Aplastic Anemia
Total 12645 results
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Indiana UniversityChildren's Hospital Medical Center, Cincinnati; Makerere University; Université... and other collaboratorsCompleted
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VersitiDana-Farber Cancer Institute; University of Illinois at Chicago; Medical College... and other collaboratorsUnknownSickle Cell Disease | Sickle Cell AnemiaUnited States
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Emmaus Medical, Inc.CompletedSickle Cell Anemia | Sickle ß0-ThalassemiaUnited States
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BloodworksUniversity of WashingtonCompletedSickle Cell Disease | Sickle Cell AnemiaUnited States
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Centre Hospitalier Universitaire de Pointe-a-PitreCompletedSickle Cell DiseaseGuadeloupe
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Assistance Publique - Hôpitaux de ParisCompletedSickle Cell AnemiaFrance
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HaEmek Medical Center, IsraelCompletedSickle Cell Anemia | Sickle Cell ThalassemiaIsrael
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National Institute of Diabetes and Digestive and...CompletedSickle Cell TraitUnited States
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Sickle Cell-Beta0-ThalassemiaUnited States
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Shanghai East HospitalUnknownChemotherapy-induced AnaemiaChina
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Agios Pharmaceuticals, Inc.RecruitingPyruvate Kinase DeficiencyUnited States, Germany, Spain, Italy, United Kingdom, Czechia, France, Canada, Korea, Republic of, Netherlands, Turkey, Portugal, Denmark, Ireland, Switzerland, Thailand
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Canada, Netherlands, United Kingdom, France, Italy
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Rocket Pharmaceuticals Inc.Active, not recruiting
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Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, United Kingdom, Netherlands, Canada, Denmark, France, Italy, Ireland, Thailand
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Rocket Pharmaceuticals Inc.Not yet recruitingPyruvate Kinase DeficiencySpain, United States
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Spain, Japan, Canada, United Kingdom, Korea, Republic of, Ireland, Thailand, Italy, Turkey, Denmark, Brazil, France, Germany, Netherlands, Switzerland
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RTI InternationalRecruitingSickle Cell DiseaseUnited States
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Children's Hospital Medical Center, CincinnatiMakerere University; Ministry of Health, Uganda; Mulago Hospital, UgandaRecruiting
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Bioray LaboratoriesChinese Academy of Medical SciencesNot yet recruiting
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Emory UniversityNational Center for Complementary and Integrative Health (NCCIH)Recruiting
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Medical University of South CarolinaNational Institute of Nursing Research (NINR)Recruiting
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Ahmadu Bello University Teaching HospitalCyprus Institute of Neurology and GeneticsNot yet recruiting
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The University of The West IndiesRecruiting
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Forma Therapeutics, Inc.Emory UniversityNot yet recruitingSickle Cell DiseaseUnited States
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Children's Hospital Medical Center, CincinnatiJinja Regional Referral Hospital (JRRH), Sickle Cell Clinic, Jinja, UgandaRecruiting
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Beam Therapeutics Inc.RecruitingSickle Cell DiseaseUnited States
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PfizerPfizerRecruitingSickle Cell DiseaseUnited States, Nigeria, Kenya, Lebanon
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David WilliamsNational Heart, Lung, and Blood Institute (NHLBI); bluebird bio; California Institute... and other collaboratorsRecruitingA Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN 2001) (GRASP)Sickle Cell DiseaseUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...Recruiting
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Hoffmann-La RocheRecruitingSickle Cell DiseaseUnited States, Spain, Brazil, United Kingdom, Italy, Turkey, Kenya, Netherlands, France, South Africa, Lebanon
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PfizerPfizerRecruitingSickle Cell DiseaseUnited States
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Enrico M NovelliNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Emory UniversityRecruitingSickle Cell DiseaseUnited States, Canada
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Hospices Civils de LyonRecruitingSickle Cell DiseaseFrance
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City of Hope Medical CenterRecruitingSickle Cell DiseaseUnited States
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Robert NickelThe Hospital for Sick Children; Ann & Robert H Lurie Children's Hospital of... and other collaboratorsRecruitingSickle Cell DiseaseUnited States, Canada
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Emory UniversityNational Center for Complementary and Integrative Health (NCCIH); Children's...RecruitingSickle Cell DiseaseUnited States
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St. Jude Children's Research HospitalBaylor College of Medicine; Children's Hospital of Philadelphia; Washington University... and other collaboratorsRecruiting
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Abdullah KutlarSecura Bio, Inc.RecruitingSickle Cell DiseaseUnited States
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Donald B. Kohn, M.D.California Institute for Regenerative Medicine (CIRM)Active, not recruiting
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The Hospital for Sick ChildrenChildren's Hospital of Eastern Ontario; Royal University Hospital Foundation; Connecticut Children's Medical CenterActive, not recruiting
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PfizerActive, not recruitingSickle Cell DiseaseUnited States, Oman, United Kingdom, France, Egypt, Ghana, Italy, Kenya, Nigeria, Saudi Arabia
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); University of Memphis; Methodist...Active, not recruiting
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Children's Hospital Medical Center, CincinnatiCompletedSickle Cell DiseaseUnited States
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Novartis PharmaceuticalsAvailableSickle Cell Disease
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Children's Hospital of PhiladelphiaPatient-Centered Outcomes Research Institute; Children's Hospital Medical Center... and other collaboratorsActive, not recruiting
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Novartis PharmaceuticalsTerminatedSickle Cell DiseaseUnited Arab Emirates, Bahrain, Kuwait, Qatar, Saudi Arabia
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Vanderbilt-Ingram Cancer CenterActive, not recruitingSickle Cell Disease | HemoglobinopathiesUnited States, United Kingdom, France
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bluebird bioEnrolling by invitationSickle Cell DiseaseUnited States, France