Clinical Trials on Diamond-Blackfan Anemia in Italy

Total 283 results

Novartis Pharmaceuticals

Completed

Expanded Access of Deferasirox to Patients With Congenital Disorders of Red Blood Cells and Chronic Iron Overload

Myelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan Anemia

United States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
Bellicum Pharmaceuticals

Terminated

Long Term Follow-up Study for Patients Enrolled on the BP-004 Clinical Study

Lymphoma, Non-Hodgkin | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Leukemia, Acute Myeloid (AML), Child

Italy
Bellicum Pharmaceuticals

Terminated

Safety Study of Gene Modified Donor T-cells Following TCRαβ+ Depleted Stem Cell Transplant

Lymphoma, Non-Hodgkin | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Myelodysplastic Syndrome | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Osteopetrosis | Leukemia, Acute Myeloid (AML), Child

United Kingdom, Italy
Bioverativ, a Sanofi company

Active, not recruiting

Safety and Tolerability Study in Adults With Cold Agglutinin Disease Previously Treated With SAR445088 or Never Treated With SAR445088

Autoimmune Haemolytic Anaemia

Netherlands, Germany, Italy, Norway, United Kingdom
University Hospital Freiburg

Completed

Assessing Immune Function in Young Patients With Cytopenia That Did Not Respond to Treatment

Myelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond Syndrome

Spain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
Bioverativ, a Sanofi company

Completed

A Safety and Tolerability Study of BIVV020 in Adults With Cold Agglutinin Disease

Autoimmune Haemolytic Anaemia

United States, Germany, Italy, Netherlands, Norway, United Kingdom
European Society for Blood and Marrow Transplantation
CHUGAI sanofi-aventis

Terminated

Randomized Study In Severe Aplastic Anemia Patients Receiving Atg, Cyclosporin A, With Or Without G-CSF (SAA-G-CSF) (SAA-G-CSF)

Aplastic Anaemia

France, Netherlands, Germany, United Kingdom, Switzerland, Italy, Sweden, Greece, Czechia
Fondazione Policlinico Universitario Agostino Gemelli...

Completed

Patient Blood Management In CARdiac sUrgical patientS (ICARUS)

Iron-deficiency | Anemia | Iron Deficiency Anemia | Iron Deficiency Anemia Treatment | Blood Loss Anemia | Erythropoiesis Abnormal

Italy
Mario Negri Institute for Pharmacological Research
Alnylam Pharmaceuticals

Withdrawn

Eculizumab to Cemdisiran Switch in aHUS (DANCE)

Atypical Hemolytic Uremic Syndrome

Italy
Istituto Ortopedico Galeazzi

Recruiting

Patient Blood Management in the Approach to Prosthetic Surgery [PBM(L4178)] (PBM(L4178))

Anemia, Iron Deficiency

Italy
Mario Negri Institute for Pharmacological Research

Recruiting

Functional Implications of Rare Gene Mutations in aHUS Open the Door to Personalized Therapy (aHUS-iPSC-EC)

Atypical Hemolytic Uremic Syndrome

Italy
Federico II University

Unknown

Alemtuzumab and Low-Dose Cyclosporine in Treating Patients With Severe Aplastic Anemia or Acquired Marrow Failure

Nonmalignant Neoplasm

Italy
Fondazione IRCCS Ca' Granda, Ospedale Maggiore...
University Hospital, Udine, Italy

Completed

A Single-Arm Pilot Study With Low-Dose Rituximab Plus Standard Oral Prednisone In Idiopathic Autoimmune Hemolytic Anemia

Autoimmune Hemolytic Disease (Cold Type) (Warm Type)

Italy
Clinica Fabia Mater

Completed

Bovine Lactoferrin to Prevent and Cure Iron Deficiency and Iron Deficiency Anemia in Complicated Pregnancies

Pregnancy | Iron Deficiency Anemia | Iron Deficiency

Italy
Società Italiana Talassemie ed Emoglobinopatie
Associazione Italiana de Ematologia e Oncologia Pediatrica; Società Italiana...

Completed

Transfusion Treatment in Patients With SCD

Anemia, Sickle Cell

Italy
IBSA Farmaceutici Italia Srl
Informapro Srl

Completed

Cross-over Study to Evaluate the Rate and the Extent of Iron Absorption of an ODF Iron Supplement vs an Iron Supplement in Capsules

Iron-deficiency

Italy
San Luigi Gonzaga Hospital

Completed

Avascular Bone Necrosis in Sickle Cell Disease: a Pediatric Study. (OsteoSCD)

Sickle Cell Disease

Italy
Mario Negri Institute for Pharmacological Research
ChemoCentryx

Terminated

Complement Inhibition in aHUS Dialysis Patients (ACCESS)

Atypical Hemolytic Uremic Syndrome

Italy
Fondazione IRCCS Ca' Granda, Ospedale Maggiore...

Unknown

Effects of a Dietary Approach to Iron Deficiency in Premenopausal Women Affected by Celiac Disease

Celiac Disease | Iron Deficiency (Without Anemia)

Italy
Società Italiana Talassemie ed Emoglobinopatie

Completed

Vitamin D and Bisphosphonates in the Treatment of Sickle Cell Disease

Sickle Cells Disease

Italy
Fondazione IRCCS Ca' Granda, Ospedale Maggiore...

Unknown

Sucrosomial Iron in Patients With Celiac Disease and IDA

Celiac Disease | Iron Deficiency Anemia

Italy
Vifor Pharma
ICON Clinical Research; American Regent, Inc.

Completed

Ferric Carboxymaltose (FCM) Assessment in Subjects With Iron Deficiency Anaemia and Non-dialysis-dependent Chronic Kidney Disease (NDD-CKD) (FIND-CKD)

Chronic Kidney Disease | Iron Deficiency Anaemia

United Kingdom, United States, Australia, Austria, Belgium, Czech Republic, Denmark, France, Germany, Greece, Italy, Netherlands, Norway, Poland, Portugal, Romania, Spain, Sweden, Turkey
Catholic University of the Sacred Heart
Fondazione Poliambulanza

Recruiting

Virtual Reality Training for Aphasia Rehabilitation (Aphasia360)

Anomic Aphasia

Italy
IRCCS Policlinico S. Matteo
Italian Group for the study of Inflammatory Bowel Disease (IG-IBD)

Recruiting

Clinical Burden of Anemia in Inflammatory Bowel Disease: Therapeutic Trial (RIDARTII)

Inflammatory Bowel Diseases | Iron Deficiency Anemia

Italy
Amgen

Completed

Study of Haemodialysis Patients Switching From Aranesp to Biosimilar (SHADE)

Anaemia

Australia, Italy, Poland, Germany, Greece, Bulgaria, Spain
Fondazione Poliambulanza Istituto Ospedaliero
Hospices Civils de Lyon; Fondazione Policlinico Universitario Agostino Gemelli... and other collaborators

Completed

Role of AI in CE for the Identification of SB Lesions in Patients With Small Intestinal Bleeding. (ArtIC)

Iron Deficiency Anemia | Obscure Gastrointestinal Bleeding

Italy
Vifor Pharma
Syneos Health; ClinStar, LLC

Completed

Ferinject® Assessment in Patients With Iron Deficiency and Chronic Heart Failure (FAIR-HF) (FAIR-HF)

Chronic Heart Failure | Iron Deficiency Anemia | Iron Deficiency | Anaemia

Italy, Spain, Germany, Poland, Romania, Ukraine, Greece, Norway, Argentina, Russian Federation
Università degli Studi di Ferrara

Completed

Impact of the Preparation Method of Red Cell Concentrates on Transfusion Indices in Thalassemic Patients

Thalassemia Major

Italy
Federico II University

Completed

The Role of OCTA in Patients Affected by Beta Thalassemia

Thalassemia

Italy
Federico II University

Completed

Endovenous Versus Liposomal Iron in CKD

Chronic Kidney Disease | Iron Deficiency Anemia

Italy
Rare Partners srl Impresa Sociale
Università degli Studi di Ferrara

Completed

Testing SIROLIMUS in Beta-thalassemia Transfusion Dependent Patients (SIRTHALACLIN)

Beta-Thalassemia

Italy
IRCCS San Raffaele
Orchard Therapeutics; Fondazione Telethon

Unknown

Gene Therapy for Transfusion Dependent Beta-thalassemia (TIGET-BTHAL)

Beta-Thalassemia

Italy
European Institute of Oncology

Recruiting

Total Body Irradiation Treatments for Patients Treated at European Institute of Oncology

Lymphoma | Leukemia | Aplastic Anemia | Leukemia, Acute | Leukemia, Chronic

Italy
IRCCS San Raffaele
Telethon Institute for Gene Therapy (OSR-TIGET)

Active, not recruiting

Long-term Follow-up of Subjects Treated With OTL-300 for Transfusion Dependent Beta-thalassemia Study (TIGET-BTHAL)

Beta Thalassaemia

Italy
Azienda Ospedaliera V. Cervello

Completed

Efficacy Study of the Use of Sequential DFP-DFO Versus DFP (SEQDFPDFO)

Beta-Thalassemia | Thalassemia Major

Italy
Royal Brompton & Harefield NHS Foundation Trust
CORDA, The Heart Charity; Apotex Inc.; The Cooley's Anemia Foundation,; The UK...

Unknown

Combined Chelation Treatment With Deferiprone and Deferoxamine in Thalassemia Major

Beta-Thalassemia

Italy
Mario Negri Institute for Pharmacological Research

Recruiting

New Analytic Tools for aHUS and C3G Diagnosis (COMPRare)

Healthy | Hemolytic-Uremic Syndrome | Membranoproliferative Glomerulonephritis

Italy
Novartis Pharmaceuticals

Completed

Effect of Deferasirox on Patients With Cardiac MRI T2* < 20 Msec

Beta Thalassemia Transfusion Dependent

Italy
GlaxoSmithKline

Recruiting

Anemia Studies in CKD: Erythropoiesis Via a Novel PHI Daprodustat - Pediatric (ASCEND-P) (ASCEND-P)

Anaemia

United States, Italy, Spain, France, United Kingdom, Korea, Republic of, Netherlands, Japan, Argentina, Belgium, Turkey
Cardiochirurgia E.H.

Completed

CardioSideral Heart Surgery: Randomized Study on Sucrosomial Iron Supplementation Before Heart Surgery (CHS)

Anemia

Italy
University of Campania "Luigi Vanvitelli"

Completed

Endocrine Function During Deferasirox Therapy

Iron Overload | Endocrine; Complications | Transfusion-dependent Thalassemia

Italy
Cerus Corporation

Completed

Study to Evaluate Efficacy and Safety of S303 Treated Red Blood Cells (RBCs)in Subjects With Thalassemia Major Requiring Chronic RBC Transfusion

Thalassemia Major

Turkey, Italy
Hospital Universitari Vall d'Hebron Research Institute

Active, not recruiting

GenoMed4ALL: Improving SCD Classification and Prognosis by AI (GenoMed4ALL)

Sickle Cell Disorders

Spain, Netherlands, France, Italy
Fondazione IRCCS Ca' Granda, Ospedale Maggiore...

Recruiting

Prospective Evaluation of Diagnosis and Treatment of Patients With Autoimmune Cytopenias Including Autoimmune Hemolytic Anemia, Immune Thrombocytopenia, and Chronic Idiopathic/Autoimmune Neutropenia (AIHA ITP CIN)

Myelodysplastic Syndromes | Immune Thrombocytopenia | Autoimmune Hemolytic Anemia | Cold Agglutinin Disease | Autoimmune Neutropenia | Chronic Idiopathic Neutropenia

Italy
University Hospital of Ferrara

Recruiting

Atrial Fibrillation in Beta-Thalassemia

Atrial Fibrillation | Thalassemia

Italy
Istituto Ortopedico Rizzoli

Completed

Transfusion Rates in Total Hip Replacement Before/After the Implementation of a Patient Blood Management Program. (pbm-hip)

Iron-deficiency | Arthroplasty | Transfusion | Anemia (Diagnosis)

Italy
Azienda Ospedaliera Universitaria Integrata Verona

Recruiting

Management of Preoperative Anaemia in Surgical Oncology

Anemia | Tumor

Italy
Gruppo Italiano Malattie EMatologiche dell'Adulto

Recruiting

Ibrutinib for the Treatment of AIHA in Patients With CLL/SLL or CLL-like MBL

Chronic Lymphocytic Leukemia | Small Lymphocytic Lymphoma | Autoimmune Hemolytic Anemia | Monoclonal B-Cell Lymphocytosis CLL-Type

Italy
Fondazione IRCCS Ca' Granda, Ospedale Maggiore...
University of Milano Bicocca

Unknown

Anemia of Inflammation: Investigation on Impaired Iron Regulation in Acutely Ill Patients and Their Clinical Outcome

Anemia of Acute Inflammation

Italy
Vertex Pharmaceuticals Incorporated
CRISPR Therapeutics

Recruiting

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

Hematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-Thalassemia

United States, Italy, Germany

Clinical Trials on Diamond-Blackfan Anemia in Italy

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