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Clinical Trials on Dystrophic Epidermolysis Bullosa in United States
Total 812 results
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
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Cooperative International Neuromuscular Research...Completed
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Hoffmann-La RocheActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, United Kingdom, Italy, Denmark
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ML Bio Solutions, Inc.Virginia Commonwealth UniversityCompletedMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, Denmark
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, France, Italy
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Solid Biosciences Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsCompletedBecker Muscular Dystrophy | Healthy VolunteerUnited States
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Santhera PharmaceuticalsCompleted
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Sarepta Therapeutics, Inc.University College, London; Catholic University of the Sacred Heart; University... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited Kingdom, United States, France, Italy
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableCongenital Muscular Dystrophy Due to Lamin A/C MutationUnited States
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Astellas Pharma IncTerminatedDuchenne Muscular Dystrophy (DMD)United States
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Virginia Commonwealth UniversityEdgewise Therapeutics, Inc.RecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Muscular Dystrophy in Children | Muscular Dystrophy, BeckerUnited States, New Zealand, United Kingdom
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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University of FloridaCompleted
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Kowa Research Institute, Inc.RecruitingFuchs Endothelial Corneal DystrophyUnited States, Germany, Spain, Canada, United Kingdom, Denmark
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Adam Fedyk, MD, FACSAlcon ResearchRecruitingCataract | Fuchs DystrophyUnited States
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The Cleveland ClinicNational Eye Institute (NEI)CompletedRetinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
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National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
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Epirium Bio Inc.CompletedBecker Muscular DystrophyUnited States
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Stealth BioTherapeutics Inc.CompletedFuchs' Corneal Endothelial Dystrophy (FCED)United States
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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GenethonActive, not recruitingLGMD2IDenmark, France, United Kingdom
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalRecruiting
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AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
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Johns Hopkins UniversityRecruitingGranular Dystrophy, CornealUnited States
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
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Price Vision GroupTerminatedFuchs' Endothelial DystrophyUnited States
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Skulpt, Inc.National Institute of Neurological Disorders and Stroke (NINDS)CompletedDuchenne Muscular DystrophyUnited States
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Akashi TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States
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Massachusetts Eye and Ear InfirmaryCompletedFuchs' Endothelial DystrophyUnited States
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Oregon Health and Science UniversityTerminated
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States
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Processa PharmaceuticalsTerminated
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Aerie PharmaceuticalsCompleted
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CureDuchenneRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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ProQR TherapeuticsWithdrawnCorneal Diseases | Fuchs Endothelial Corneal Dystrophy | FECD3 | LRS | Descemet's Membrane DisorderUnited Kingdom