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Clinical Trials on Cystinosis in United States
Total 22 results
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University of California, San DiegoRaptor Pharmaceuticals Corp.CompletedCystinosis | Nephropathic CystinosisUnited States
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National Human Genome Research Institute (NHGRI)Recruiting
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National Eye Institute (NEI)CompletedCystinosisUnited States
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University of California, San DiegoCalifornia Institute for Regenerative Medicine (CIRM); Cystinosis Research...Active, not recruiting
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Stanford UniversityRecruiting
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University of California, San DiegoEnrolling by invitationCystinosisUnited States
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National Eye Institute (NEI)Completed
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National Institute of Diabetes and Digestive and...Completed
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Horizon Pharma USA, Inc.Completed
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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National Center for Research Resources (NCRR)Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCystinosisUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedPseudotumor Cerebri | CystinosisUnited States
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Horizon Pharma USA, Inc.Completed
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Recordati Rare DiseasesCompletedCystinosisBelgium, France, United Kingdom, Germany, Italy
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Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, Netherlands
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Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, United Kingdom, Belgium, Italy, Netherlands
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Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, Netherlands
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Alice BertainaCalifornia Institute for Regenerative Medicine (CIRM)RecruitingCKD Stage 4 | Cystinosis | FSGS | SLE Nephritis | SIODUnited States
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National Institute of Dental and Craniofacial Research...CompletedDiabetes Mellitus | Head and Neck Neoplasms | Dental Caries | Sarcoidosis | Cystinosis | Sjorgren's SyndromeUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom