- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Craniofacial Abnormalities in South Africa
Total 1398 results
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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Alnylam PharmaceuticalsCompletedAcute Hepatic PorphyriaUnited States, Belgium, Bulgaria, France, Italy, Mexico, Spain, Taiwan, United Kingdom, Netherlands, Korea, Republic of, Switzerland, Czechia, Poland, Finland, Australia, Germany, Israel, Norway, South Africa
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Netherlands, Portugal
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Kevin HillNational Center for Advancing Translational Sciences (NCATS)CompletedInflammatory Response | Congenital Heart Disease in ChildrenUnited States
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SanofiRecruiting
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W.L.Gore & AssociatesActive, not recruitingMigraine | Patent Foramen Ovale | PFO - Patent Foramen OvaleUnited States
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Monash UniversityNational Health and Medical Research Council, Australia; Cerebral Palsy Alliance and other collaboratorsRecruitingFetal Growth Retardation | Pregnancy Preterm | Stillbirth and Fetal DeathAustralia, New Zealand
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Mezzion Pharma Co. LtdRecruitingSingle Ventricle Heart DiseaseUnited States
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Mezzion Pharma Co. LtdNational Heart, Lung, and Blood Institute (NHLBI)UnknownFunctional Single Ventricle Heart DiseaseUnited States, Korea, Republic of, Canada
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Aerie PharmaceuticalsCompleted
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Mayne Pharma International Pty LtdTerminatedLamellar IchthyosisUnited States, Spain, Canada, Germany, France, Australia, Israel, Ukraine, United Kingdom
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston... and other collaboratorsCompletedPrader-Willi Syndrome | Rett Syndrome | Angelman Syndrome | Sleep ProblemsUnited States
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atHeart MedicalRecruitingHeart Diseases | Cardiovascular Diseases | Congenital Abnormalities | Heart Septal Defects, Atrial | Heart Defects, Congenital | Cardiovascular Abnormalities | Heart Septal DefectUnited States, France
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Fougera Pharmaceuticals Inc.CompletedPsoriasis | Atopic DermatitisUnited States
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Ardea Biosciences, Inc.Completed
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La Jolla Pharmaceutical CompanyTerminatedBeta-ThalassemiaAustralia, Thailand, United States, Greece, Italy, Lebanon, Turkey, United Kingdom
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Glycomine, Inc.Recruiting24-Week Study to Assess the PD, Safety, Tolerability, and PK of GLM101 in Participants With PMM2-CDGPmm2-CDGSpain, Australia, United States
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Greenwood Genetic CenterCompletedGalactosialidosis | Sialidosis | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Beta Mannosidosis | Mucolipidosis II | Mucolipidosis III | Schindler DiseaseUnited States
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Genzyme, a Sanofi CompanyWithdrawn
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Ultragenyx Pharmaceutical IncActive, not recruitingAngelman SyndromeUnited States, United Kingdom, Canada, Australia, France, Germany, Spain, Israel
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Australia, Belgium, Germany, Italy, Poland, Romania, United Kingdom, Argentina, Canada, France, Netherlands, Russian Federation
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University of AlbertaCompletedPain | Retinopathy of Prematurity | Acupuncture | Premature InfantCanada, Australia, Malaysia
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Pediatric Spine FoundationColumbia UniversityRecruitingEarly-Onset Scoliosis Deformity of SpineUnited States, Canada, Finland, Hong Kong
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Western Sydney Local Health DistrictRecruitingFamilial Adenomatous PolyposisAustralia
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Mucpharm Pty LtdSt George Hospital, Australia; Mobius Medical Pty Ltd.CompletedCOVID-19 Pneumonia | COVID-19 Acute Respiratory Distress Syndrome | Bromelains Adverse Reaction | Acetylcysteine Adverse Reaction | Mucus; PlugAustralia
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Zimmer BiometActive, not recruitingOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Patellofemoral Osteoarthritis | Traumatic Arthritis | Varus Deformity | Valgus Deformity | Knee Pain Chronic | Polyarthritis | Flexion Deformity of the KneeUnited States
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Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
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Timber Pharmaceuticals Inc.Active, not recruitingIchthyosisUnited States, Canada, Germany, France, Italy
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Rambam Health Care CampusHadassah Medical Organization; Tel-Aviv Sourasky Medical Center; Soroka University...CompletedGVHD | Bone Marrow Transplant Failure | Alpha 1-AntitrypsinIsrael
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SanofiTerminatedCongenital Cystic Kidney DiseaseGermany, Spain, United States, Australia, Belgium, Japan, Korea, Republic of, Netherlands
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SanofiRecruitingDermatitis AtopicArgentina, Japan, China, Czechia, Spain, United States, South Africa, United Kingdom, Denmark, Sweden, Turkey
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Oregon Health and Science UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingPancreatitis | Pancreatitis, Acute | Pancreas Divisum | Pancreatitis Idiopathic | Pancreas InflamedUnited States, Canada, Netherlands
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Vertex Pharmaceuticals IncorporatedTerminatedCystic FibrosisUnited Kingdom, Canada, Australia
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Vertex Pharmaceuticals IncorporatedCompleted
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Sequenom, Inc.CompletedDown Syndrome | Aneuploidy | Noninvasive Prenatal ScreeningUnited States
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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Mezzion Pharma Co. LtdNational Heart, Lung, and Blood Institute (NHLBI)CompletedSingle Ventricle Heart DiseaseUnited States, Korea, Republic of, Canada
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Otsuka Pharmaceutical Development & Commercialization...CompletedChronic Kidney Disease | Autosomal Dominant Polycystic Kidney DiseaseAustralia, Belgium, Italy, Spain, Sweden, United States, Canada, Netherlands, Czechia, Poland, Germany, Russian Federation, Hungary, Israel, Puerto Rico, Argentina, Denmark, South Africa, United Kingdom, Norway, France, Romania
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Erasmus Medical CenterUniversitaire Ziekenhuizen KU Leuven; ZonMw: The Netherlands Organisation for... and other collaboratorsTerminatedNeurofibromatosis Type 1Spain, Belgium, Netherlands
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Gilead SciencesTerminatedCystic FibrosisFrance, Germany, Spain, United Kingdom, Australia
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ACELYRIN Inc.RecruitingThyroid Eye DiseaseUnited States, Australia
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Hill Dermaceuticals, Inc.Covance; Synteract, Inc.TerminatedAtopic DermatitisUnited States
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncEnrolling by invitationMucopolysaccharidosis III-AUnited States, Australia, Spain
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Abbott Medical DevicesRecruitingStroke | Patent Foramen OvaleUnited States, Germany, Canada, Switzerland, Italy, Portugal, United Kingdom
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Hoffmann-La RocheRecruitingSickle Cell DiseaseUnited States, Spain, Brazil, United Kingdom, Italy, Turkey, Kenya, Netherlands, France, South Africa, Lebanon
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Abbott Medical DevicesCompletedAtrial Septal DefectUnited States
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BayerCompletedHemophilia A | Hematologic DiseaseFrance, Italy, Spain, United States, United Kingdom