- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Congenital Bone Marrow Failure Syndromes
Total 12504 results
-
Centre Hospitalier Universitaire, AmiensUnknownMyelodysplastic SyndromesFrance
-
Memorial Sloan Kettering Cancer CenterWeill Medical College of Cornell University; YUKIGUNI COMPANYCompletedMyelodysplastic SyndromeUnited States
-
Shandong UniversityWithdrawn
-
National Heart, Lung, and Blood Institute (NHLBI)NovartisRecruitingSevere Aplastic AnemiaUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedThrombocytopenia | Anemia, Aplastic | Anemia, HypoplasticUnited States
-
SCRI Development Innovations, LLCNovartis PharmaceuticalsTerminated
-
PersImmune, IncUniversity of California, San DiegoUnknown
-
Institute of Hematology & Blood Diseases Hospital...RecruitingPlatelet Transfusion Refractoriness | Severe Aplastic AnemiaChina
-
CelgeneCompletedMyelodysplastic SyndromesUnited States, Germany
-
Peking Union Medical College HospitalNot yet recruitingMyelodysplastic Syndromes
-
The First Affiliated Hospital of Soochow UniversityEnrolling by invitation
-
CelgeneCompleted
-
Groupe Francophone des MyelodysplasiesCelgeneCompletedLenalidomide Combined to Azacitidine in Intermediate-2 or High Risk MDS With Del 5q (GFM-AZA-REV-09)Myelodysplastic SyndromesFrance
-
Sanquin Research & Blood Bank DivisionsNetherlands: Ministry of Health, Welfare and SportsWithdrawnMyelodysplastic SyndromesNetherlands
-
AkesoRecruitingHigher-risk Myelodysplastic SyndromesUnited States, China
-
Nuwacell Biotechnologies Co., Ltd.The First Affiliated Hospital of University of Science and Technology of...Not yet recruitingRelapsed / Refractory Myelodysplastic Syndromes
-
Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
-
University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
-
ALX Oncology Inc.Active, not recruitingHigher Risk Myelodysplastic SyndromesKorea, Republic of, United States, Spain
-
Eunice Kennedy Shriver National Institute of Child...CompletedStem Cell Transplant | Aplastic Anemia | HemoglobinUnited States
-
OHSU Knight Cancer InstituteNational Heart, Lung, and Blood Institute (NHLBI)CompletedChronic Myeloproliferative Disorders | Fanconi Anemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
-
Federal Research Institute of Pediatric Hematology...Not yet recruitingAplastic Anemia | Aplastic Anemia Idiopathic
-
National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic AnemiaUnited States
-
University Children's Hospital TuebingenUnknownAplastic Anemia | Acute Leukemias | Childhood Solid TumorGermany, Austria
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA)United States
-
Cooperative Study Group A for HematologyUnknownAplastic AnemiaKorea, Republic of
-
University of LeipzigCelgene CorporationRecruitingMyelodysplastic Syndromes | AnemiaGermany
-
Groupe Francophone des MyelodysplasiesCelgeneRecruitingMyelodysplastic Syndromes | MDSFrance
-
M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingLeukemiaUnited States
-
Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompleted
-
Nanfang Hospital of Southern Medical UniversityPeking University People's Hospital; Guangzhou First People's Hospital; Sun Yat-Sen... and other collaboratorsUnknownChemotherapy | Myelodysplastic SyndromeChina
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...TerminatedGenetic Disorder | Severe Aplastic Anemia | Immunodeficiency SyndromeUnited States
-
M.D. Anderson Cancer CenterTerminated
-
Memorial Sloan Kettering Cancer CenterRecruitingHemoglobinopathies | AML | MDS | Bone Marrow Failure | ALL | Inherited Metabolic Disorders | HLH | MPD Withou Myelofibrosis | NHL or HLUnited States
-
Rigel PharmaceuticalsRecruitingLow Risk Myelodysplastic SyndromesUnited States
-
Bristol-Myers SquibbActive, not recruitingLower-risk Myelodysplastic SyndromesJapan
-
Sumitomo Pharma America, Inc.TerminatedAnemia in Myelodysplastic SyndromesUnited States
-
National Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
-
Sunnybrook Health Sciences CentreNot yet recruitingMyelodysplastic Syndromes | MDSCanada
-
Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Actinium PharmaceuticalsCompletedLeukemia | Myelodysplastic SyndromeUnited States
-
Peking University People's HospitalUnknownLeukemia | Myelodysplastic SyndromeChina
-
Peking Union Medical College HospitalRecruitingAplastic Anemia | Drug Therapy | CSAChina
-
The Korean Society of Pediatric Hematology OncologyUnknownAnemia, AplasticKorea, Republic of
-
The Korean Society of Pediatric Hematology OncologyUnknown
-
Sumitomo Pharma America, Inc.TerminatedMyelodysplastic Syndromes (MDS)United States
-
Groupe Francophone des MyelodysplasiesUnknownAnemia in Myelodysplastic SyndromesFrance
-
Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
-
Peking University People's HospitalRecruitingMyelodysplastic Syndromes | Acute LeukemiaChina