- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Disability
Total 1546 results
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Oregon Health and Science UniversityActive, not recruitingObstructive Sleep Apnea of ChildUnited States
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ShireCompletedHunter SyndromeUnited States, United Kingdom
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Diskapi Yildirim Beyazit Education and Research...UnknownCerebral Palsy | Covid19 | Telemedicine | Disability, Developmental | Caregiver Quality of LifeTurkey
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Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
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Bambino Gesù Hospital and Research InstituteAutour Des Williams; AceaUnknownFragile X Syndrome | Williams SyndromeItaly
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National Taiwan University HospitalUnknownRett Syndrome | Tourette Syndrome | Tic DisordersTaiwan
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Universidad de GuanajuatoCompletedDown Syndrome | Metabolic Syndrome XMexico
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Myelodysplastic/Myeloproliferative NeoplasmsUnited States, Canada, Puerto Rico, Australia, Netherlands, New Zealand, Switzerland
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Children's Health IrelandBelfast Health and Social Care Trust; University of Edinburgh; University Hospital... and other collaboratorsRecruitingQuality of Life | Obstructive Sleep Apnea | Down Syndrome | Behavior | Adherence, TreatmentUnited Kingdom, Ireland
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
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Hospices Civils de LyonCompletedAutism Spectrum Disorder | Williams Beuren Syndrome
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Sanko UniversityCompletedCerebral Palsy | Muscular Dystrophy | Down Syndrome | Parents | Spina BifidaTurkey
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Children's Hospital of PhiladelphiaCompletedObstructive Sleep Apnea Syndrome | Down SyndromeUnited States
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University Hospital, BordeauxFondation Syndrome de Rubinstein-TaybiCompletedRubinstein-Taybi SyndromeFrance
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University of California, San FranciscoMassachusetts General Hospital; Children's Hospital of Philadelphia; National... and other collaboratorsActive, not recruitingStroke | Epilepsy | Cerebral Palsy | Intellectual Disability | Intracranial Hemorrhages | Hypoxic-Ischemic Encephalopathy | Neonatal SeizureUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHypertension | Cardiovascular Disease | Williams Syndrome | Multisystem Developmental Disorder | Elastin Gene DeletionUnited States
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University of California, DavisUniversity of Alberta; St. Justine's HospitalCompletedNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXS | Mental Retardation, X LinkedUnited States, Canada
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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ShireCompleted
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis (MPS)United States, Argentina, Mexico, Spain, United Kingdom
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National Human Genome Research Institute (NHGRI)CompletedMental Retardation | Sleep Disorders, Circadian Rhythm | Developmental Delay Disorders | Chromosome Deletion | Self Injurious BehaviorUnited States
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Psyadon PharmaCompletedLesch-Nyhan DiseaseUnited States
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Dr. Rebecca SchuleGerman Research Foundation; German Center for Neurodegenerative Diseases (DZNE)RecruitingSpastic AtaxiaCanada, France, Germany, Italy, Netherlands, Turkey, United Kingdom
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National Cancer Institute (NCI)RecruitingDown Syndrome | B Acute Lymphoblastic Leukemia | B Lymphoblastic LymphomaUnited States, Canada, Puerto Rico, Australia, New Zealand
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The Hospital for Sick ChildrenRecruitingPrader-Willi Syndrome | Sleep Apnea, CentralCanada
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Enrolling by invitationIntellectual Disability | Down Syndrome | Attention Deficit Hyperactivity Disorder | Fragile X SyndromeUnited States
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Canada
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Children's Hospital of Eastern OntarioThe Physicians' Services Incorporated FoundationCompletedCerebral Palsy | Neuromuscular Diseases | Chronic Pain | Physical Disability | Concussion Post Syndrome | Congenital Heart DefectCanada
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Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Novo Nordisk A/SCompletedHealthy | Prader-Willi Syndrome | Genetic Disorder | Growth Disorder | Idiopathic Short StatureUnited States
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University Hospital, ToulouseRecruitingEpilepsy | Prader-Willi Syndrome | Angelman Syndrome | Smith-Magenis Syndrome | X Fragile SyndromeFrance
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingAcute Myeloid Leukemia | Down Syndrome | Myelodysplastic Syndrome | Myeloproliferative Neoplasm | Myeloid Leukemia Associated With Down SyndromeUnited States, Canada, Saudi Arabia, Puerto Rico, Australia, New Zealand
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Kahramanmaras Sutcu Imam UniversityCompletedCerebral Palsy | Muscular Dystrophy | Caregiver Burden | Down Syndrome | Spina Bifida | Disabilities MultipleTurkey
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ShireCovance; PRA Health Sciences; PharmaNetCompletedMucopolysaccharidosis II | Hunter Syndrome | MPS IIBrazil, Poland, Taiwan
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University of California, San DiegoBioMarin PharmaceuticalWithdrawnBehavioral Manifestations of Lesch-Nyhan DiseaseUnited States
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Axis Shield Diagnostics LtdThe Clinical Trial CompanyCompletedTrisomy 21 in Fetus | Trisomy 18 in Fetus | Trisomy 13 in FetusUnited Kingdom
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Women and Infants Hospital of Rhode IslandNatera, Inc.CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy XUnited States
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Lundquist Institute for Biomedical Innovation at...CompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIUnited States
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Cyprium Therapeutics, Inc.Enrolling by invitation
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Natera, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsTerminatedAneuploidy | Trisomy 21 | Trisomy 18 | Trisomy 13United States, Ireland, Canada, Italy, Korea, Republic of, Spain
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Fondazione TelethonCompletedPyruvate Dehydrogenase Complex DeficiencyItaly
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston... and other collaboratorsCompletedPrader-Willi Syndrome | Rett Syndrome | Angelman Syndrome | Sleep ProblemsUnited States
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Eunice Kennedy Shriver National Institute of Child...Completed
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Hospital Universitario ArabaBioaraba Health Research InstituteNot yet recruitingHypertension | Usability | Patient Experience | Cardiac Function and HemodynamicsSpain
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TakedaRecruitingHunter SyndromeCanada, France