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Clinical Trials on Dystrophies, Landouzy-Dejerine
Total 1256 results
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Par Pharmaceutical, Inc.SFBC AnapharmCompletedTo Determine Bioequivalence Under Fed Conditions
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Rigshospitalet, DenmarkRecruitingLimb Girdle Muscular DystrophyDenmark
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Lenus Therapeutics, LLCTerminatedDystrophic Epidermolysis Bullosa | Junctional Epidermolysis BullosaUnited States
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Virginia Commonwealth UniversityWashington University School of Medicine; University of Iowa; University of Minnesota and other collaboratorsRecruitingMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, United Kingdom
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Sarepta Therapeutics, Inc.Active, not recruiting
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ML Bio Solutions, Inc.Virginia Commonwealth UniversityCompletedMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, Denmark
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Neurogen Brain and Spine InstituteWithdrawn
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Université de ParakouUniversity of Copenhagen; Hôpital Cochin; University of Ghana; Institut de Recherche... and other collaboratorsCompletedDetermine the Impact of Treatment on the Acquisition of Anti-malarial Antibodies in Children Before, During and After the Intervention | Determine the Prevalence of Malarial Infection in Children Before, During and After Seasonal Malaria ChemopreventionBenin
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Rigshospitalet, DenmarkFunding: Toyota Foundation; Funding: Hede Nielsen Foundation; Funding: Grosserer... and other collaboratorsActive, not recruiting
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GenethonActive, not recruitingLGMD2IDenmark, France, United Kingdom
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Human Stem Cell Institute, RussiaGenotargetEnrolling by invitationDysferlinopathy | Miyoshi Myopathy | LGMDR2 | DMATRussian Federation
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Neurogen Brain and Spine InstituteWithdrawn
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Intelligent Medical Implants GmbHUnknownRetinitis Pigmentosa | Choroideremia | Cone-Rod Dystrophy
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OrganogenesisTerminatedEpidermolysis Bullosa Dystrophica | Epidermolysis Bullosa, JunctionalUnited States
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Alex Ekwueme Federal University Teaching HospitalCompletedTo Determine Efficacy of Tranexamic Acid in Reducing Blood Loss During MyomectomyNigeria
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Philips HealthcareCompletedCompare Image Quality Between SDCT and Conventional CT Images of Any Tissue Lesion, Determine Optimal Monochromatic Energy Level for a Coronary Artery ImageUnited States
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Sultan Qaboos UniversityCompleted
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Ascidian Therapeutics, IncRecruitingStargardt Disease | Stargardt Disease 1 | Juvenile Macular Degeneration | Cone Rod DystrophyUnited States
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University Hospital, LilleRecruitingMacular Degeneration | Cone Dystrophy | Cone Rod Dystrophy | Retinal Dystrophy, Cone-RodFrance
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Egyptian Atomic Energy AuthorityWaleed Nemr,Egyptian Atomic Energy AuthorityCompletedEpidermolysis Bullosa | Chronic Skin UlcerEgypt
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Badr UniversityCompletedto Determine the Effect of Pilate's Exercises on Gross Motor Function and BalanceEgypt
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Frontera TherapeuticsRecruitingBiallelic RPE65 Mutation-associated Retinal DystrophyChina
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Novartis PharmaceuticalsActive, not recruitingBiallelic RPE65 Mutation-associated Retinal DystrophyJapan
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Assistance Publique - Hôpitaux de ParisNot yet recruitingLimb Girdle Muscular Dystrophy
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedLimb-Girdle Muscular DystrophyUnited States
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Assiut UniversityNot yet recruitingLimb-girdle Muscular Dystrophy
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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Newcastle-upon-Tyne Hospitals NHS TrustJain FoundationActive, not recruitingDysferlinopathy | LGMD2B Now Classified as LGMDR2 | Miyoshi MyopathyKorea, Republic of, Chile, Spain, United States, Denmark, France, Italy, Japan, United Kingdom
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Rigshospitalet, DenmarkCompleted
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Par Pharmaceutical, Inc.Cetero Research, San AntonioCompletedTo Determine Bioequivalence Under Fasting Conditions
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PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
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Rigshospitalet, DenmarkCompletedLimb-girdle Muscular DystrophyDenmark
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Castle Creek Pharmaceuticals, LLCCompletedDystrophic Epidermolysis Bullosa | Epidermolysis Bullosa Simplex | Junctional Epidermolysis Bullosa | Epidermolysis Bullosa (EB)United States
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PYC TherapeuticsRecruitingRetinal Dystrophy | PRPF31 Mutationassociated Retinal Dystrophy | RP11United States
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Innostellar Biotherapeutics Co.,LtdActive, not recruitingInherited Retinal Dystrophy Associated With RPE65 MutationsChina
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Sarepta Therapeutics, Inc.Active, not recruiting
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, France, Germany
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Denmark, Italy
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Laval UniversityCompleted
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Retrotope, Inc.Active, not recruitingInfantile Neuroaxonal DystrophyUnited States
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George Papanicolaou HospitalCompletedTo Present the Clinical Outcomes of Diurnal IOP Monitoring and Determine Its Value in Our Clinical Practice
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
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University Hospital, Basel, SwitzerlandInstitute of Molecular and Clinical Ophthalmology BaselRecruitingRetinal DystrophiesUnited States, Switzerland, China, Germany, Hungary, Italy, United Kingdom
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Retrotope, Inc.CompletedInfantile Neuroaxonal Dystrophy | INADUnited States
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National Eye Institute (NEI)TerminatedInherited Retinal Degeneration | Inherited Ophthalmic DiseasesUnited States
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University of Arkansas, FayettevilleCompletedDetermine the Effects of Nitrosigine and Citrulline-malate on Flow-mediated Dilation Among Young AdultsUnited States
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Netherlands Institute for Innovative Ocular SurgeryAmnitrans Eyebank Rotterdam; Melles CorneaClinic RotterdamCompletedCorneal Dystrophies, HereditaryNetherlands
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Winthrop University HospitalNational Institute on Aging (NIA)CompletedDetermine Effect of Vitamin D on Bone Health in Elderly African American WomenUnited States
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Cooperative International Neuromuscular Research...United States Department of DefenseCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Japan, Canada
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)CompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States