- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Disability in United States
Total 696 results
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Seaside Therapeutics, Inc.SuspendedFragile X SyndromeUnited States
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Italy, Argentina, France, Spain, Mexico, Canada, New Zealand, Singapore, United Kingdom
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University Hospitals Coventry and Warwickshire...University College, London; University of WarwickNot yet recruitingAmputation | Prosthesis User | Amputation; Traumatic, Hand | Prosthesis DurabilityUnited Kingdom
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RespireRxFRAXA Research FoundationCompletedFragile X Syndrome | AutismUnited States
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Duke UniversityFoundation for Prader-Willi ResearchCompletedChildhood Obesity | Prader Willi Syndrome | Syndromic ObesityUnited States, Canada
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University of EdinburghNHS LothianCompletedBurnout, Professional | Psychological Distress | Self Efficacy | Acceptance Processes | Intellectual Disabilities With Other Behavioral SymptomsUnited Kingdom
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University of South FloridaUniversity of California, Los Angeles; Temple UniversityCompletedGeneralized Anxiety Disorder | Social Phobia | Separation Anxiety Disorder | Specific Phobia | Autism | Autism Spectrum Disorders | Obsessive-compulsive Disorder | Asperger's Syndrome | Pervasive Developmental Disability - Not Otherwise SpecifiedUnited States
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Radius Pharmaceuticals, Inc.TerminatedPrader-Willi SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Oregon Health and Science UniversityActive, not recruitingObstructive Sleep Apnea of ChildUnited States
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Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHypertension | Cardiovascular Disease | Williams Syndrome | Multisystem Developmental Disorder | Elastin Gene DeletionUnited States
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National Human Genome Research Institute (NHGRI)CompletedMental Retardation | Sleep Disorders, Circadian Rhythm | Developmental Delay Disorders | Chromosome Deletion | Self Injurious BehaviorUnited States
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Children's Hospital of PhiladelphiaCompletedObstructive Sleep Apnea Syndrome | Down SyndromeUnited States
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REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
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ShireCompleted
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Boston Children's HospitalPhelan-McDermid Syndrome FoundationCompletedIntellectual Disability | Autism Spectrum Disorder | Phelan-McDermid SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Institute of Child HealthCompleted
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Ionis Pharmaceuticals, Inc.RecruitingMethyl CpG Binding Protein 2 (MECP2) Duplication SyndromeUnited States
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Ovid Therapeutics Inc.CompletedFragile X Syndrome (FXS)United States
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Radius Pharmaceuticals, Inc.TerminatedPrader-Willi SyndromeUnited States
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University of Southern CaliforniaNational Institute on Aging (NIA); Alzheimer's Therapeutic Research Institute; Alzheimer's Clinical Trials ConsortiumRecruitingDementia | Alzheimer Disease | Down SyndromeUnited States, Spain, United Kingdom
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Sequenom, Inc.RecruitingDown Syndrome | Fetal AneuploidyUnited States, Canada
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Spain, Canada, New Zealand, Argentina, Mexico, Singapore
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Maimonides Medical CenterFoundation for Prader-Willi ResearchRecruitingBody Weight | Hyperphagia | Prader-Willi Syndrome | Mood | Behavior | Excessive Daytime SleepinessUnited States
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Maimonides Medical CenterRecruitingAggression | Behavioral Symptoms | Pathologic Processes | Nervous System Diseases | Obesity | Neurologic Manifestations | Neurobehavioral Manifestations | Congenital Abnormalities | Overnutrition | Nutrition Disorders | Genetic Diseases, Inborn | Intellectual Disability | Self-Injurious Behavior | Abnormalities, Multiple and other conditionsUnited States
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Duke UniversityRecruiting
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxAvailableMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States
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University of MiamiUniversity of Pennsylvania; National Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health (NIH) and other collaboratorsRecruiting
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Cyprium Therapeutics, Inc.Enrolling by invitation
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Eunice Kennedy Shriver National Institute of Child...Completed
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Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Novo Nordisk A/SCompletedHealthy | Prader-Willi Syndrome | Genetic Disorder | Growth Disorder | Idiopathic Short StatureUnited States
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Lundquist Institute for Biomedical Innovation at...CompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIUnited States
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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ShireCompleted
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Neuren Pharmaceuticals Limitedrettsyndrome.orgCompleted
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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University of California, San FranciscoNational Human Genome Research Institute (NHGRI)CompletedEpilepsy | Cerebral Palsy | Intellectual Disability | Developmental Delay | Metabolic Disease | Neuro-Degenerative Disease | Encephalopathy | Birth Defect | Multiple Congenital Anomaly | Developmental DefectUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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Cindy CisnerosCompletedDown Syndrome | Aneuploidy | Trisomy 21 | Trisomy 18 | Trisomy 13United States
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Rocket Pharmaceuticals Inc.Recruiting
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REGENXBIO Inc.Withdrawn
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University of California, San DiegoBioMarin PharmaceuticalWithdrawnBehavioral Manifestations of Lesch-Nyhan DiseaseUnited States
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Women and Infants Hospital of Rhode IslandNatera, Inc.CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy XUnited States
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University of Colorado, DenverNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)RecruitingPsoriasis | Down Syndrome | Vitiligo | Hidradenitis Suppurativa | Alopecia Areata | Atopic Dermatitis / EczemaUnited States
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Masonic Cancer Center, University of MinnesotaWithdrawn