- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Durability
Total 1520 results
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Children's Healthcare of AtlantaTerminated
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King's College LondonUnknown
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Johns Hopkins UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Not yet recruitingDepression | Quality of Life | End Stage Renal Disease | Disability PhysicalUnited States
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Perha PharmaceuticalsFondation Jérôme Lejeune; European Innovation Council; France 2030 programRecruitingHealthy Volunteers | Down Syndrome | Alzheimer's DiseaseFrance
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Assistance Publique - Hôpitaux de ParisNot yet recruitingPeriodontitis | Trisomy 21France
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRecruitingMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States, United Kingdom, Netherlands
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
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University of Kansas Medical CenterNational Institute on Aging (NIA)CompletedAlzheimer Disease | Down SyndromeUnited States
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Stanford UniversityCompletedIntellectual Disability | Fragile X SyndromeUnited States
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University Hospital, ToulouseCompletedPrader-Willi SyndromeFrance
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development...Completed
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Parc de Salut MarHospital Infantil Universitario Niño Jesús, Madrid, Spain; Hospital Universitario... and other collaboratorsCompletedDown Syndrome | Fragile X SyndromeSpain
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University Hospital, MontpellierUnknownCongenital Heart Defects | Dysmorphic Facial Features and Intellectual Developmental DisorderFrance
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedFragile X Syndrome (FXS)United States
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Children's Oncology GroupNational Cancer Institute (NCI)Withdrawn
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ShionogiCompletedCerebral Palsy | Sialorrhea | Mental Retardation | Neurological ConditionsUnited States
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New York State Institute for Basic ResearchEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedDown Syndrome | Alzheimer's Disease
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National Human Genome Research Institute (NHGRI)CompletedMicrocephaly | Failure to Thrive | Abnormalities | Mental RetardationUnited States
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National Center for Research Resources (NCRR)Completed
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ACADIA Pharmaceuticals Inc.RecruitingHyperphagia in Prader-Willi SyndromeUnited States, Canada, United Kingdom
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Gazi UniversityRecruitingKnee Osteoarthritis | Foot Deformities | Disability Physical | Pes Planus | Knee Pain Chronic | Lower Limb Deformity | Pes CavusTurkey
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University of UlsterBelfast Health and Social Care Trust; Sheffield Teaching Hospitals NHS Foundation... and other collaboratorsRecruitingStroke | Paralysis | Motor Neuron Disease | Disorder of Consciousness | Physical DisabilityUnited Kingdom, Ireland
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University of Colorado, DenverRecruitingAlzheimer Disease | Down Syndrome | Mild Cognitive ImpairmentUnited States
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ACADIA Pharmaceuticals Inc.Enrolling by invitationHyperphagia in Prader-Willi SyndromeUnited States
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxAvailableMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States
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Hospices Civils de LyonCompletedWilliams Beuren SyndromeFrance
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Michael RafiiJanssen Research & Development, LLCCompleted
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Centre Hospitalier Universitaire de Saint EtienneMinistry of Health, FranceCompleted
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Sequenom, Inc.PRA Health SciencesCompletedPregnancy | Down Syndrome | Aneuploidy | Edwards SyndromeUnited States, France
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Children's Treatment NetworkMcMaster UniversityCompletedCerebral Palsy | Brain Injury | Autism | Down's SyndromeCanada
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National Institute on Aging (NIA)UnknownDown Syndrome | Alzheimer's DiseaseUnited States
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Ionis Pharmaceuticals, Inc.RecruitingMethyl CpG Binding Protein 2 (MECP2) Duplication SyndromeUnited States
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University of Colorado, DenverNational Heart, Lung, and Blood Institute (NHLBI)RecruitingDown Syndrome | Dysphagia, OropharyngealUnited States
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University of PaviaEnrolling by invitationDown Syndrome | Gingival BleedingItaly
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METAFORA biosystemsAssistance Publique - Hôpitaux de Paris; European Commission; Ministry for Health... and other collaboratorsCompletedMovement Disorders | Intellectual Disability | Seizures | Ataxia | Glut1 Deficiency Syndrome | De Vivo DiseaseFrance
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University Hospital, MontpellierFondation Jérôme Lejeune; association autour des Williams; réseau de santé Maladies...UnknownAnxiety | Williams SyndromeFrance
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Ovid Therapeutics Inc.Completed
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Centre Hospitalier Sud FrancilienNot yet recruiting
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Qilu Hospital of Shandong UniversityRecruitingChild | Williams Syndrome | Neurodevelopmental DelayChina
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University of Kansas Medical CenterNot yet recruitingObesity | Alzheimer Disease | Down SyndromeUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingCardiovascular Disease | Williams Syndrome | Supravalvular Aortic StenosisUnited States
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LuMind IDSC FoundationAlzheimer's Disease Cooperative Study (ADCS)Active, not recruitingAlzheimer's Disease in Down SyndromeUnited States
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Massachusetts General HospitalCompleted
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityCompleted
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Brigham and Women's HospitalChildren's Hospital of Philadelphia; University of Michigan; University of Texas... and other collaboratorsCompletedSleep Disordered Breathing | Down SyndromeUnited States
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome, Preserved Speech Variant | Mecp2 Duplication Syndrome | Rett-related DisordersUnited States
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University Hospital, BrestUnknownDysautonomia | Masculinity | MECP2-Related Severe Neonatal EncephalopathyFrance
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Madonna Rehabilitation HospitalUnknownStroke | Multiple Sclerosis | Paralysis | Brain Injuries | Spinal Cord Injuries | Disability PhysicalUnited States
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Duke UniversityFoundation for Prader-Willi ResearchCompletedChildhood Obesity | Prader Willi Syndrome | Syndromic ObesityUnited States, Canada
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Sequenom, Inc.ObstetrixCompleted