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Clinical Trials on Developmental Dysphasia Familial in South Africa
Total 295 results
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GB002, Inc., a wholly owned subsidiary of Gossamer...RecruitingPulmonary Arterial HypertensionUnited States, Australia, Spain, Czechia, France, Germany, United Kingdom, Belgium
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ActelionCompletedPulmonary Arterial HypertensionUnited States, Austria, Germany
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, Italy, United Kingdom, France, Sweden, Germany
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SanofiRecruitingOsteogenesis ImperfectaUnited States, Australia, Canada, France
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ActelionCompletedPulmonary Arterial HypertensionUnited States, Denmark, Sweden, Germany, Spain, Brazil, Saudi Arabia, Portugal, Greece, Slovakia, United Kingdom, Czech Republic
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ActelionCompletedPulmonary Arterial HypertensionUnited States, Canada, Colombia, Malaysia, Austria, Israel, Ukraine, Germany, Australia, China, Argentina, Mexico, Spain, Hungary, Belarus, Belgium, Chile, Czechia, Denmark, France, Greece, India, Ireland, Italy, Korea, Republic of, Nethe... and more
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NewAmsterdam PharmaActive, not recruitingDyslipidemias | Hypercholesterolemia | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Familial Hypercholesterolemia | Metabolic Disease | High Cholesterol | Genetic Disease, Inborn | Lipid Metabolism DisorderUnited States, Canada, Czechia, Georgia, Netherlands, Norway, Poland, South Africa, Spain, United Kingdom
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Washington University School of MedicineEli Lilly and Company; Hoffmann-La Roche; Avid Radiopharmaceuticals; National Institute... and other collaboratorsRecruitingDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, Italy, Argentina, Australia, Colombia, France, Ireland, Mexico, Netherlands, Puerto Rico, Spain, United Kingdom, Brazil, Japan, Germany
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MallinckrodtCompletedIdiopathic Pulmonary Arterial Hypertension | CardiomyopathyUnited Kingdom, United States, France, Spain, Netherlands
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Acceleron Pharma, Inc., a wholly-owned subsidiary...CompletedPulmonary Arterial HypertensionUnited States, Argentina, Australia, Belgium, Brazil, Canada, Czechia, France, Germany, Israel, Italy, Korea, Republic of, Mexico, Netherlands, New Zealand, Poland, Serbia, Spain, Sweden, Switzerland, United Kingdom
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ShionogiIntegriumCompletedCombined HyperlipidemiaUnited States
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, Japan, United Kingdom
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SynapDxCompleted
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Washington University School of MedicineNational Institute on Aging (NIA); Alzheimer's Association; Eisai Inc.; Accelerating...RecruitingDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, Italy, Argentina, Australia, Colombia, Netherlands, Puerto Rico, Spain, United Kingdom, France, Ireland, Mexico, Brazil, Japan, Germany
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Lumos PharmaEnrolling by invitationGrowth Hormone DeficiencyUnited States, Australia
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The University of Texas Health Science Center,...CompletedTuberous Sclerosis | AngiofibromasUnited States, Australia
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BioMarin PharmaceuticalCompletedAchondroplasiaUnited States, Australia, United Kingdom, Japan
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United TherapeuticsCompletedAn Open-Label, Long-Term Study of Oral Treprostinil in Subjects With Pulmonary Arterial HypertensionPulmonary Arterial HypertensionKorea, Republic of, United States, Australia, Austria, Taiwan, China, Israel, Canada, India, Germany, Singapore, United Kingdom, Brazil, Italy, Netherlands, Argentina, Sweden, Chile, Denmark, France, Greece, Mexico, Poland
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United TherapeuticsCompletedPulmonary Arterial HypertensionKorea, Republic of, United States, Australia, Austria, Taiwan, China, Israel, Canada, India, Germany, Singapore, United Kingdom, Brazil, Italy, Netherlands, Argentina, Sweden, Chile, Denmark, France, Greece, Mexico, Poland
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Jazz PharmaceuticalsCompletedAutism Spectrum DisorderUnited States, Spain, Germany, Canada, Australia, United Kingdom
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Insmed IncorporatedRecruitingPulmonary Arterial HypertensionUnited States, Spain, Argentina, Australia, Belgium, Brazil, Germany, Italy, Japan, Malaysia, Mexico, Philippines, Switzerland, United Kingdom, Serbia, Austria, Denmark
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University of SydneyUniversity of Pennsylvania; University of California, San Diego; University of... and other collaboratorsCompletedInfant, Newborn, Diseases | Infant, Premature, Diseases | Retinopathy of Prematurity | Bronchopulmonary Dysplasia | Infant, Very Low Birth WeightAustralia
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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Merck Sharp & Dohme LLCActive, not recruitingPulmonary Arterial Hypertension | Hypertension, PulmonaryUnited States, Argentina, Australia, Belgium, Canada, Colombia, France, Germany, Greece, Israel, Italy, Mexico, New Zealand, Poland, Russian Federation, Sweden, Turkey, United Kingdom
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Bellerophon Pulse TechnologiesCompletedPulmonary Arterial Hypertension | Pulmonary HypertensionUnited States, Canada
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ActelionTerminatedPulmonary Arterial HypertensionGermany, Korea, Republic of, Israel, Singapore, United States, Russian Federation, Brazil, Netherlands, Malaysia, Saudi Arabia, United Kingdom, Hong Kong, France, United Arab Emirates, Argentina
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GB002, Inc.RecruitingPulmonary Arterial HypertensionUnited States, Spain, Israel, Korea, Republic of, Netherlands, France, Singapore, United Kingdom, Lithuania, Australia, Latvia, Argentina, Portugal, Greece, Czechia, Puerto Rico, Belgium, Italy, Poland, Romania, Serbia, Austria, Chile, Denma... and more
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Acceleron Pharma, Inc., a wholly-owned subsidiary...RecruitingPulmonary Arterial Hypertension | PAHUnited States, France, Germany, Spain, Sweden, Argentina, Australia, Austria, Colombia, Croatia, Denmark, Greece, Israel, Italy, Korea, Republic of, Netherlands, New Zealand, Portugal, Serbia, Taiwan, United Kingdom, Brazil, Canada, B... and more
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Washington University School of MedicineHoffmann-La Roche; Genentech, Inc.; National Institute on Aging (NIA); Alzheimer...SuspendedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, Italy, France, Spain, Ireland, Argentina, Australia, Colombia, Germany, Mexico, Netherlands, Puerto Rico, United Kingdom
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United TherapeuticsCompletedPulmonary Arterial HypertensionUnited States, Canada, India, United Kingdom, Spain, Israel, Australia, Belgium, France, Austria, China, Germany, Ireland, Italy, Mexico, Netherlands, Poland, Portugal, Puerto Rico, Sweden
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PfizerCompletedGrowth Hormone Deficiency | Idiopathic Short StatureUnited States
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BioMarin PharmaceuticalCompletedAchondroplasiaUnited States, Australia, Germany, Spain, United Kingdom, Japan, Turkey
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Merck Sharp & Dohme LLCActive, not recruitingHypercholesterolemia | Familial HypercholesterolemiaUnited States, Australia, Brazil, Canada, Chile, Colombia, Czechia, Finland, Hong Kong, Hungary, Israel, Netherlands, New Zealand, Norway, Singapore, Spain, Taiwan
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United TherapeuticsCompletedPulmonary Arterial HypertensionUnited States
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PfizerCompletedIdiopathic Short StatureUnited States
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Merck Sharp & Dohme LLCCompletedHypercholesterolemia | Familial HypercholesterolemiaUnited States, Germany, Japan, Korea, Republic of, Mexico, Norway, Turkey, United Kingdom
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, Germany, Spain, United Kingdom, Japan, Turkey
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University of Colorado, DenverNational Heart, Lung, and Blood Institute (NHLBI)CompletedLung Diseases | Bronchopulmonary DysplasiaUnited States
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NewAmsterdam PharmaRecruitingDyslipidemias | Hypercholesterolemia | Familial Hypercholesterolemia | High Cholesterol | ASCVDUnited States
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CuremarkActive, not recruiting
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University of North Carolina, Chapel HillEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedBronchopulmonary DysplasiaUnited States
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ACADIA Pharmaceuticals Inc.RecruitingIrritability Associated With Autism Spectrum DisorderUnited States, Spain, France, Australia, Poland, Italy, Serbia, Hungary
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Merck KGaA, Darmstadt, GermanyCompletedAdult Growth Hormone DeficiencyUnited Kingdom, Germany, Australia, Sweden
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CuremarkCompletedAutismUnited States
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AmgenTerminatedOsteogenesis Imperfecta (OI)Canada, Czechia, Spain, United Kingdom, United States, Italy, Hungary, Australia, Belgium, France, Germany, Poland
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United TherapeuticsTerminatedCardiovascular Diseases | Vascular Diseases | Lung Diseases | Hypertension | Pulmonary Arterial Hypertension | Familial Primary Pulmonary Hypertension | Hypertension, Pulmonary | Pulmonary Hypertension | PAH | Respiratory Tract Disease | Connective Tissue DiseaseSpain, United States, Australia, Canada, United Kingdom, Italy, Argentina, Austria, Belgium, Brazil, Germany, Poland
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Reata, a wholly owned subsidiary of BiogenTerminatedConnective Tissue Disease-Associated Pulmonary Arterial HypertensionUnited States, Spain, Japan, Australia, United Kingdom, Canada, Germany, Belgium, Argentina, Israel, Mexico, Brazil, Czechia, Netherlands, Philippines
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Oak Hill Bio LtdTerminatedIntraventricular Hemorrhage | Bronchopulmonary Dysplasia | Chronic Lung Disease of Prematurity | Retinopathy of Prematurity (ROP)United States, Italy, United Kingdom
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Lumos PharmaActive, not recruitingGrowth Hormone DeficiencyUnited States, Australia, Israel, New Zealand, Poland, Ukraine