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Clinical Trials on Dystonia, Familial
Total 1684 results
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LIB Therapeutics LLCCompletedHomozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey, India
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Israel, Netherlands, Taiwan, Belgium, Denmark
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NovartisCompletedMixed Dyslipidemia | Heterozygous Familial HypercholesterolemiaSwitzerland
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PfizerCompletedTransthyretin Familial Amyloid Poluneuropathy
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Baylor Research InstituteUnknownUterine AtonyUnited States
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Herzog HospitalJoint Distribution Committee (JDC)Unknown
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University of California, IrvineWithdrawnDysfunctional LaborUnited States
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Hopital FochCompletedRadiotherapy Side Effect | Cervical Spasm | Botulinum ToxinFrance
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Castle Creek Biosciences, LLC.CompletedDysphonia Resulting From Vocal Fold Scarring | Age-related DysphoniaUnited States
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The Rogosin InstituteRecruitingHomozygous Familial HypercholesterolemiaUnited States
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel
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VIVE - The Danish Center for Social Science ResearchKFUMs Sociale Arbejde; FDF; KFUM spejderneCompleted
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GCS IHFB Cognacq-JayFondation de FranceCompletedBereaved FamiliesFrance
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NYU Langone HealthRecruitingHereditary Sensory and Autonomic Neuropathies | Familial Dysautonomia (Riley-Day Syndrome) | Hereditary Sensory and Autonomic Neuropathy 3United States, Israel
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KK Women's and Children's HospitalUnknownEmotional Well-being of First-time Families | Nutritional Health of Mother and Child | Parenting Self-Efficacy for First-time Families | Experience of First-time FamiliesSingapore
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National Institute of Diabetes and Digestive and...RecruitingLipodystrophyUnited States
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Chinese Medical AssociationRecruitingAortic Dissection | Family Research | Aortic Dissection, Familial, With or Without Aortic AneurysmChina
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Shenzhen People's HospitalInnovent Biopharmaceutical Co., Ltd.Active, not recruitingEfficacy and Safety | Heterozygous Familial Hypercholesterolemia | PCSK9China
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Danish Headache CenterEUROHEADCompletedHealthy Volunteers | Familial Hemiplegic Migraine Type 1 and 2Denmark
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Assistance Publique - Hôpitaux de ParisInstitute of Cardiometabolism and Nutrition, FranceCompletedFamilial Hypercholesterolemia - HeterozygousFrance
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Catabasis PharmaceuticalsCompletedHypertriglyceridemia | Hyperlipoproteinemia Type I | Lipoprotein Lipase Deficiency, Familial | Chylomicronemia, FamilialCanada
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M.D. Anderson Cancer CenterNot yet recruitingFamilial Platelet Disorder | HematopoieticUnited States
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National Institutes of Health Clinical Center (CC)Completed
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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Akcea TherapeuticsCaligorRx, Inc.No longer availableFamilial Chylomicronemia
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Shenzhen People's HospitalRecruitingEvaluate the Efficacy and Safety of IBI306 in Subjects With Homozygous Familial HypercholesterolemiaLipid Metabolism Disorders | Familial Hypercholesterolemia - Homozygous | Proprotein Convertase Subtilisin/Kexin 9China
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The Hospital for Sick ChildrenCompletedFamilial or Severe HypercholesterolemiaCanada
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Mayo ClinicCompleted
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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Mayo ClinicUniversity of California, San Francisco; University of MinnesotaCompletedFamilial Pancreatic CancerUnited States
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Assiut UniversityBaylor College of Medicine; Middle-Eastern College of Obstetricians and GynecologistsNot yet recruitingPre-Eclampsia | Gestational Diabetes | Labour Dystocia
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Massachusetts General HospitalNational Institute on Deafness and Other Communication Disorders (NIDCD)CompletedMuscle Tension Dysphonia | Vocal Fold NodulesUnited States
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Meir Medical CenterUnknown
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University Hospital, MontpellierEA2415 - Montpellier University, Montpellier, FranceRecruitingCongenital Torticollis | Positionnel Skull DeformationFrance
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Mario Negri Institute for Pharmacological ResearchFondazione TelethonCompleted
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REGENXBIO Inc.Active, not recruitingHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Netherlands
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Karo Bio ABTerminatedHeterozygous Familial Hypercholesterolaemia
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University Medical Center GroningenAstraZenecaCompletedHeart Failure | Cardiomyopathy, Familial | Phospholamban R14del CardiomyopathyNetherlands
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Institute of Cardiometabolism and Nutrition, FranceAmgenUnknownFamilial Hypercholesterolemia - HeterozygousFrance
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Visirna Therapeutics HK LimitedNot yet recruitingFamilial Chylomicronemia Syndrome
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Ionis Pharmaceuticals, Inc.AvailableFamilial Chylomicronemia Syndrome
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Jiangsu HengRui Medicine Co., Ltd.CompletedMixed Hyperlipidemia | Non-familial HypercholesterolemiaChina
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Abhimanyu GargCompletedFamilial Partial LipodystrophyUnited States
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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UniQure Biopharma B.V.CompletedLipoprotein Lipase Deficiency | Familial Hyperlipoproteinemia Type 1 | Familial HyperchylomicronemiaGermany
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom