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Clinical Trials on Congenital Erythropoietic Porphyria
Total 9000 results
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University of AberdeenNHS GrampianCompletedAbdominal Pain | Abdominal Cutaneous Nerve Entrapment SyndromeUnited Kingdom
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Afyonkarahisar Health Sciences UniversityCompletedMusculoskeletal Diseases | Carpal Tunnel Syndrome | Median Neuropathy | Entrapment NeuropathyTurkey
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C. R. BardTerminatedThe WavelinQ™ Arterio-Venous Endovascular Fistula: A Global, Post-Market Investigation (WAVE-Global)Chronic Kidney Diseases | End Stage Kidney Disease | Kidney Disease, Chronic | Kidney Failure | AV Fistula | Kidney Insufficiency | Fistulas ArteriovenousSwitzerland, Belgium, Greece
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SanofiTerminatedRetinitis Pigmentosa | Usher SyndromeUnited States, France
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Hospices Civils de LyonCompletedTelangiectasia, Hereditary Hemorrhagic | Osler Rendu DiseaseFrance
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Stanford UniversityCompletedEpistaxis | Hereditary Hemorrhagic Telangiectasia | HHT | Nose Bleeds | Nasal BleedingUnited States
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PellePharm, Inc.CompletedBasal Cell Nevus SyndromeUnited Kingdom
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Columbia UniversityWithdrawnBasal Cell Nevus Syndrome
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Pulmonary Hypertension | Cerebrovascular Disease | Chuvash PolycythemiaUnited States, Russian Federation
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University of California, San DiegoCompletedHereditary Hemorrhagic Telangiectasia (HHT)United States
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University of California, San DiegoCompletedHereditary Hemorrhagic Telangiectasia (HHT)United States
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Institut Jerome LejeuneFondation Jérôme LejeuneCompletedObstructive Sleep Apnea Syndrome | Down SyndromeFrance
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NYU Langone HealthCompletedAnxiety Disorders | Familial Dysautonomia | Dysthymia | Paroxysmal Hypertension | Autosomal Recessive DiseaseUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedChronic Kidney Disease | Autosomal Dominant Polycystic Kidney DiseaseAustralia, Belgium, Italy, Spain, Sweden, United States, Canada, Netherlands, Czechia, Poland, Germany, Russian Federation, Hungary, Israel, Puerto Rico, Argentina, Denmark, South Africa, United Kingdom, Norway, France, Romania
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University Health Network, TorontoCompletedBasal Cell Nevus SyndromeCanada
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HaEmek Medical Center, IsraelCompletedAnorexia | Sickle Cell Anemia | Thalassemia | Chronic Renal Failure | Suicide AttemptIsrael
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsBrazil
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University of California, San FranciscoCompletedArteriovenous Malformations | Cavernous Angiomas | Brain AneurysmsUnited States
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedNon-melanomatous Skin CancerUnited States
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University of California, San DiegoGenentech, Inc.WithdrawnHereditary Hemorrhagic Telangiectasia (HHT) | Nosebleeds
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Assistance Publique - Hôpitaux de ParisAventis PharmaceuticalsCompletedEHLERS-DANLOS SYNDROME, TYPE IV, AUTOSOMAL DOMINANT | CHROMOSOME 2q31.2 DELETION SYNDROME
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Mayo ClinicNovartis; National Center for Research Resources (NCRR)CompletedLiver Diseases | Abdominal Pain | Polycystic Kidney, Autosomal Dominant | Hepatomegaly | Polycystic Liver Disease | Kidney, PolycysticUnited States
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University of RochesterCompletedObstructive Sleep Apnea Syndrome | Cleft Lip/PalateUnited States
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Ankara City Hospital BilkentNot yet recruiting
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University of Campania "Luigi Vanvitelli"Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico; University of Milan and other collaboratorsRecruitingChronic Kidney Diseases | Ureteropelvic Junction ObstructionItaly
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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Istituto Ortopedico RizzoliRecruitingCollagen Diseases | Joint Hypermobility | Hypermobility Syndrome | Laxity of Ligament | Danlos Disease, EhlersItaly
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University of the PunjabHigher Education Commission (Pakistan); Centre of Excellence in Molecular Biology... and other collaboratorsRecruitingBurn Scar | Craniofacial Microsomia | Romberg Disease | Post-Traumatic Scar (Disorder)Pakistan
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Telomere Biology Disorders | Inherited Bone Marrow Failure SyndromesUnited States
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University of Colorado, DenverMayo Clinic; National Institute of Diabetes and Digestive and Kidney Diseases...RecruitingOverweight and Obesity | Autosomal Dominant Polycystic KidneyUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingDisorders of Sex Development (DSD) | Pediatric and Adolescent Cancers of the Genital Tract | Reproductive Endocrine Conditions in Puberty | Structural Gynecologic Conditions Including Vulvar and Vaginal ConditionsUnited States
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Children's Hospital of Eastern OntarioThe Physicians' Services Incorporated FoundationRecruitingChild | Obstructive Sleep Apnea | Down SyndromeCanada
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Johns Hopkins UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAnhydramnios | Potter Syndrome | Lung Hypoplasia | Multicystic Dysplastic Kidney | Multicystic Renal Dysplasia, Bilateral | Lower Urinary Tract Obstructive Syndrome | Fetal Renal AnomalyUnited States
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Novartis PharmaceuticalsRecruitingAcute Myeloid Leukemia | Primary Myelofibrosis | Polycythemia Vera | Thalassemia | Graft Versus Host DiseaseKorea, Republic of, Italy, Belgium, Japan, Germany, Australia, Bulgaria, Chile, China, Denmark, Greece, Hungary, Israel, Lebanon, Poland, Portugal, Russian Federation, Slovakia, South Africa, Spain, Sweden, Thailand, India, Mexico, Turkey, Fran...
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophies | Inherited Neuromuscular Conditions | Inherited Neuropathies | Muscle Myopathies | Hereditary Spastic ParaplegiasUnited States
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National Cancer Institute (NCI)SuspendedDown Syndrome | Recurrent B Acute Lymphoblastic LeukemiaUnited States, Canada, Puerto Rico, Australia
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Pharnext S.C.A.Premier Research Group plc; Eurofins Optimed; Synteract HCR (Syneos Health); Gr... and other collaboratorsActive, not recruitingCharcot-Marie-Tooth Disease, Type IAUnited States, Belgium, Canada, France, Netherlands, Spain, United Kingdom
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Vastra Gotaland RegionGöteborg UniversityCompletedHypermobile Ehlers-Danlos Syndrome | Joint Hypermobility SyndromeSweden
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Imperial College LondonCompletedHereditary Hemorrhagic Telangiectasia | Pulmonary Arteriovenous MalformationsUnited Kingdom
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Texas Tech University Health Sciences Center, El...TerminatedCerebral Cavernous Malformation | Hemorrhagic Stroke, IntracerebralUnited States
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Sol-Gel Technologies, Ltd.TerminatedBasal Cell Nevus SyndromeUnited States, France, Belgium, Denmark, Germany, Italy, Netherlands, Spain, United Kingdom
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Institut Jerome LejeuneHôpital Necker-Enfants MaladesActive, not recruitingDown Syndrome | Obstructive Sleep Apnea of NewbornFrance
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ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
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University Hospital, BordeauxAMRO-HHT-France - Association Maladie de Rendu-OslerCompletedHereditary Hemorrhagic Telangiectasia | Osler Weber Rendu DiseaseFrance
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SanofiActive, not recruitingUsher's SyndromeUnited States, France
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Yuzuncu Yıl UniversityCompleted
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Poznan University of Life SciencesCompletedObesity | Polycystic Ovary Syndrome | Hyperandrogenism | Insulin ResistancePoland
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Indiana University School of MedicineTerminatedSleep Apnea, Obstructive | Respiration DisordersUnited States
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Near East University, TurkeyCompletedPolycystic Ovary Syndrome | c Type Natriuretic Peptide | Menstrual Irregularity | HyperandrogenismCyprus
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UCSF Benioff Children's Hospital OaklandNational Cancer Institute (NCI)CompletedNeoplastic SyndromeUnited States