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Clinical Trials on Congenital Sucrase-isomaltase Deficiency
Total 345 results
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic DisorderIsrael
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic DisorderJapan
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University Hospital, AngersUniversity of Angers, AngersUnknownIsolated Growth Hormone Deficiency | Turner Syndrome | Pediatrics | Social Cognition | Cognitive Functions
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Delivery Systems | Foetal Growth Problem | Small for Gestational AgeFrance
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Delivery Systems | Foetal Growth Problem | Small for Gestational AgeFrance
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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Ferring PharmaceuticalsTerminated
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormon Deficiency | Turner Syndrome in Pre-pubertal Children
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedFanconi Syndrome | Cystinosis
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Baylor College of MedicineNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedRothmund-Thomson SyndromeUnited States
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National Institute of Diabetes and Digestive and...RecruitingCystic Fibrosis | Turner Syndrome | Congenital Hepatic Fibrosis | Immunologic Deficiency Syndrome | Idiopathic Non-Cirrhotic Portal HypertensionUnited States
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Bellicum PharmaceuticalsTerminatedLymphoma, Non-Hodgkin | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Myelodysplastic Syndrome | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Osteopetrosis | Leukemia, Acute Myeloid (AML), ChildUnited Kingdom, Italy
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Rambam Health Care CampusRecruitingBronchiectasis | Cystic Fibrosis | Bronchiolitis Obliterans | Primary Ciliary Dyskinesia | Primary Immune DeficiencyIsrael
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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Direction Centrale du Service de Santé des ArméesUnknownKaposi's DiseaseFrance
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Izmir Katip Celebi UniversityRecruitingClass III Malocclusion | Anterior Crossbite | Maxillary DeficiencyTurkey
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University Hospital, ToulouseCompletedPrader-Willi Syndrome | Growth Hormone DeficiencyFrance
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Marmara UniversityNational Institute of Allergy and Infectious Diseases (NIAID)UnknownProtein-Losing Enteropathies | CD55 - Cluster of Differentiation Antigen 55 Deficiency | Primary Intestinal Lymphangiectasis | Complement Regulatory Factor DefectTurkey
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Porteus, Matthew, MDRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Fred Hutchinson Cancer CenterNational Heart, Lung, and Blood Institute (NHLBI); Rocket Pharma LimitedTerminated
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Sanguine BiosciencesTerminated
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)Completed
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Unspecified Adult Solid Tumor, Protocol Specific | Fanconi AnemiaUnited States
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Acquired Bleeding Disorder | Acquired Haemophilia | Congenital FVII Deficiency | Glanzmann's DiseaseFrance
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Children's Hospital Los AngelesGenentech, Inc.CompletedGrowth Hormone Deficiency | Hypopituitarism | Septo-Optic DysplasiaUnited States
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Clinuvel Europe LimitedRecruitingXeroderma PigmentosumGermany
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Walter Reed Army Institute of Research (WRAIR)CompletedGlucosephosphate Dehydrogenase Deficiency | FavismUnited States
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de... and other collaboratorsCompletedFanconi AnemiaSpain
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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Rigshospitalet, DenmarkCompletedSpinal Muscular Atrophy | Merosin Deficient Congenital Muscular DystrophyDenmark
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Guy's and St Thomas' NHS Foundation TrustKing's College London; Newcastle University; University of CambridgeCompletedXeroderma PigmentosumUnited Kingdom
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Clinuvel Europe LimitedRecruitingXeroderma PigmentosumBelgium, Spain
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Institut PasteurInstitut Pasteur de la Guyane; Centre Hospitalier Andrée Rosemon de CayenneRecruiting
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Dong-A ST Co., Ltd.RecruitingGrowth Hormone Deficiency | Turner Syndrome | Small for Gestational Age | Idiopathic Short StatureKorea, Republic of
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Chronic Renal Failure | Turner Syndrome | Small for Gestational Age
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Zhizheng GeWithdrawnGastrointestinal Bleeding of Unknown Origin | Gastrointestinal Vascular Malformation | Thalidomide EfficiencyChina
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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University of RochesterRecruitingLymphoma | Myelodysplastic Syndromes | Multiple Myeloma | Solid Tumor | Acute Leukemia | Aplastic Anemia | Chronic Leukemia | Immune Deficiency Disorder | Congenital Hematological Disorder | Metabolism DisorderUnited States
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Inozyme PharmaGACI GlobalNot yet recruitingATP-Binding Cassette Subfamily C Member 6 Deficiency | Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
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Indiana UniversityCompletedAutosomal Dominant Hypophosphatemic RicketsUnited States
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Children's Hospital Medical Center, CincinnatiRecruiting
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain, United Kingdom
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States